Diversifying the structure of zinc finger nucleases for high-precision genome editing
Paschon, David E., Lussier, Stephanie, Wangzor, Tenzin, Xia, Danny F., Li, Patrick W., Hinkley, Sarah J., Scarlott, Nicholas A., Lam, Stephen C., Waite, Adam J., Truong, Lynn N., Gandhi, Nimisha, Kadam, Bhakti N., Patil, Deepak P., Shivak, David A., Lee, Gary K., Holmes, Michael C., Zhang, Lei, Miller, Jeffrey C., Rebar, Edward J.
Published in Nature communications (08.03.2019)
Published in Nature communications (08.03.2019)
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Precise genome modification in the crop species Zea mays using zinc-finger nucleases
Shukla, Vipula K, Doyon, Yannick, Miller, Jeffrey C, DeKelver, Russell C, Moehle, Erica A, Worden, Sarah E, Mitchell, Jon C, Arnold, Nicole L, Gopalan, Sunita, Meng, Xiangdong, Choi, Vivian M, Rock, Jeremy M, Wu, Ying-Ying, Katibah, George E, Zhifang, Gao
Published in Nature (21.05.2009)
Published in Nature (21.05.2009)
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Improved specificity of TALE-based genome editing using an expanded RVD repertoire
Miller, Jeffrey C, Zhang, Lei, Xia, Danny F, Campo, John J, Ankoudinova, Irina V, Guschin, Dmitry Y, Babiarz, Joshua E, Meng, Xiangdong, Hinkley, Sarah J, Lam, Stephen C, Paschon, David E, Vincent, Anna I, Dulay, Gladys P, Barlow, Kyle A, Shivak, David A, Leung, Elo, Kim, Jinwon D, Amora, Rainier, Urnov, Fyodor D, Gregory, Philip D, Rebar, Edward J
Published in Nature methods (01.05.2015)
Published in Nature methods (01.05.2015)
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Genetic engineering of human pluripotent cells using TALE nucleases
Jaenisch, Rudolf, Hockemeyer, Dirk, Wang, Haoyi, Kiani, Samira, Lai, Christine S, Gao, Qing, Cassady, John P, Cost, Gregory J, Zhang, Lei, Santiago, Yolanda, Miller, Jeffrey C, Zeitler, Bryan, Cherone, Jennifer M, Meng, Xiangdong, Hinkley, Sarah J, Rebar, Edward J, Gregory, Philip D, Urnov, Fyodor D
Published in Nature biotechnology (01.08.2011)
Published in Nature biotechnology (01.08.2011)
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A TALE nuclease architecture for efficient genome editing
Rebar, Edward J, Miller, Jeffrey C, Tan, Siyuan, Qiao, Guijuan, Barlow, Kyle A, Wang, Jianbin, Xia, Danny F, Meng, Xiangdong, Paschon, David E, Leung, Elo, Hinkley, Sarah J, Dulay, Gladys P, Hua, Kevin L, Ankoudinova, Irina, Cost, Gregory J, Urnov, Fyodor D, Zhang, H Steve, Holmes, Michael C, Zhang, Lei, Gregory, Philip D
Published in Nature biotechnology (01.02.2011)
Published in Nature biotechnology (01.02.2011)
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Functional footprinting of regulatory DNA
Vierstra, Jeff, Reik, Andreas, Chang, Kai-Hsin, Stehling-Sun, Sandra, Zhou, Yuanyue, Hinkley, Sarah J, Paschon, David E, Zhang, Lei, Psatha, Nikoletta, Bendana, Yuri R, O'Neil, Colleen M, Song, Alexander H, Mich, Andrea K, Liu, Pei-Qi, Lee, Gary, Bauer, Daniel E, Holmes, Michael C, Orkin, Stuart H, Papayannopoulou, Thalia, Stamatoyannopoulos, George, Rebar, Edward J, Gregory, Philip D, Urnov, Fyodor D, Stamatoyannopoulos, John A
Published in Nature methods (01.10.2015)
Published in Nature methods (01.10.2015)
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Enhancing gene editing specificity by attenuating DNA cleavage kinetics
Miller, Jeffrey C., Patil, Deepak P., Xia, Danny F., Paine, Charles B., Fauser, Friedrich, Richards, Hunter W., Shivak, David A., Bendaña, Yuri R., Hinkley, Sarah J., Scarlott, Nicholas A., Lam, Stephen C., Reik, Andreas, Zhou, Yuanyue, Paschon, David E., Li, Patrick, Wangzor, Tenzin, Lee, Gary, Zhang, Lei, Rebar, Edward J.
