Elucidation of the EP defect in Diamond-Blackfan anemia by characterization and prospective isolation of human EPs
Iskander, Deena, Psaila, Bethan, Gerrard, Gareth, Chaidos, Aristeidis, En Foong, Hui, Harrington, Yvonne, Karnik, Leena C., Roberts, Irene, de la Fuente, Josu, Karadimitris, Anastasios
Published in Blood (16.04.2015)
Published in Blood (16.04.2015)
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Journal Article
Complex Clonal Evolution Can Occur Following Transplantation for Transfusion Dependent Thalassaemia in the Context of Mixed Myeloid Chimerism and Reduced Conditioning Regimens
Gassas, Adam, O'Boyle, Farah, Chaudhury, Shahzya, Petterson, Toni, Lund, Kirstin, Karnik, Leena, de la Fuente, Josu
Published in Blood (23.11.2021)
Published in Blood (23.11.2021)
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Journal Article
Stable Neurocognitive Function with Improvement in Processing Speed Following Haploidentical Bone Marrow Transplant with Post-Transplant Cytoxan in Children and Adolescents with Sickle Cell Disease
Patel, Dilan A, Prussien, Kemar V, Wilkerson, Karina L, Armstrong, Becky, Karnik, Leena, Kassim, Adetola A., de la Fuente, Josu
Published in Blood (13.11.2019)
Published in Blood (13.11.2019)
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Single-cell profiling of human bone marrow progenitors reveals mechanisms of failing erythropoiesis in Diamond-Blackfan anemia
Iskander, Deena, Wang, Guanlin, Heuston, Elisabeth F, Christodoulidou, Chrysi, Psaila, Bethan, Ponnusamy, Kanagaraju, Ren, Hongwei, Mokhtari, Zeinab, Robinson, Mark, Chaidos, Aristeidis, Trivedi, Pritesh, Trasanidis, Nikolaos, Katsarou, Alexia, Szydlo, Richard, Palii, Carmen G, Zaidi, Mehmood H, Al-Oqaily, Qais, Caputo, Valentina S, Roy, Anindita, Harrington, Yvonne, Karnik, Leena, Naresh, Kikkeri, Mead, Adam J, Thongjuea, Supat, Brand, Marjorie, de la Fuente, Josu, Bodine, David M, Roberts, Irene, Karadimitris, Anastasios
Published in Science translational medicine (08.09.2021)
Published in Science translational medicine (08.09.2021)
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Fludarabine/Treosulfan/Thiotepa/ATG Conditioning for Related Transplantation in b Thalassaemia Major Leads to Early and Sustained Engraftment with Low Incidence of VOD and GvHD but a High Rate of Long-Term Mixed Chimerism
O'Boyle, Farah, Karnik, Leena, Lund, Kirstin, Szydlo, Richard, de la Fuente, Josu
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Journal Article
Pre-Transplantation Suppression of Haemopoiesis Is Associated with a High Rate of Macrophage Activation Syndrome in Ptcy Haploidentical Transplantation for Haemoglobinopathies
Katewa, Satyendra, Kharya, Gaurav, Karnik, Leena, Kassim, Adetola A., de la Fuente, Josu
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Journal Article
Effective Desensitization Strategy for Patients with Sickle Cell Disease with High Donor Specific Antibodies Undergoing Haploidentical Bone Marrow Transplant with Posttransplant Cyclophosphamide
Biltibo, Eden, Jayani, Reena, Karnik, Leena, Gassas, Adam, O'Boyle, Farah, Dexter, Daniel, Wilkerson, Karina, Gatwood, Katie S., Orton, Lindsay, Dholaria, Bhagirathbhai, Savani, Bipin N., Engelhardt, Brian G., Sengsayadeth, Salyka M., Kitko, Carrie Lynn, Connelly, James P, Kassim, Adetola A., de la Fuente, Josu
Published in Blood (15.11.2022)
Published in Blood (15.11.2022)
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Journal Article
Improvement in Processing Speed Following Haploidentical Bone Marrow Transplant with Post-Transplant Cytoxan in Children and Adolescents with Sickle Cell Disease
Prussien, Kemar V., Patel, Dilan A., Wilkerson, Karina, Armstrong, Becky, Karnik, Leena, de la Fuente, Josu, Kassim, Adetola A.
