Trial of Sodium Phenylbutyrate–Taurursodiol for Amyotrophic Lateral Sclerosis
Paganoni, Sabrina, Macklin, Eric A, Hendrix, Suzanne, Berry, James D, Elliott, Michael A, Maiser, Samuel, Karam, Chafic, Caress, James B, Owegi, Margaret A, Quick, Adam, Wymer, James, Goutman, Stephen A, Heitzman, Daragh, Heiman-Patterson, Terry, Jackson, Carlayne E, Quinn, Colin, Rothstein, Jeffrey D, Kasarskis, Edward J, Katz, Jonathan, Jenkins, Liberty, Ladha, Shafeeq, Miller, Timothy M, Scelsa, Stephen N, Vu, Tuan H, Fournier, Christina N, Glass, Jonathan D, Johnson, Kristin M, Swenson, Andrea, Goyal, Namita A, Pattee, Gary L, Andres, Patricia L, Babu, Suma, Chase, Marianne, Dagostino, Derek, Dickson, Samuel P, Ellison, Noel, Hall, Meghan, Hendrix, Kent, Kittle, Gale, McGovern, Michelle, Ostrow, Joseph, Pothier, Lindsay, Randall, Rebecca, Shefner, Jeremy M, Sherman, Alexander V, Tustison, Eric, Vigneswaran, Prasha, Walker, Jason, Yu, Hong, Chan, James, Wittes, Janet, Cohen, Joshua, Klee, Justin, Leslie, Kent, Tanzi, Rudolph E, Gilbert, Walter, Yeramian, Patrick D, Schoenfeld, David, Cudkowicz, Merit E
Published in The New England journal of medicine (03.09.2020)
Published in The New England journal of medicine (03.09.2020)
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Journal Article
A randomized placebo‐controlled phase 3 study of mesenchymal stem cells induced to secrete high levels of neurotrophic factors in amyotrophic lateral sclerosis
Cudkowicz, Merit E., Lindborg, Stacy R., Goyal, Namita A., Miller, Robert G., Burford, Matthew J., Berry, James D., Nicholson, Katharine A., Mozaffar, Tahseen, Katz, Jonathan S., Jenkins, Liberty J., Baloh, Robert H., Lewis, Richard A., Staff, Nathan P., Owegi, Margaret A., Berry, Donald A., Gothelf, Yael, Levy, Yossef S., Aricha, Revital, Kern, Ralph Z., Windebank, Anthony J., Brown, Robert H.
Published in Muscle & nerve (01.03.2022)
Published in Muscle & nerve (01.03.2022)
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Journal Article
Phrenic nerve conduction studies as a biomarker of respiratory insufficiency in amyotrophic lateral sclerosis
Jenkins, J. A. Liberty, Sakamuri, Sarada, Katz, Jonathan S., Forshew, Dallas A., Guion, Lee, Moore, Dan, Miller, Robert G.
Published in Amyotrophic lateral sclerosis and frontotemporal degeneration (18.05.2016)
Published in Amyotrophic lateral sclerosis and frontotemporal degeneration (18.05.2016)
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Journal Article
Long‐term survival of participants in the CENTAUR trial of sodium phenylbutyrate‐taurursodiol in amyotrophic lateral sclerosis
Paganoni, Sabrina, Hendrix, Suzanne, Dickson, Samuel P., Knowlton, Newman, Macklin, Eric A., Berry, James D., Elliott, Michael A., Maiser, Samuel, Karam, Chafic, Caress, James B., Owegi, Margaret Ayo, Quick, Adam, Wymer, James, Goutman, Stephen A., Heitzman, Daragh, Heiman‐Patterson, Terry D., Jackson, Carlayne E., Quinn, Colin, Rothstein, Jeffrey D., Kasarskis, Edward J., Katz, Jonathan, Jenkins, Liberty, Ladha, Shafeeq, Miller, Timothy M., Scelsa, Stephen N., Vu, Tuan H., Fournier, Christina N., Glass, Jonathan D., Johnson, Kristin M., Swenson, Andrea, Goyal, Namita A., Pattee, Gary L., Andres, Patricia L., Babu, Suma, Chase, Marianne, Dagostino, Derek, Hall, Meghan, Kittle, Gale, Eydinov, Matthew, McGovern, Michelle, Ostrow, Joseph, Pothier, Lindsay, Randall, Rebecca, Shefner, Jeremy M., Sherman, Alexander V., St Pierre, Maria E., Tustison, Eric, Vigneswaran, Prasha, Walker, Jason, Yu, Hong, Chan, James, Wittes, Janet, Yu, Zi‐Fan, Cohen, Joshua, Klee, Justin, Leslie, Kent, Tanzi, Rudolph E., Gilbert, Walter, Yeramian, Patrick D., Schoenfeld, David, Cudkowicz, Merit E.
