Employing a gain-of-function factor IX variant R338L to advance the efficacy and safety of hemophilia B human gene therapy: preclinical evaluation supporting an ongoing adeno-associated virus clinical trial
Monahan, Paul E, Sun, Junjiang, Gui, Tong, Hu, Genlin, Hannah, William B, Wichlan, David G, Wu, Zhijian, Grieger, Joshua C, Li, Chengwen, Suwanmanee, Thipparat, Stafford, Darrel W, Booth, Carmen J, Samulski, Jade J, Kafri, Tal, McPhee, Scott W J, Samulski, R Jude
Published in Human gene therapy (01.02.2015)
Published in Human gene therapy (01.02.2015)
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A Retrospective Study of the Cytokine Profile Changes in Mice with FVIII Inhibitor Development After Adeno-Associated Virus-Mediated Gene Therapy in a Hemophilia A Mouse Model
Sun, Junjiang, Yuan, Zhenhua, Abajas, Yasmina L, Szollosi, Doreen E, Hu, Genlin, Hua, Baolai, Xiao, Xiao, Li, Chengwen
Published in Human gene therapy (01.03.2018)
Published in Human gene therapy (01.03.2018)
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Integration-deficient Lentiviral Vectors Expressing Codon-optimized R338L Human FIX Restore Normal Hemostasis in Hemophilia B Mice
Suwanmanee, Thipparat, Hu, Genlin, Gui, Tong, Bartholomae, Cynthia C, Kutschera, Ina, von Kalle, Christof, Schmidt, Manfred, Monahan, Paul E, Kafri, Tal
Published in Molecular therapy (01.03.2014)
Published in Molecular therapy (01.03.2014)
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IL‐6 receptor antagonist as adjunctive therapy with clotting factor replacement to protect against bleeding‐induced arthropathy in hemophilia
Narkbunnam, N., Sun, J., Hu, G., Lin, F.‐C., Bateman, T. A., Mihara, M., Monahan, P. E.
Published in Journal of thrombosis and haemostasis (01.05.2013)
Published in Journal of thrombosis and haemostasis (01.05.2013)
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Cloning and identification of magnetic field-responsive genes in Daudi cells
Wu, Ruiying, Jiang, Huai, Hu, Genlin, Fu, Yiti, Lu, Deqiang
Published in Chinese science bulletin (01.06.2000)
Published in Chinese science bulletin (01.06.2000)
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