Efficient genome engineering in human pluripotent stem cells using Cas9 from Neisseria meningitidis
Hou, Zhonggang, Zhang, Yan, Propson, Nicholas E., Howden, Sara E., Chu, Li-Fang, Sontheimer, Erik J., Thomson, James A.
Published in Proceedings of the National Academy of Sciences - PNAS (24.09.2013)
Published in Proceedings of the National Academy of Sciences - PNAS (24.09.2013)
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Cellular extrusion bioprinting improves kidney organoid reproducibility and conformation
Lawlor, Kynan T, Vanslambrouck, Jessica M, Higgins, J William, Chambon, Alison, Bishard, Kristina, Arndt, Derek, Er, Pei Xuan, Wilson, Sean B, Howden, Sara E, Tan, Ker Sin, Li, Fanyi, Hale, Lorna J, Shepherd, Benjamin, Pentoney, Stephen, Presnell, Sharon C, Chen, Alice E, Little, Melissa H
Published in Nature materials (01.02.2021)
Published in Nature materials (01.02.2021)
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Introducing a Spectrum of Long-Range Genomic Deletions in Human Embryonic Stem Cells Using Type I CRISPR-Cas
Dolan, Adam E., Hou, Zhonggang, Xiao, Yibei, Gramelspacher, Max J., Heo, Jaewon, Howden, Sara E., Freddolino, Peter L., Ke, Ailong, Zhang, Yan
Published in Molecular cell (06.06.2019)
Published in Molecular cell (06.06.2019)
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3D organoid-derived human glomeruli for personalised podocyte disease modelling and drug screening
Hale, Lorna J, Howden, Sara E, Phipson, Belinda, Lonsdale, Andrew, Er, Pei X, Ghobrial, Irene, Hosawi, Salman, Wilson, Sean, Lawlor, Kynan T, Khan, Shahnaz, Oshlack, Alicia, Quinlan, Catherine, Lennon, Rachel, Little, Melissa H
Published in Nature communications (04.12.2018)
Published in Nature communications (04.12.2018)
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Evaluation of variability in human kidney organoids
Phipson, Belinda, Er, Pei X, Combes, Alexander N, Forbes, Thomas A, Howden, Sara E, Zappia, Luke, Yen, Hsan-Jan, Lawlor, Kynan T, Hale, Lorna J, Sun, Jane, Wolvetang, Ernst, Takasato, Minoru, Oshlack, Alicia, Little, Melissa H
Published in Nature methods (01.01.2019)
Published in Nature methods (01.01.2019)
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Reproducibility and staging of 3D human retinal organoids across multiple pluripotent stem cell lines
Capowski, Elizabeth E, Samimi, Kayvan, Mayerl, Steven J, Phillips, M Joseph, Pinilla, Isabel, Howden, Sara E, Saha, Jishnu, Jansen, Alex D, Edwards, Kimberly L, Jager, Lindsey D, Barlow, Katherine, Valiauga, Rasa, Erlichman, Zachary, Hagstrom, Anna, Sinha, Divya, Sluch, Valentin M, Chamling, Xitiz, Zack, Donald J, Skala, Melissa C, Gamm, David M
Published in Development (Cambridge) (01.01.2019)
Published in Development (Cambridge) (01.01.2019)
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Patient-iPSC-Derived Kidney Organoids Show Functional Validation of a Ciliopathic Renal Phenotype and Reveal Underlying Pathogenetic Mechanisms
Forbes, Thomas A., Howden, Sara E., Lawlor, Kynan, Phipson, Belinda, Maksimovic, Jovana, Hale, Lorna, Wilson, Sean, Quinlan, Catherine, Ho, Gladys, Holman, Katherine, Bennetts, Bruce, Crawford, Joanna, Trnka, Peter, Oshlack, Alicia, Patel, Chirag, Mallett, Andrew, Simons, Cas, Little, Melissa H.
Published in American journal of human genetics (03.05.2018)
Published in American journal of human genetics (03.05.2018)
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Plasticity of distal nephron epithelia from human kidney organoids enables the induction of ureteric tip and stalk
Howden, Sara E., Wilson, Sean B., Groenewegen, Ella, Starks, Lakshi, Forbes, Thomas A., Tan, Ker Sin, Vanslambrouck, Jessica M., Holloway, Emily M., Chen, Yi-Hsien, Jain, Sanjay, Spence, Jason R., Little, Melissa H.
Published in Cell stem cell (01.04.2021)
Published in Cell stem cell (01.04.2021)
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Journal Article
Enhanced metanephric specification to functional proximal tubule enables toxicity screening and infectious disease modelling in kidney organoids
Vanslambrouck, Jessica M., Wilson, Sean B., Tan, Ker Sin, Groenewegen, Ella, Rudraraju, Rajeev, Neil, Jessica, Lawlor, Kynan T., Mah, Sophia, Scurr, Michelle, Howden, Sara E., Subbarao, Kanta, Little, Melissa H.
Published in Nature communications (08.10.2022)
Published in Nature communications (08.10.2022)
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Renal Subcapsular Transplantation of PSC-Derived Kidney Organoids Induces Neo-vasculogenesis and Significant Glomerular and Tubular Maturation In Vivo
van den Berg, Cathelijne W., Ritsma, Laila, Avramut, M. Cristina, Wiersma, Loes E., van den Berg, Bernard M., Leuning, Daniëlle G., Lievers, Ellen, Koning, Marije, Vanslambrouck, Jessica M., Koster, Abraham J., Howden, Sara E., Takasato, Minoru, Little, Melissa H., Rabelink, Ton J.