Published in Pediatric blood & cancer (08.10.2019)
Published in Pediatric blood & cancer (08.10.2019)
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Journal Article
Fludarabine/Treosulfan/Thiotepa/ATG Conditioning for Matched and Single Antigen Mismatched Unrelated Bone Marrow Transplantation in Haemoglobinopathies Is Feasible and Leads to Early and Sustanined Engraftment with No Long-Term Toxicity or GvHD
O'Boyle, Farah, Karnik, Leena, Bradshaw, Anne, Szydlo, Richard M, de la Fuente, Josu
Published in Blood (02.12.2016)
Published in Blood (02.12.2016)
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Journal Article
Fludarabine/Treosulfan/Thiotepa/ATG Conditioning for Related Transplantation in β Thalassaemia Major Leads to Early and Sustained Engraftment with Low Incidence of VOD and GvHD
O'Boyle, Farah, Karnik, Leena, Bradshaw, Anne, Szydlo, Richard M, de la Fuente, Josu
Published in Blood (02.12.2016)
Published in Blood (02.12.2016)
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Journal Article
Improvement in processing speed following haploidentical bone marrow transplant with posttransplant cytoxan in children and adolescents with sickle cell disease
Prussien, Kemar V., Patel, Dilan A., Wilkerson, Karina, Armstrong, Becky, Karnik, Leena, la Fuente, Josu, Kassim, Adetola A.
Published in Pediatric blood & cancer (01.01.2020)
Published in Pediatric blood & cancer (01.01.2020)
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Journal Article
Increased Incidence of New-Onset Diabetes Mellitus Type II Following Haploidentical Bone Marrow Transplant with Post-Transplant Cyclophosphamide for Sickle Cell Disease
Patel, Dilan A, de la Fuente, Josu, Matheney, Michael, Karnik, Leena, Chen, Heidi, Gatwood, Katie S., Culos, Kathryn A., Wilkerson, Karina L, Byrne, Michael T., Sengsayadeth, Salyka M., Goodman, Stacey Ann, Dholaria, Bhagirathbhai, Savani, Bipin N., Chinratanalab, Wichai, Jayani, Reena, Connelly, Jim, Kitko, Carrie, Engelhardt, Brian G., Kassim, Adetola A.
Published in Blood (05.11.2020)
Published in Blood (05.11.2020)
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Journal Article
Single-Cell Transcriptional Landscapes of Human Bone Marrow Reveal Distinct Erythroid Phenotypes Underpinned By Genotype in Diamond-Blackfan Anemia
Iskander, Deena, Wang, Guanlin, Heuston, Elisabeth F, Christodoulidou, Chrysi, Psaila, Bethan, Robinson, Mark E, Chaidos, Aristeidis, Trivedi, Pritesh, Trasanidis, Nikolaos, Katsarou, Alexia, Szydlo, Richard, SequencingProgram, NISC Comparative, Al-Oqaily, Qais, Caputo, Valentina S, Ponnusamy, Kanagaraju, Roy, Anindita, Karnik, Leena, Naresh, Kikkeri, Mead, Adam J., Thongjuea, Supat, Brand, Marjorie, de la Fuente, Josu, Bodine, David M., Roberts, Irene, Karadimitris, Anastasios
Published in Blood (05.11.2020)
Published in Blood (05.11.2020)
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Journal Article
Fludarabine/Treosulfan/Thiotepa/ATG Conditioning for Related Transplantation in Haemoglobinopathies Leads to Early and Sustanined Engraftment with Low Incidence of VOD and GvHD
O'Boyle, Farah, Hing, Sandra, Harrington, Yvonne, Chakravorty, Subarna, Karnik, Leena, New, Helen, Bradshaw, Anne, Szydlo, Richard, de la Fuente, Josu
Published in Blood (03.12.2015)
