A Phase 3 Randomized Trial of Voxelotor in Sickle Cell Disease
Vichinsky, Elliott, Hoppe, Carolyn C, Ataga, Kenneth I, Ware, Russell E, Nduba, Videlis, El-Beshlawy, Amal, Hassab, Hoda, Achebe, Maureen M, Alkindi, Salam, Brown, R. Clark, Diuguid, David L, Telfer, Paul, Tsitsikas, Dimitris A, Elghandour, Ashraf, Gordeuk, Victor R, Kanter, Julie, Abboud, Miguel R, Lehrer-Graiwer, Joshua, Tonda, Margaret, Intondi, Allison, Tong, Barbara, Howard, Jo
Published in The New England journal of medicine (08.08.2019)
Published in The New England journal of medicine (08.08.2019)
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Journal Article
Biologic and Clinical Efficacy of LentiGlobin for Sickle Cell Disease
Kanter, Julie, Walters, Mark C, Krishnamurti, Lakshmanan, Mapara, Markus Y, Kwiatkowski, Janet L, Rifkin-Zenenberg, Stacey, Aygun, Banu, Kasow, Kimberly A, Pierciey, Francis J, Bonner, Melissa, Miller, Alex, Zhang, Xinyan, Lynch, Jessie, Kim, Dennis, Ribeil, Jean-Antoine, Asmal, Mohammed, Goyal, Sunita, Thompson, Alexis A, Tisdale, John F
Published in The New England journal of medicine (17.02.2022)
Published in The New England journal of medicine (17.02.2022)
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Journal Article
Crizanlizumab for the Prevention of Pain Crises in Sickle Cell Disease
Ataga, Kenneth I, Kutlar, Abdullah, Kanter, Julie, Liles, Darla, Cancado, Rodolfo, Friedrisch, João, Guthrie, Troy H, Knight-Madden, Jennifer, Alvarez, Ofelia A, Gordeuk, Victor R, Gualandro, Sandra, Colella, Marina P, Smith, Wally R, Rollins, Scott A, Stocker, Jonathan W, Rother, Russell P
Published in The New England journal of medicine (02.02.2017)
Published in The New England journal of medicine (02.02.2017)
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Journal Article
Perspectives of individuals with sickle cell disease on barriers to care
Phillips, Shannon, Chen, Yumei, Masese, Rita, Noisette, Laurence, Jordan, Kasey, Jacobs, Sara, Hsu, Lewis L, Melvin, Cathy L, Treadwell, Marsha, Shah, Nirmish, Tanabe, Paula, Kanter, Julie
Published in PloS one (23.03.2022)
Published in PloS one (23.03.2022)
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Journal Article
Salvage therapy of refractory hemophagocytic lymphohistiocytosis with alemtuzumab
Marsh, Rebecca A., Allen, Carl E., McClain, Kenneth L., Weinstein, Joanna L., Kanter, Julie, Skiles, Jodi, Lee, Nadine D., Khan, Shakila P., Lawrence, Julia, Mo, Jun Q., Bleesing, Jack J., Filipovich, Alexandra H., Jordan, Michael B.
Published in Pediatric blood & cancer (01.01.2013)
Published in Pediatric blood & cancer (01.01.2013)
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Journal Article
Current and novel therapies for the prevention of vaso-occlusive crisis in sickle cell disease
Osunkwo, Ifeyinwa, Manwani, Deepa, Kanter, Julie
Published in Therapeutic Advances in Hematology (2020)
Published in Therapeutic Advances in Hematology (2020)
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Book Review
Journal Article
Density-based separation in multiphase systems provides a simple method to identify sickle cell disease
Kumar, Ashok A., Patton, Matthew R., Hennek, Jonathan W., Lee, Si Yi Ryan, D'Alesio-Spina, Gaetana, Yang, Xiaoxi, Kanter, Julie, Shevkoplyas, Sergey S., Brugnara, Carlo, Whitesides, George M.
Published in Proceedings of the National Academy of Sciences - PNAS (14.10.2014)
Published in Proceedings of the National Academy of Sciences - PNAS (14.10.2014)
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Journal Article
Lovo‐cel gene therapy for sickle cell disease: Treatment process evolution and outcomes in the initial groups of the HGB‐206 study
Kanter, Julie, Thompson, Alexis A., Pierciey, Francis J., Hsieh, Matthew, Uchida, Naoya, Leboulch, Philippe, Schmidt, Manfred, Bonner, Melissa, Guo, Ruiting, Miller, Alex, Ribeil, Jean‐Antoine, Davidson, David, Asmal, Mohammed, Walters, Mark C., Tisdale, John F.
