rAAV8-PC Gene Therapy for Severe Protein C Deficiency Using a Novel Murine Model
Levy-Mendelovich, Sarina, Avishai, Einat, Samelson-Jones, Ben J, Dardik, Rima, barazani-Brutman, Tami, Nisgav, Yael, Livnat, Tami, Kenet, Gili
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Journal Article
Factor VIII Mimetic Rescue of Hemophilia B Causing Factor IX Variants
Lee, Kyumin, Chau, Julia Q, Sternberg, Anna R, Pishko, Allyson M, George, Lindsey, Samelson-Jones, Ben J
Published in Blood (15.11.2022)
Published in Blood (15.11.2022)
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Journal Article
Long-Term Real-World Safety and Efficacy of Liver-Directed AAV Gene Therapy for Severe Hemophilia with and without Inbibitors in Privately Owned Dogs
Doshi, Bhavya S, Samelson-Jones, Ben J, Nichols, Timothy C, Merricks, Elizabeth P, Arruda, Valder R, Callan, Mary Beth
Published in Blood (15.11.2022)
Published in Blood (15.11.2022)
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Journal Article
Ontogeny of the Alloimmune Anti-Canine Factor VIII Inhibitor Response in Severe Hemophilia Α Dogs
Chen, Robert, Doshi, Bhavya S, Nichols, Timothy C., Milone, Michael C., Samelson-Jones, Ben J., Arruda, Valder R, Bhoj, Vijay, Siegel, Don L.
Published in Blood (23.11.2021)
Published in Blood (23.11.2021)
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Journal Article
Gene therapy for immune tolerance induction in hemophilia with inhibitors
Arruda, V. R., Samelson‐Jones, B. J.
Published in Journal of thrombosis and haemostasis (01.06.2016)
Published in Journal of thrombosis and haemostasis (01.06.2016)
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Journal Article
Leveraging CAR T cells to Achieve Desensitization and Enable Transplantation
Markmann, Caroline Anna, Zheng, Zheng, Yu, Ming, Rostami, Susan, Wang, Wei, Ochoa, Trini, Parvathaneni, Kalpana, Xu, Xiaoming, Scholler, John, Zhang, Qian, Posey, Avery, Allman, David, Milone, Michael, Arruda, Valder, Jones, Ben Samelson, Naji, Ali, Bhoj, Vijay
Published in The Journal of immunology (1950) (01.05.2022)
Published in The Journal of immunology (1950) (01.05.2022)
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Journal Article
Health-Related Quality of Life in Adults with Hemophilia B after Receiving Gene Therapy with Fidanacogene Elaparvovec
von Mackensen, Sylvia, Ducore, Jonathan M., George, Lindsey A., Giermasz, Adam, McGuinn, Catherine, Rasko, John E. J., Samelson-Jones, Ben J, Sullivan, Spencer K., Teitel, Jerome M., Chhabra, Amit, Fang, Annie F., O'Brien, Amanda, Plonski, Frank, Rupon, Jeremy, Smith, Lynne, Winburn, Ian
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Journal Article
Follow-up of More Than 5 Years in a Cohort of Patients with Hemophilia B Treated with Fidanacogene Elaparvovec Adeno-Associated Virus Gene Therapy
Samelson-Jones, Ben J., Sullivan, Spencer K., Rasko, John E.J., Giermasz, Adam, George, Lindsey A., Ducore, Jonathan M., Teitel, Jerome M., McGuinn, Catherine E., O'Brien, Amanda, Winburn, Ian, Smith, Lynne M, Chhabra, Amit, Rupon, Jeremy
Published in Blood (23.11.2021)
Published in Blood (23.11.2021)
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Journal Article
New Hyperactive Factor IX Variants Bioengineered Based upon Biochemical Studies of Factor IX Padua
Samelson-Jones, Ben J., Finn, Jonathan D, Camire, Rodney M., Arruda, Valder R
Published in Blood (02.12.2016)
Published in Blood (02.12.2016)
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Journal Article
Regulation of Factor VIII By Activated Protein C: Assessment In Vitro and In Vivo
Parsons, Nicole A., Ho, Michelle D., Davidson, Robert J., Thalji, Nabil K., Samelson-Jones, Ben J., Camire, Rodney M, George, Lindsey A.
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Journal Article
Spk-9001: Adeno-Associated Virus Mediated Gene Transfer for Hemophilia B Achieves Sustained Factor IX with Minimal Immune Response
Hui, Daniel J, Liu, Yun, Patel, Ruchi, Chen, Yifeng, George, Lindsey A., Sullivan, Spencer K., Giermasz, Adam, Rasko, John, Samelson-Jones, Ben J., Ducore, Jonathan M., Dasen, Sue, Carr, Marcus E., Anguela, Xavier M., High, Katherine A.
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Journal Article
A Phase 1/2 Trial of Investigational Spk-8011 in Hemophilia a Demonstrates Durable Expression and Prevention of Bleeds
High, Katherine A., George, Lindsey A., Eyster, M. Elaine, Sullivan, Spencer K., Ragni, Margaret V., Croteau, Stacy E., Samelson-Jones, Ben J., Evans, Matthew, Joseney-Antoine, Marcelyne, Macdougall, Amy, Kadosh, Judith, Runoski, Alexa R., Campbell-Baird, Cynthia, Douglas, Kayla, Tompkins, Summer, Hait, Howard, Couto, Linda B., Bassiri, Ashlyn Eaton, Valentino, Leonard A., Carr, Marcus E., Hui, Daniel J, Wachtel, Katie, Takefman, Daniel, Mingozzi, Federico, Anguela, Xavier M., Reape, Kathleen B
Published in Blood (29.11.2018)
Published in Blood (29.11.2018)
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Journal Article