Published in Blood (03.12.2015)
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Journal Article
Outcomes of Non-Myeloablative HLA-Haploidentical Bone Marrow Transplant with Thiotepa and Post-Transplant Cyclophosphamide in Children and Adults with Severe Sickle Cell Disease, a Phase II Trial: Vanderbilt Global Haploidentical Transplant Learning Collaborative (VGC2)
Kassim, Adetola A., de la Fuente, Josu, Alahmari, Ali Debsan, Eckrich, Michael J., Hanna, Rabi, Dhedin, Nathalie, Horn, Biljana N., Black, Vandy, Gouveia, Roseane V, Seber, Adriana, Simões, Belinda Pinto, Costa, Thalita Cristina de Mello, Guerino-Cunha, Renato, Bonfim, Carmem M.S., da Silva, Roberto Luiz, Hamerschlak, Nelson, Fernandes, Juliana Folloni, Kent, Michael, Yadav, Satya Prakash, Nur, Erfan, Alzahrani, Mohsen, Carpenter, Ben, Tse, William, Isabel, Maria, Rangarajan, Hemalatha G, Ahmed, Ibrahim, Akinsete, Adeseye Michael, Fitzhugh, Courtney D., Culos, Kathryn A., Karnik, Leena, Connelly, James, Kitko, Carrie, Andrews, Jennifer, Wilkerson, Karina L, Brodsky, Robert, Koyama, Tatsuki, DeBaun, Michael R.
Published in Blood (05.11.2020)
Published in Blood (05.11.2020)
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Haploidentical Bone Marrow Transplant with Post-Transplant Cytoxan Plus Thiotepa Improves Donor Engraftment in Patients with Sickle Cell Anemia: Results of an International Multicenter Learning Collaborative
Dhedin, Nathalie, de la Fuente, Josu, Bernaudin, Francoise, Kuentz, Mathieu, Karnik, Leena, Koyama, Tatsuki, Brodsky, Robert A., DeBaun, Michael, Kassim, Adetola A.
Published in Blood (02.12.2016)
Published in Blood (02.12.2016)
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Journal Article
389 - The Combination of Rituximab, Plasmapheresis, Intravenous Immunoglobulins and Pre-Transplant Immunosuppression Is an Effective Desensitization Strategy for Patients with Sickle Cell Disease and High Donor Specific Anti-Human Leukocyte Antigen Titer Undergoing Haploidentical Bone Marrow Transplant
Biltibo, Eden, Jayani, Reena V, Karnik, Leena, Gassas, Adam, O’Boyle, Farah, Wilkerson, Karina, Gatwood, Katie S., Orton, Lindsay, Dholaria, Bhagirathbhai, Savani, Bipin, Engelhardt, Brian G., Sengsayadeth, Salyka, Kitko, Carrie L., Connelly, James A, Kassim, Adetola A., de la Fuente, Josu
Published in Transplantation and cellular therapy (01.02.2023)
Published in Transplantation and cellular therapy (01.02.2023)
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Journal Article
The Combination of Rituximab, Plasmapheresis, Intravenous Immunoglobulins and Pre-Transplant Immunosuppression Is an Effective Desensitization Strategy for Patients with Sickle Cell Disease and High Donor Specific Anti-Human Leukocyte Antigen Titer Undergoing Haploidentical Bone Marrow Transplant
Biltibo, Eden, Jayani, Reena V, Karnik, Leena, Gassas, Adam, O’Boyle, Farah, Wilkerson, Karina, Gatwood, Katie S., Orton, Lindsay, Dholaria, Bhagirathbhai, Savani, Bipin, Engelhardt, Brian G., Sengsayadeth, Salyka, Kitko, Carrie L., Connelly, James A, Kassim, Adetola A., de la Fuente, Josu
Published in Transplantation and cellular therapy (01.02.2023)
Published in Transplantation and cellular therapy (01.02.2023)
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