Published in Stem cell reports (13.03.2018)
Published in Stem cell reports (13.03.2018)
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Optic Vesicle‐like Structures Derived from Human Pluripotent Stem Cells Facilitate a Customized Approach to Retinal Disease Treatment
Meyer, Jason S., Howden, Sara E., Wallace, Kyle A., Verhoeven, Amelia D., Wright, Lynda S., Capowski, Elizabeth E., Pinilla, Isabel, Martin, Jessica M., Tian, Shulan, Stewart, Ron, Pattnaik, Bikash, Thomson, James A., Gamm, David M.
Published in Stem cells (Dayton, Ohio) (01.08.2011)
Published in Stem cells (Dayton, Ohio) (01.08.2011)
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A Cas9 Variant for Efficient Generation of Indel-Free Knockin or Gene-Corrected Human Pluripotent Stem Cells
Howden, Sara E., McColl, Bradley, Glaser, Astrid, Vadolas, Jim, Petrou, Steven, Little, Melissa H., Elefanty, Andrew G., Stanley, Edouard G.
Published in Stem cell reports (13.09.2016)
Published in Stem cell reports (13.09.2016)
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DevKidCC allows for robust classification and direct comparisons of kidney organoid datasets
Wilson, Sean B, Howden, Sara E, Vanslambrouck, Jessica M, Dorison, Aude, Alquicira-Hernandez, Jose, Powell, Joseph E, Little, Melissa H
Published in Genome medicine (22.02.2022)
Published in Genome medicine (22.02.2022)
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Simultaneous Reprogramming and Gene Correction of Patient Fibroblasts
Howden, Sara E., Maufort, John P., Duffin, Bret M., Elefanty, Andrew G., Stanley, Edouard G., Thomson, James A.
Published in Stem cell reports (08.12.2015)
Published in Stem cell reports (08.12.2015)
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Kidney Organoids Generated Using an Allelic Series of NPHS2 Point Variants Reveal Distinct Intracellular Podocin Mistrafficking
Dorison, Aude, Ghobrial, Irene, Graham, Alison, Peiris, Thanushi, Forbes, Thomas A, See, Michael, Das, Mithun, Saleem, Moin A, Quinlan, Catherine, Lawlor, Kynan T, Ramialison, Mirana, Howden, Sara E, Little, Melissa H
Published in Journal of the American Society of Nephrology (01.01.2023)
Published in Journal of the American Society of Nephrology (01.01.2023)
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Phosphorylation regulates human OCT4
Brumbaugh, Justin, Hou, Zhonggang, Russell, Jason D, Howden, Sara E, Yu, Pengzhi, Ledvina, Aaron R, Coon, Joshua J, Thomson, James A
Published in Proceedings of the National Academy of Sciences - PNAS (08.05.2012)
Published in Proceedings of the National Academy of Sciences - PNAS (08.05.2012)
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Genetic correction and analysis of induced pluripotent stem cells from a patient with gyrate atrophy
Howden, Sara E, Gore, Athurva, Li, Zhe, Fung, Ho-Lim, Nisler, Benjamin S, Nie, Jeff, Chen, Goukai, McIntosh, Brian E, Gulbranson, Daniel R, Diol, Nicole R, Taapken, Seth M, Vereide, David T, Montgomery, Karen Dyer, Zhang, Kun, Gamm, David M, Thomson, James A
Published in Proceedings of the National Academy of Sciences - PNAS (19.04.2011)
Published in Proceedings of the National Academy of Sciences - PNAS (19.04.2011)
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Direct reprogramming to human nephron progenitor-like cells using inducible piggyBac transposon expression of SNAI2-EYA1-SIX1
Vanslambrouck, Jessica M., Woodard, Lauren E., Suhaimi, Norseha, Williams, Felisha M., Howden, Sara E., Wilson, Sean B., Lonsdale, Andrew, Er, Pei X., Li, Joan, Maksimovic, Jovana, Oshlack, Alicia, Wilson, Matthew H., Little, Melissa H.
Published in Kidney international (01.05.2019)
Published in Kidney international (01.05.2019)
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Generation of a homozygous (MCRIi031-A-3) WT1 knockout human iPSC line
Pachernegg, Svenja, Robevska, Gorjana, Ferreira, Lucas G.A., van den Bergen, Jocelyn A., Vlahos, Katerina, Howden, Sara E., Sinclair, Andrew H., Ayers, Katie L.
Published in Stem cell research (01.09.2024)
Published in Stem cell research (01.09.2024)
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Journal Article
Generation of heterozygous (MCRIi031-A-1) and homozygous (MCRIi031-A-2) SOX9 knockout human iPSC lines
Pachernegg, Svenja, Robevska, Gorjana, G. A. Ferreira, Lucas, van den Bergen, Jocelyn A., Vlahos, Katerina, Howden, Sara E., Sinclair, Andrew H., Ayers, Katie L.
Published in Stem cell research (01.09.2024)
Published in Stem cell research (01.09.2024)
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