Eptacog beta for the management of patients with haemophilia A and B with inhibitors: A European perspective
Miesbach, Wolfgang, Carcao, Manuel, Mahlangu, Johnny, Dargaud, Yesim, Jimenez‐Yuste, Victor, Hermans, Cédric
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.03.2024)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.03.2024)
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Journal Article
Global Seroprevalence of Pre-existing Immunity Against AAV5 and Other AAV Serotypes in People with Hemophilia A
Klamroth, Robert, Hayes, Gregory, Andreeva, Tatiana, Gregg, Keith, Suzuki, Takashi, Mitha, Ismail Haroon, Hardesty, Brandon, Shima, Midori, Pollock, Toni, Slev, Patricia, Oldenburg, Johannes, Ozelo, Margareth C, Stieltjes, Natalie, Castet, Sabine-Marie, Mahlangu, Johnny, Peyvandi, Flora, Kazmi, Rashid, Schved, Jean-François, Leavitt, Andrew D, Callaghan, Michael, Pan-Petesch, Brigitte, Quon, Doris V, Andrews, Jayson, Trinh, Alex, Li, Mingjin, Wong, Wing Yen
Published in Human gene therapy (01.04.2022)
Published in Human gene therapy (01.04.2022)
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Journal Article
A randomized, placebo-controlled, double-blind trial of canakinumab in children and young adults with sickle cell anemia
Rees, David C., Kilinc, Yurdanur, Unal, Selma, Dampier, Carlton, Pace, Betty S., Kaya, Banu, Trompeter, Sara, Odame, Isaac, Mahlangu, Johnny, Unal, Sule, Brent, Julie, Grosse, Regine, Fuh, Beng R., Inusa, Baba P.D., Koren, Ariel, Leblebisatan, Goksel, Levin, Carina, McNamara, Elizabeth, Meiser, Karin, Hom, Douglas, Oliver, Stephen J.
Published in Blood (28.04.2022)
Published in Blood (28.04.2022)
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Journal Article
Recommendations for a minimum data set for monitoring gene therapy in hemophilia: communication from the ISTH SSC Working Group on Gene Therapy
Miesbach, Wolfgang, Konkle, Barbara, Chowdary, Pratima, Kaczmarek, Radoslaw, Leebeek, Frank, Mahlangu, Johnny, Makris, Michael, Pipe, Steven W., Srivastava, Alok, Voorberg, Jan, Pierce, Glenn F., Peyvandi, Flora
Published in Journal of thrombosis and haemostasis (01.05.2024)
Published in Journal of thrombosis and haemostasis (01.05.2024)
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Journal Article
Trials in Progress: The Randomized, Double-Blind, Placebo-Controlled Phase 1b CROSSWALK-a and Phase 2a CROSSWALK-c Trials - Crovalimab for the Treatment and Prevention of Vaso-Occlusive Episodes in Sickle Cell Disease
Salvino, Marco Aurelio, Antmen, Bulent, Chite Asirwa, Frederick, Chonat, Satheesh, De Franceschi, Lucia, Eleftheriou, Perla, Inati, Adlette, Mahlangu, Johnny, Nur, Erfan, Payán-Pernía, Salvador, Charania, Asad, Gradinaru, Diana, Hsia, Allison, Luder, Yves, Perretti, Thomas, Srekovic, Sasha, Bartolucci, Pablo
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Journal Article
Phase 3 Trial of Concizumab in Hemophilia with Inhibitors
Matsushita, Tadashi, Shapiro, Amy, Abraham, Aby, Angchaisuksiri, Pantep, Castaman, Giancarlo, Cepo, Katarina, d’Oiron, Roseline, Frei-Jones, Melissa, Goh, Ai-Sim, Haaning, Jesper, Hald Jacobsen, Sanja, Mahlangu, Johnny, Mathias, Mary, Nogami, Keiji, Skovgaard Rasmussen, Josephine, Stasyshyn, Oleksandra, Tran, Huyen, Vilchevska, Kateryna, Villarreal Martinez, Laura, Windyga, Jerzy, You, Chur Woo, Zozulya, Nadezhda, Zulfikar, Bulent, Jiménez-Yuste, Victor
