BAX 335 hemophilia B gene therapy clinical trial results: potential impact of CpG sequences on gene expression
Konkle, Barbara A., Walsh, Christopher E., Escobar, Miguel A., Josephson, Neil C., Young, Guy, von Drygalski, Annette, McPhee, Scott W.J., Samulski, R. Jude, Bilic, Ivan, de la Rosa, Maurus, Reipert, Birgit M., Rottensteiner, Hanspeter, Scheiflinger, Friedrich, Chapin, John C., Ewenstein, Bruce, Monahan, Paul E.
Published in Blood (11.02.2021)
Published in Blood (11.02.2021)
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Phase 3 study of recombinant factor VIII Fc fusion protein in severe hemophilia A
Mahlangu, Johnny, Powell, Jerry S., Ragni, Margaret V., Chowdary, Pratima, Josephson, Neil C., Pabinger, Ingrid, Hanabusa, Hideji, Gupta, Naresh, Kulkarni, Roshni, Fogarty, Patrick, Perry, David, Shapiro, Amy, Pasi, K. John, Apte, Shashikant, Nestorov, Ivan, Jiang, Haiyan, Li, Shuanglian, Neelakantan, Srividya, Cristiano, Lynda M., Goyal, Jaya, Sommer, Jurg M., Dumont, Jennifer A., Dodd, Nigel, Nugent, Karen, Vigliani, Gloria, Luk, Alvin, Brennan, Aoife, Pierce, Glenn F.
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Connors, Joseph M, Jurczak, Wojciech, Straus, David J, Ansell, Stephen M, Kim, Won S, Gallamini, Andrea, Younes, Anas, Alekseev, Sergey, Illés, Árpád, Picardi, Marco, Lech-Maranda, Ewa, Oki, Yasuhiro, Feldman, Tatyana, Smolewski, Piotr, Savage, Kerry J, Bartlett, Nancy L, Walewski, Jan, Chen, Robert, Ramchandren, Radhakrishnan, Zinzani, Pier L, Cunningham, David, Rosta, Andras, Josephson, Neil C, Song, Eric, Sachs, Jessica, Liu, Rachael, Jolin, Hina A, Huebner, Dirk, Radford, John
Published in The New England journal of medicine (25.01.2018)
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Brentuximab vedotin plus bendamustine: a highly active first salvage regimen for relapsed or refractory Hodgkin lymphoma
LaCasce, Ann S., Bociek, R. Gregory, Sawas, Ahmed, Caimi, Paolo, Agura, Edward, Matous, Jeffrey, Ansell, Stephen M., Crosswell, Howland E., Islas-Ohlmayer, Miguel, Behler, Caroline, Cheung, Eric, Forero-Torres, Andres, Vose, Julie, O'Connor, Owen A., Josephson, Neil, Wang, Yinghui, Advani, Ranjana
Published in Blood (05.07.2018)
Published in Blood (05.07.2018)
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Safety and prolonged activity of recombinant factor VIII Fc fusion protein in hemophilia A patients
Powell, Jerry S., Josephson, Neil C., Quon, Doris, Ragni, Margaret V., Cheng, Gregory, Li, Ella, Jiang, Haiyan, Li, Lian, Dumont, Jennifer A., Goyal, Jaya, Zhang, Xin, Sommer, Jurg, McCue, Justin, Barbetti, Margaret, Luk, Alvin, Pierce, Glenn F.
Published in Blood (29.03.2012)
Published in Blood (29.03.2012)
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Results of genetic analysis of 11 341 participants enrolled in the My Life, Our Future hemophilia genotyping initiative in the United States
Johnsen, Jill M., Fletcher, Shelley N., Dove, Angela, McCracken, Haley, Martin, Beth K., Kircher, Martin, Josephson, Neil C., Shendure, Jay, Ruuska, Sarah E., Valentino, Leonard A., Pierce, Glenn F., Watson, Crystal, Cheng, Dunlei, Recht, Michael, Konkle, Barbara A.
Published in Journal of thrombosis and haemostasis (01.09.2022)
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Recombinant factor IX-Fc fusion protein (rFIXFc) demonstrates safety and prolonged activity in a phase 1/2a study in hemophilia B patients
Shapiro, Amy D., Ragni, Margaret V., Valentino, Leonard A., Key, Nigel S., Josephson, Neil C., Powell, Jerry S., Cheng, Gregory, Thompson, Arthur R., Goyal, Jaya, Tubridy, Karen L., Peters, Robert T., Dumont, Jennifer A., Euwart, Donald, Li, Lian, Hallén, Bengt, Gozzi, Peter, Bitonti, Alan J., Jiang, Haiyan, Luk, Alvin, Pierce, Glenn F.
Published in Blood (19.01.2012)
Published in Blood (19.01.2012)
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Novel approach to genetic analysis and results in 3000 hemophilia patients enrolled in the My Life, Our Future initiative
Johnsen, Jill M., Fletcher, Shelley N., Huston, Haley, Roberge, Sarah, Martin, Beth K., Kircher, Martin, Josephson, Neil C., Shendure, Jay, Ruuska, Sarah, Koerper, Marion A., Morales, Jaime, Pierce, Glenn F., Aschman, Diane J., Konkle, Barbara A.