Published in Nature biotechnology (01.08.2019)
Published in Nature biotechnology (01.08.2019)
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Humanized Mouse Model of HIV-1 Latency with Enrichment of Latent Virus in PD-1 + and TIGIT + CD4 T Cells
Llewellyn, George N, Seclén, Eduardo, Wietgrefe, Stephen, Liu, Siyu, Chateau, Morgan, Pei, Hua, Perkey, Katherine, Marsden, Matthew D, Hinkley, Sarah J, Paschon, David E, Holmes, Michael C, Zack, Jerome A, Louie, Stan G, Haase, Ashley T, Cannon, Paula M
Published in Journal of virology (15.05.2019)
Published in Journal of virology (15.05.2019)
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Allele-selective transcriptional repression of mutant HTT for the treatment of Huntington’s disease
Zeitler, Bryan, Froelich, Steven, Marlen, Kimberly, Shivak, David A, Yu, Qi, Li, Davis, Pearl, Jocelynn R, Miller, Jeffrey C, Zhang, Lei, Paschon, David E, Hinkley, Sarah J, Ankoudinova, Irina, Lam, Stephen, Guschin, Dmitry, Kopan, Lexi, Cherone, Jennifer M, Nguyen, Hoang-Oanh B, Qiao, Guijuan, Ataei, Yasaman, Mendel, Matthew C, Amora, Rainier, Surosky, Richard, Laganiere, Josee, Vu, B Joseph, Narayanan, Anand, Sedaghat, Yalda, Tillack, Karsten, Thiede, Christina, Gärtner, Annette, Kwak, Seung, Bard, Jonathan, Mrzljak, Ladislav, Park, Larry, Heikkinen, Taneli, Lehtimäki, Kimmo K, Svedberg, Marie M, Häggkvist, Jenny, Tari, Lenke, Tóth, Miklós, Varrone, Andrea, Halldin, Christer, Kudwa, Andrea E, Ramboz, Sylvie, Day, Michelle, Kondapalli, Jyothisri, Surmeier, D James, Urnov, Fyodor D, Gregory, Philip D, Rebar, Edward J, Muñoz-Sanjuán, Ignacio, Zhang, H Steve
Published in Nature medicine (01.07.2019)
Published in Nature medicine (01.07.2019)
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641. Highly Efficient, ZFN-Driven Knockout of Surface Expression of the T-Cell Receptor and HLA Class I Proteins in Human T-Cells for Enhancing Allogeneic Adoptive Cell Therapies
Lee, Gary K., Liu, Pei-qi, Gandhi, Nimisha, Truong, Lynn, Reik, Andreas, Lam, Stephen, Hinkley, Sarah J., Miller, Jeffrey C., Paschon, David E., Zhang, Lei, Rebar, Edward J., Holmes, Michael C.
Published in Molecular therapy (01.05.2016)
Published in Molecular therapy (01.05.2016)
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Genetic engineering of human ES and iPS cells using TALE nucleases
Hockemeyer, Dirk, Wang, Haoyi, Kiani, Samira, Lai, Christine S, Gao, Qing, Cassady, John P, Cost, Gregory J, Zhang, Lei, Santiago, Yolanda, Miller, Jeffrey C, Zeitler, Bryan, Cherone, Jennifer M, Meng, Xiangdong, Hinkley, Sarah J, Rebar, Edward J, Gregory, Philip D, Urnov, Fyodor D, Jaenisch, Rudolf
Published in Nature biotechnology (07.07.2011)
Published in Nature biotechnology (07.07.2011)
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