Published in The New England journal of medicine (31.08.2023)
Published in The New England journal of medicine (31.08.2023)
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Journal Article
Compound Homozygous Factor V Leiden and Heterozygous Prothrombin Gene Mutation: The First Report in a Pregnant African with Extensive Thrombosis
Dogara, Livingstone Gayus, Ovosi, Joseph Ogirima, Mohammed, Caleb, Farouk, Bilkisu, Mafika, Ziphozonke, Mahlangu, Johnny
Published in Blood (29.11.2018)
Published in Blood (29.11.2018)
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Journal Article
World federation of hemophilia international hemophilia training fellowship program: 50 years of enhancing global care
Escobar, Miguel A., Beijlevelt, Marlène, Loney, Aleah, Mahlangu, Johnny, Nanayakkara, Lochana, Neme, Daniela, Pasta, Gianluigi, Toulon, Pierre, Tran, Huyen
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.09.2022)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.09.2022)
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Journal Article
Eptacog Beta (rFVIIa) Has a Low Incidence of Spontaneous Rebleeding through 24 and 48 Hours in Adult and Adolescent Patients with Hemophilia A or B with Inhibitors
Dunn, Amy L., Dargaud, Yesim, Abajas, Yasmina L., Carcao, Manuel, Castaman, Giancarlo, Giermasz, Adam, Hermans, Cédric, Lewandowska, Magdalena D., Mahlangu, Johnny, Meeks, Shannon L., Miesbach, Wolfgang A., Recht, Michael, Salinas, Vanessa, Chrisentery-Singleton, Tammuella, Wang, Hongying, Mitchell, Ian S, Young, Guy
Published in Blood (15.11.2022)
Published in Blood (15.11.2022)
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Journal Article
Seroprevalence of Pre-Existing Nabs Against AAV1, 2, 5, 6 and 8 in South African Hemophilia B Patient Population
Majowicz, Anna, Ncete, Nolukholo, van Waes, Floris, Timmer, Nikki, van Deventer, Sander J, Mahlangu, Johnny N, Ferreira, Valerie
Published in Blood (13.11.2019)
Published in Blood (13.11.2019)
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Journal Article
Long‐term safety and sustained efficacy for up to 5 years of treatment with recombinant factor IX Fc fusion protein in subjects with haemophilia B: Results from the B‐YOND extension study
Pasi, K. John, Fischer, Kathelijn, Ragni, Margaret, Kulkarni, Roshni, Ozelo, Margareth C., Mahlangu, Johnny, Shapiro, Amy, P’Ng, Stephanie, Chambost, Hervé, Nolan, Beatrice, Bennett, Carolyn, Matsushita, Tadashi, Winding, Bent, Fruebis, Joachim, Yuan, Huixing, Rudin, Dan, Oldenburg, Johannes
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2020)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2020)
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Journal Article
Stable Therapeutic Transgenic FIX Levels for More Than 10 Years in Subjects with Severe Hemophilia B Who Received scAAV2/8-LP1-Hfixco Adeno-Associated Virus Gene Therapy
Reiss, Ulrike M., Davidoff, Andrew M., Tuddenham, Edward G. D., Chowdary, Pratima, McIntosh, Jenny H., Riddell, Anne, Pie, Arnulfo, Batty, Paul, Calvert, Joanna C. M., Mangles, Sarah, Mahlangu, Johnny, Haley, Kristina M., Recht, Michael, Shen, Yu-Min, Halka, Kathleen G., Zhou, Junfang, Kang, Guolian, Okhomina, Victoria, Morton, Christopher L, Nathwani, Amit C.
