The Pharmacokinetics (PK) of GBT440 Following Single Doses in Pediatric Patients with Sickle Cell Disease (SCD)
Washington, Carla B, Green, Michelle, Inati, Adlette C., Brown, Clark, Hoppe, Carolyn C, Wang, Winfred, Balaratnam, Ganesh, Dixon, Sandra, Fong, Erica, Hutchaleelaha, Athiwat, Tonda, Margaret E, Lehrer, Josh
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Journal Article
Initial Results from a Cohort in a Phase 2a Study (GBT440-007) Evaluating Adolescents with Sickle Cell Disease Treated with Multiple Doses of GBT440, a HbS Polymerization Inhibitor
Hoppe, Carolyn C, Inati, Adlette C., Brown, Clark, Wang, Winfred, Gordeuk, Victor R., Liem, Robert, Woods, Gerald, Piccone, Connie M., Fong, Erica, Balaratnam, Ganesh, Dixon, Sandy, Tonda, Margaret E, Washington, Carla B, Yaron, Yifah, Lehrer, Josh
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Journal Article
Iron Overload Indices In Thalassemia Major Children Cured by Stem Cell Transplantation at Enrollment In a Prospective Randomized Trial Comparing Phlebotomy and Deferasirox
Inati, Adlette C., Khoriaty, Evelyne, Sbeiti, Nada, Pierre, Timothy G St, Koussa, Suzanne, Musallam, Khaled M, Taher, Ali T
Published in Blood (19.11.2010)
Published in Blood (19.11.2010)
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Journal Article
HQK-1001 Is Well Tolerated and Augments Hemoglobin F and Hemoglobin Levels In Patients with Beta Thalassemia Intermedia
Fuchareon, Suthat, Inati, Adlette C., Siritanaratkul, Noppadol, Koussa, Suzanne, Taher, Ali, Boosalis, Michael S, Thein, Swee Lay, Wallis, Wayne, Bobbitt, Patrick, Thomson, Audrey, Johnson, Elsa, Berenson, Ronald J, Perrine, Susan P
Published in Blood (19.11.2010)
Published in Blood (19.11.2010)
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Journal Article