Promoterless gene targeting without nucleases ameliorates haemophilia B in mice
Barzel, A, Paulk, N K, Shi, Y, Huang, Y, Chu, K, Zhang, F, Valdmanis, P N, Spector, L P, Porteus, M H, Gaensler, K M, Kay, M A
Published in Nature (London) (15.01.2015)
Published in Nature (London) (15.01.2015)
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Journal Article
A Minicircle Plasmid Containing the Human Manganese Superoxide Dismutase (MnSOD) Transgene Confers Radioprotection to Cells InVitro
Zhang, X, Epperly, M.W, Kay, M.A, Chen, Z, Smith, T, Franicola, D, Greenberger, J.S
Published in International journal of radiation oncology, biology, physics (01.11.2007)
Published in International journal of radiation oncology, biology, physics (01.11.2007)
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Extracellular matrix component cotransplantation prolongs survival of heterotopically transplanted human hepatocytes in mice
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Conference Proceeding
Heterotopically Transplanted Hepatocyte Survival Depends on Extracellular Matrix Components
Ohashi, K., Kay, M.A., Kuge, H., Yokoyama, T., Kanehiro, H., Hisanaga, M., Ko, S., Nagao, M., Sho, M., Nakajima, Y.
Published in Transplantation proceedings (01.12.2005)
Published in Transplantation proceedings (01.12.2005)
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Journal Article
Genomic progression in mouse models for liver tumors
Tward, A D, Jones, K D, Yant, S, Kay, M A, Wang, R, Bishop, J M
Published in Cold Spring Harbor Symposia on Quantitative Biology (2005)
Published in Cold Spring Harbor Symposia on Quantitative Biology (2005)
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Journal Article
Efficient gene transduction to cultured hepatocytes by HIV-1 derived lentiviral vector
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Conference Proceeding
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cMet activation allows persistent engraftment of ectopically transplanted xenogenic human hepatocytes in mice
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Journal Article
Conference Proceeding
Upregulation of the microRNA cluster at the Dlk1-Dio3 locus in lung adenocarcinoma
Valdmanis, P N, Roy-Chaudhuri, B, Kim, H K, Sayles, L C, Zheng, Y, Chuang, C-H, Caswell, D R, Chu, K, Zhang, Y, Winslow, M M, Sweet-Cordero, E A, Kay, M A
Published in Oncogene (02.01.2015)
Published in Oncogene (02.01.2015)
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Journal Article
Site-specific genomic integration produces therapeutic Factor IX levels in mice
Calos, Michele P, Olivares, Eric C, Hollis, Roger P, Chalberg, Thomas W, Meuse, Leonard, Kay, Mark A
Published in Nature biotechnology (01.11.2002)
Published in Nature biotechnology (01.11.2002)
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Journal Article
Transposition from a gutless adeno-transposon vector stabilizes transgene expression in vivo
Kay, Mark A, Yant, Stephen R, Ehrhardt, Anja, Mikkelsen, Jacob Giehm, Meuse, Leonard, Pham, Thao
Published in Nature biotechnology (01.10.2002)
Published in Nature biotechnology (01.10.2002)
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Journal Article
In vivo Hepatic Gene Therapy: Complete Albeit Transient Correction of Factor IX Deficiency in Hemophilia B Dogs
Kay, Mark A., Landen, Charles N., Rothenberg, Steven R., Taylor, Lesli A., Leland, Frances, Wiehle, Sandra, Fang, Bingliang, Bellinger, Dwight, Finegold, Milton, Thompson, Arthur R., Read, Marjorie, Brinkhous, Kenneth M., Savio L. C. Woo
Published in Proceedings of the National Academy of Sciences - PNAS (15.03.1994)
Published in Proceedings of the National Academy of Sciences - PNAS (15.03.1994)
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75 In vivo selection of primary and bone-marrowderived hepatocytes after allogeneic transplantation in mice
Streetz, K.L., Doyonnas, R., Jenkins, D., Perryman, S., Fuess, S., Lin, S., Shizuru, J., Blau, H., Trautwein, C., Sylvester, K., Kay, M.A.
Published in Journal of hepatology (01.04.2006)
Published in Journal of hepatology (01.04.2006)
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A model to quantitate cell transplant function after liver-specific injury
Jenkins, D.D., Streetz, K., Kay, M.A., Longaker, M.T., Sylvester, K.G.
Published in The Journal of surgical research (01.10.2003)
Published in The Journal of surgical research (01.10.2003)
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Journal Article
Hepatic Gene Therapy: Efficient Gene Delivery and Expression in Primary Hepatocytes Utilizing a Conjugated Adenovirus-DNA Complex
Cristiano, Richard J., Smith, Louis C., Kay, Mark A., Brinkley, B. R., Savio L. C. Woo
Published in Proceedings of the National Academy of Sciences - PNAS (15.12.1993)
Published in Proceedings of the National Academy of Sciences - PNAS (15.12.1993)
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Developmental genetics of ribosome synthesis in Drosophila
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