Published in Blood advances (23.05.2017)
Published in Blood advances (23.05.2017)
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Recombinant factor VIII Fc (rFVIIIFc) fusion protein reduces immunogenicity and induces tolerance in hemophilia A mice
Krishnamoorthy, Sriram, Liu, Tongyao, Drager, Douglas, Patarroyo-White, Susannah, Chhabra, Ekta Seth, Peters, Robert, Josephson, Neil, Lillicrap, David, Blumberg, Richard S., Pierce, Glenn F., Jiang, Haiyan
Published in Cellular immunology (01.03.2016)
Published in Cellular immunology (01.03.2016)
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Long‐acting recombinant factor IX Fc fusion protein (rFIXFc) for perioperative management of subjects with haemophilia B in the phase 3 B‐LONG study
Powell, Jerry S., Apte, Shashikant, Chambost, Hervé, Hermans, Cedric, Jackson, Shannon, Josephson, Neil C., Mahlangu, Johnny N., Ozelo, Margareth C., Peerlinck, Kathelijne, Pasi, John, Perry, David, Ragni, Margaret V., Wang, Xuefeng, Jiang, Haiyan, Li, Shuanglian, Cristiano, Lynda M., Innes, Alison, Nugent, Karen, Brennan, Aoife, Luk, Alvin, Allen, Geoffrey, Pierce, Glenn F., Robinson, Brian
Published in British journal of haematology (01.01.2015)
Published in British journal of haematology (01.01.2015)
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Phenotypes of allo- and autoimmune antibody responses to FVIII characterized by surface plasmon resonance
Lewis, Kenneth B, Hughes, Richard J, Epstein, Melinda S, Josephson, Neil C, Kempton, Christine L, Kessler, Craig M, Key, Nigel S, Howard, Tom E, Kruse-Jarres, Rebecca, Lusher, Jeanne M, Walsh, Christopher E, Watts, Raymond G, Ettinger, Ruth A, Pratt, Kathleen P
Published in PloS one (08.05.2013)
Published in PloS one (08.05.2013)
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Incomplete restoration of Mpl expression in the mpl−/− mouse produces partial correction of the stem cell–repopulating defect and paradoxical thrombocytosis
Lannutti, Brian J., Epp, Angela, Roy, Jacqueline, Chen, Junmei, Josephson, Neil C.
Published in Blood (19.02.2009)
Published in Blood (19.02.2009)
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Real-world economic burden of hematopoietic cell transplantation among a large US commercially insured population with hematologic malignancies
Bonafede, Machaon, Richhariya, Akshara, Cai, Qian, Josephson, Neil C, McMorrow, Donna, Garfin, Phillip M, Perales, Miguel-Angel
Published in Journal of medical economics (02.12.2017)
Published in Journal of medical economics (02.12.2017)
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Phase 3 Study of Recombinant Factor IX Fc Fusion Protein in Hemophilia B
Powell, Jerry S, Pasi, K. John, Ragni, Margaret V, Ozelo, Margareth C, Valentino, Leonard A, Mahlangu, Johnny N, Josephson, Neil C, Perry, David, Manco-Johnson, Marilyn J, Apte, Shashikant, Baker, Ross I, Chan, Godfrey C, Novitzky, Nicolas, Wong, Raymond S, Krassova, Snejana, Allen, Geoffrey, Jiang, Haiyan, Innes, Alison, Li, Shuanglian, Cristiano, Lynda M, Goyal, Jaya, Sommer, Jurg M, Dumont, Jennifer A, Nugent, Karen, Vigliani, Gloria, Brennan, Aoife, Luk, Alvin, Pierce, Glenn F
Published in The New England journal of medicine (12.12.2013)
Published in The New England journal of medicine (12.12.2013)
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Suppression of the Immune Response to FVIII in Hemophilia A Mice by Transgene Modified Tolerogenic Dendritic Cells
Su, Rui-Jun, Epp, Angela, Feng, Junli, Roy, Jackie, Latchman, Yvette, Wu, Xiaoping, Bolgiano, Doug, Josephson, Neil C
Published in Molecular therapy (01.10.2011)
Published in Molecular therapy (01.10.2011)
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Proteomic analysis of the androgen receptor via MS-compatible purification of biotinylated protein on streptavidin resin
Austin, Ryan J., Smidansky, Heidi M., Holstein, Carly A., Chang, Deborah K., Epp, Angela, Josephson, Neil C., Martin, Daniel B.
Published in Proteomics (Weinheim) (01.01.2012)
Published in Proteomics (Weinheim) (01.01.2012)
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Transduction of Human NOD/SCID-Repopulating Cells with Both Lymphoid and Myeloid Potential by Foamy Virus Vectors
Josephson, Neil C., Vassilopoulos, George, Trobridge, Grant D., Priestley, Greg V., Wood, Brent L., Papayannopoulou, Thalia, Russell, David W.
Published in Proceedings of the National Academy of Sciences - PNAS (11.06.2002)
Published in Proceedings of the National Academy of Sciences - PNAS (11.06.2002)
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