Published in Muscle & nerve (01.01.2021)
Published in Muscle & nerve (01.01.2021)
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Journal Article
Effect of sodium phenylbutyrate/taurursodiol on tracheostomy/ventilation-free survival and hospitalisation in amyotrophic lateral sclerosis: long-term results from the CENTAUR trial
Paganoni, Sabrina, Hendrix, Suzanne, Dickson, Samuel P, Knowlton, Newman, Berry, James D, Elliott, Michael A, Maiser, Samuel, Karam, Chafic, Caress, James B, Owegi, Margaret Ayo, Quick, Adam, Wymer, James, Goutman, Stephen A, Heitzman, Daragh, Heiman-Patterson, Terry D, Jackson, Carlayne, Quinn, Colin, Rothstein, Jeffrey D, Kasarskis, Edward J, Katz, Jonathan, Jenkins, Liberty, Ladha, Shafeeq S, Miller, Timothy M, Scelsa, Stephen N, Vu, Tuan H, Fournier, Christina, Johnson, Kristin M, Swenson, Andrea, Goyal, Namita, Pattee, Gary L, Babu, Suma, Chase, Marianne, Dagostino, Derek, Hall, Meghan, Kittle, Gale, Eydinov, Mathew, Ostrow, Joseph, Pothier, Lindsay, Randall, Rebecca, Shefner, Jeremy M, Sherman, Alexander V, Tustison, Eric, Vigneswaran, Prasha, Yu, Hong, Cohen, Joshua, Klee, Justin, Tanzi, Rudolph, Gilbert, Walter, Yeramian, Patrick, Cudkowicz, Merit
Published in Journal of neurology, neurosurgery and psychiatry (01.08.2022)
Published in Journal of neurology, neurosurgery and psychiatry (01.08.2022)
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Journal Article
Debamestrocel multimodal effects on biomarker pathways in amyotrophic lateral sclerosis are linked to clinical outcomes
Lindborg, Stacy R, Goyal, Namita A, Katz, Jonathan, Burford, Matthew, Li, Jenny, Kaspi, Haggai, Abramov, Natalie, Boulanger, Bruno, Berry, James D, Nicholson, Katharine, Mozaffar, Tahseen, Miller, Robert, Jenkins, Liberty, Baloh, Robert H, Lewis, Richard, Staff, Nathan P, Owegi, Margaret Ayo, Dagher, Bob, Blondheim-Shraga, Netta R, Gothelf, Yael, Levy, Yossef S, Kern, Ralph, Aricha, Revital, Windebank, Anthony J, Bowser, Robert, Brown, Jr, Robert H, Cudkowicz, Merit E
Published in Muscle & nerve (01.06.2024)
Published in Muscle & nerve (01.06.2024)
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Journal Article
Differential diagnosis
Jenkins, Liberty, Turner, Martin
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (01.11.2019)
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (01.11.2019)
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Book Chapter
Emerging diagnostic biomarkers
Jenkins, Liberty, Turner, Martin
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (01.11.2019)
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (01.11.2019)
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Book Chapter
Defining the syndrome
Jenkins, Liberty, Turner, Martin
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (01.11.2019)
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (01.11.2019)
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Book Chapter
Investigations
Jenkins, Liberty, Turner, Martin
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (01.11.2019)
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (01.11.2019)
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Book Chapter
The first symptoms
Jenkins, Liberty, Turner, Martin
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (01.11.2019)
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (01.11.2019)
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Book Chapter
Epidemiology and pathophysiology
Jenkins, Liberty, Turner, Martin
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (01.11.2019)
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (01.11.2019)
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Book Chapter
Useful resources
Jenkins, Liberty, Turner, Martin
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (01.11.2019)
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (01.11.2019)
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Book Chapter
Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis
Jenkins, Liberty, Turner, Martin
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (2019)
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Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (2019)
Book Chapter
Introduction
Jenkins, Liberty, Turner, Martin
Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (2019)
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Published in Fast Facts: Diagnosing Amyotrophic Lateral Sclerosis (2019)
Book Chapter