Published in American journal of hematology (01.01.2023)
Published in American journal of hematology (01.01.2023)
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Journal Article
Factors associated with left ventricular hypertrophy in children with sickle cell disease; results from the DISPLACE study
Galadanci, Najibah A, Johnson, Walter, Carson, April, Hellemann, Gerhard, Howard, Virginia, Kanter, Julie
Published in Haematologica (Roma) (01.10.2022)
Published in Haematologica (Roma) (01.10.2022)
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Journal Article
Sex-based differences in the manifestations and complications of sickle cell disease: Report from the Sickle Cell Disease Implementation Consortium
Masese, Rita V, Bulgin, Dominique, Knisely, Mitchell R, Preiss, Liliana, Stevenson, Eleanor, Hankins, Jane S, Treadwell, Marsha J, King, Allison A, Gordeuk, Victor R, Kanter, Julie, Gibson, Robert, Glassberg, Jeffrey A, Tanabe, Paula, Shah, Nirmish
Published in PloS one (29.10.2021)
Published in PloS one (29.10.2021)
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Journal Article
Current Methods of Newborn Screening Follow-Up for Sickle Cell Disease Are Highly Variable and without Quality Assurance: Results from the ENHANCE Study
Galadanci, Najibah, Phillips, Shannon, Schlenz, Alyssa, Ivankova, Nataliya, Kanter, Julie
Published in International journal of neonatal screening (01.03.2024)
Published in International journal of neonatal screening (01.03.2024)
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Journal Article
Publication of data collection forms from NHLBI funded sickle cell disease implementation consortium (SCDIC) registry
Glassberg, Jeffrey A, Linton, Elizabeth A, Burson, Katrina, Hendershot, Tabitha, Telfair, Joseph, Kanter, Julie, Gordeuk, Victor R, King, Allison A, Melvin, Cathy L, Shah, Nirmish, Hankins, Jane S, Epié, Axel Yannick, Richardson, Lynne D
Published in Orphanet journal of rare diseases (07.07.2020)
Published in Orphanet journal of rare diseases (07.07.2020)
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Journal Article
Validation of a Low-Cost Paper-Based Screening Test for Sickle Cell Anemia
Piety, Nathaniel Z, Yang, Xiaoxi, Kanter, Julie, Vignes, Seth M, George, Alex, Shevkoplyas, Sergey S
Published in PloS one (06.01.2016)
Published in PloS one (06.01.2016)
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Journal Article
Identifying barriers to evidence-based care for sickle cell disease: results from the Sickle Cell Disease Implementation Consortium cross-sectional survey of healthcare providers in the USA
Smeltzer, Matthew P, Howell, Kristen E, Treadwell, Marsha, Preiss, Liliana, King, Allison A, Glassberg, Jeffrey A, Tanabe, Paula, Badawy, Sherif M, DiMartino, Lisa, Gibson, Robert, Kanter, Julie, Klesges, Lisa M, Hankins, Jane S
Published in BMJ open (17.11.2021)
Published in BMJ open (17.11.2021)
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Journal Article
PB2524: TRIAL IN PROGRESS: THE HIBISCUS‐KIDS STUDY, A SINGLE‐ARM, OPEN‐LABEL, PHASE 1/2 STUDY TO EVALUATE THE PHARMACOKINETICS AND SAFETY OF ETAVOPIVAT IN PEDIATRIC PATIENTS WITH SICKLE CELL DISEASE
Colombatti, Raffaella, Kanter, Julie, Wu, Eric, Clay, Leila J., Campbell, Andrew
Published in HemaSphere (08.08.2023)
Published in HemaSphere (08.08.2023)
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Journal Article
Social determinants of health and treatment center affiliation: analysis from the sickle cell disease implementation consortium registry
Mendez, Gustavo G, Nocek, Judith M, Brambilla, Donald J, Jacobs, Sara, Cole, Oladipo, Kanter, Julie, Glassberg, Jeffrey, Saving, Kay L, Melvin, Cathy L, Gibson, Robert W, Treadwell, Marsha, Jackson, George L, King, Allison A, Gordeuk, Victor R, Kroner, Barbara, Hsu, Lewis L
Published in BMC health services research (06.03.2024)
Published in BMC health services research (06.03.2024)
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Journal Article