Novel Combinatorial MicroRNA-Binding Sites in AAV Vectors Synergistically Diminish Antigen Presentation and Transgene Immunity for Efficient and Stable Transduction
Muhuri, Manish, Zhan, Wei, Maeda, Yukiko, Li, Jia, Lotun, Anoushka, Chen, Jennifer, Sylvia, Katelyn, Dasgupta, Ishani, Arjomandnejad, Motahareh, Nixon, Thomas, Keeler, Allison M, Manokaran, Sangeetha, He, Ran, Su, Qin, Tai, Phillip W L, Gao, Guangping
Published in Frontiers in immunology (28.04.2021)
Published in Frontiers in immunology (28.04.2021)
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Modulating immune responses to AAV by expanded polyclonal T-regs and capsid specific chimeric antigen receptor T-regulatory cells
Arjomandnejad, Motahareh, Sylvia, Katelyn, Blackwood, Meghan, Nixon, Thomas, Tang, Qiushi, Muhuri, Manish, Gruntman, Alisha M., Gao, Guangping, Flotte, Terence R., Keeler, Allison M.
Published in Molecular therapy. Methods & clinical development (10.12.2021)
Published in Molecular therapy. Methods & clinical development (10.12.2021)
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Intralingual and Intrapleural AAV Gene Therapy Prolongs Survival in a SOD1 ALS Mouse Model
Keeler, Allison M., Zieger, Marina, Semple, Carson, Pucci, Logan, Veinbachs, Alessandra, Brown, Robert H., Mueller, Christian, ElMallah, Mai K.
Published in Molecular therapy. Methods & clinical development (12.06.2020)
Published in Molecular therapy. Methods & clinical development (12.06.2020)
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Immunogenicity of Recombinant Adeno-Associated Virus (AAV) Vectors for Gene Transfer
Arjomandnejad, Motahareh, Dasgupta, Ishani, Flotte, Terence R., Keeler, Allison M.
Published in BioDrugs : clinical immunotherapeutics, biopharmaceuticals, and gene therapy (01.05.2023)
Published in BioDrugs : clinical immunotherapeutics, biopharmaceuticals, and gene therapy (01.05.2023)
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Long-term Correction of Very Long-chain Acyl-CoA Dehydrogenase Deficiency in Mice Using AAV9 Gene Therapy
Keeler, Allison M, Conlon, Thomas, Walter, Glenn, Zeng, Huadong, Shaffer, Scott A, Dungtao, Fu, Erger, Kirsten, Cossette, Travis, Tang, Qiushi, Mueller, Christian, Flotte, Terence R
Published in Molecular therapy (01.06.2012)
Published in Molecular therapy (01.06.2012)
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Bridging from Intramuscular to Limb Perfusion Delivery of rAAV: Optimization in a Non-human Primate Study
Gruntman, Alisha M., Gernoux, Gwladys, Tang, Qiushi, Ye, Guo-Jie, Knop, Dave R., Wang, Gensheng, Benson, Janet, Coleman, Kristen E., Keeler, Allison M., Mueller, Christian, Chicoine, Louis G., Chulay, Jeffrey D., Flotte, Terence R.
Published in Molecular therapy. Methods & clinical development (14.06.2019)
Published in Molecular therapy. Methods & clinical development (14.06.2019)
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Pollen-derived RNAs Are Found in the Human Circulation
Koupenova, Milka, Mick, Eric, Corkrey, Heather A., Singh, Anupama, Tanriverdi, Selim E., Vitseva, Olga, Levy, Daniel, Keeler, Allison M., Ezzaty Mirhashemi, Marzieh, ElMallah, Mai K., Gerstein, Mark, Rozowsky, Joel, Tanriverdi, Kahraman, Freedman, Jane E.
Published in iScience (27.09.2019)
Published in iScience (27.09.2019)
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Systemic AAV9 gene transfer in adult GM1 gangliosidosis mice reduces lysosomal storage in CNS and extends lifespan
Weismann, Cara M, Ferreira, Jennifer, Keeler, Allison M, Su, Qin, Qui, Linghua, Shaffer, Scott A, Xu, Zuoshang, Gao, Guangping, Sena-Esteves, Miguel
Published in Human molecular genetics (01.08.2015)
Published in Human molecular genetics (01.08.2015)
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AAV gene therapy for Tay-Sachs disease
Flotte, Terence R, Cataltepe, Oguz, Puri, Ajit, Batista, Ana Rita, Moser, Richard, McKenna-Yasek, Diane, Douthwright, Catherine, Gernoux, Gwladys, Blackwood, Meghan, Mueller, Christian, Tai, Phillip W L, Jiang, Xuntian, Bateman, Scot, Spanakis, Spiro G, Parzych, Julia, Keeler, Allison M, Abayazeed, Aly, Rohatgi, Saurabh, Gibson, Laura, Finberg, Robert, Barton, Bruce A, Vardar, Zeynep, Shazeeb, Mohammed Salman, Gounis, Matthew, Tifft, Cynthia J, Eichler, Florian S, Brown, Jr, Robert H, Martin, Douglas R, Gray-Edwards, Heather L, Sena-Esteves, Miguel
Published in Nature medicine (01.02.2022)
Published in Nature medicine (01.02.2022)
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CAR T-Cell Therapy: Progress and Prospects
Wilkins, Olivia, Keeler, Allison M, Flotte, Terence R
Published in Human gene therapy. Part B. Methods (01.04.2017)
Published in Human gene therapy. Part B. Methods (01.04.2017)
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Regulatory T Cell Therapeutics for Neuroinflammatory Disorders
Harkins, Ashley L, Kopec, Acadia L, Keeler, Allison M
Published in Critical reviews in immunology (2022)
Published in Critical reviews in immunology (2022)
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Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector
Choudhury, Sourav R, Harris, Anne F, Cabral, Damien J, Keeler, Allison M, Sapp, Ellen, Ferreira, Jennifer S, Gray-Edwards, Heather L, Johnson, Jacob A, Johnson, Aime K, Su, Qin, Stoica, Lorelei, DiFiglia, Marian, Aronin, Neil, Martin, Douglas R, Gao, Guangping, Sena-Esteves, Miguel
Published in Molecular therapy (01.04.2016)
Published in Molecular therapy (01.04.2016)
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Systemic Delivery of AAVB1-GAA Clears Glycogen and Prolongs Survival in a Mouse Model of Pompe Disease
Keeler, Allison M, Zieger, Marina, Todeasa, Sophia H, McCall, Angela L, Gifford, Jennifer C, Birsak, Samantha, Choudhury, Sourav R, Byrne, Barry J, Sena-Esteves, Miguel, ElMallah, Mai K
Published in Human gene therapy (01.01.2019)
Published in Human gene therapy (01.01.2019)
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