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Journal Article
Low Rebleed Incidence with Eptacog Beta Treatment through 24 and 48 Hours in Children (<12 years) with Hemophilia a or B with Inhibitors
Pipe, Steven, Oldenburg, Johannes, Carcao, Manuel, Chitlur, Meera, Dargaud, Yesim, Davis, Joanna, Escuriola, Carmen, Hay, Charles, Hermans, Cédric, Hwang, Nina, Jiménez-Yuste, Víctor, Kessler, Craig, Mahlangu, Johnny, Mancuso, Maria Elisa, McGuinn, Catherine, Miesbach, Wolfgang, Chrisentery-Singleton, Tammuella, Thornburg, Courtney, Wang, Michael, Bonzo, Daniel, Mitchell, Ian, Wilkinson, Thomas, Dunn, Amy
Published in Blood (02.11.2023)
Published in Blood (02.11.2023)
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Journal Article
Emicizumab is efficacious in people with hemophilia A with comorbidities aged ≥50 years: analysis of 4 phase III trials
Jiménez-Yuste, Víctor, Oldenburg, Johannes, Tzeng, Eunice, Lim, Elise, Sanabria, Fabian, Mahlangu, Johnny
Published in Research and practice in thrombosis and haemostasis (01.03.2024)
Published in Research and practice in thrombosis and haemostasis (01.03.2024)
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Journal Article
Emicizumab Prophylaxis in Persons with Mild or Moderate Hemophilia A: Results from the Interim Analysis of the HAVEN 6 Study
Négrier, Claude, Mahlangu, Johnny, Lehle, Michaela, Chowdary, Pratima, Catalani, Olivier, Jiménez-Yuste, Víctor, Beckermann, Benjamin M., Schmitt, Christophe, Hermans, Cedric, Ventriglia, Giuliana, Windyga, Jerzy, Kiialainen, Anna, d'Oiron, Roseline, Moorehead, Paul, Teodoro, Vanda, Shapiro, Amy D., Oldenburg, Johannes
Published in Blood (23.11.2021)
Published in Blood (23.11.2021)
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Journal Article
Switching from Sucrose-Formulated rFVIII to Octocog Alfa
Moulton, Thomas, Mahlangu, Johnny, Kenet, Gili, Wicklund, Brian M, Escobar, Miguel, Ahuja, Sanjay P
Published in Journal of blood medicine (30.06.2023)
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Published in Journal of blood medicine (30.06.2023)
Journal Article
A cohort study of the relationship between anaemia, mean corpuscular volume and mortality among a CKD population in South Africa
Nalado, Aishatu, Waziri, Bala, Olorunfemi, Gbenga, Mahlangu, Johnny, Paget, Graham, Duarte, Raquel, Naicker, Saraladevi
Published in African health sciences (01.12.2021)
Published in African health sciences (01.12.2021)
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Journal Article
Implementation of a gene therapy education initiative by the ASGCT and Muhimbili University of Health and Allied Sciences
Cornetta, Kenneth, Kay, Samantha, Urio, Florence, Minja, Irene Kida, Mbugi, Erasto, Mgaya, Josephine, Mselle, Teddy, Nkya, Siana, Alimohamed, Mohamed Zahir, Ndaki, Kinuma, Bonamino, Martín, Koya, Richard C., Shah, Lesha D., Mahlangu, Johnny, Drago, Daniela, Rangarajan, Savita, Jayandharan, Giridhara Rao
Published in Molecular therapy (06.09.2023)
Published in Molecular therapy (06.09.2023)
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Journal Article
Phase 2/3 Trial of Subcutaneously Administered Marzeptacog Alfa (activated) an Engineered FVIIa in Hemophilia with Inhibitors - Pharmacokinetics, Pharmacodynamics, Safety and Efficacy
Levy, Howard, Makhaldiani, Levani, Iosava, Genadi, Mahlangu, Johnny, Kosinova, Marina V, Khacchatryan, Heghine, Del Greco, Frank, Booth, Frank V. McL
Published in Blood (29.11.2018)
Published in Blood (29.11.2018)
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Journal Article
Health‐related quality of life and caregiver burden of emicizumab in children with haemophilia A and factor VIII inhibitors—Results from the HAVEN 2 study
Mancuso, Maria Elisa, Mahlangu, Johnny, Sidonio, Robert, Trask, Peter, Uguen, Marianne, Chang, Tiffany, Shima, Midori, Young, Guy, Oldenburg, Johannes, Mackensen, Sylvia
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2020)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2020)
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Journal Article