Insight and Development of Advanced Recombinant Adeno-Associated Virus Analysis Tools Exploiting Single-Particle Quantification by Multidimensional Droplet Digital PCR
Zanker, Jeanette, Lázaro-Petri, Sara, Hüser, Daniela, Heilbronn, Regine, Savy, Adrien
Published in Human gene therapy (01.09.2022)
Published in Human gene therapy (01.09.2022)
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Journal Article
OneBac: platform for scalable and high-titer production of adeno-associated virus serotype 1-12 vectors for gene therapy
Mietzsch, Mario, Grasse, Sabrina, Zurawski, Catherine, Weger, Stefan, Bennett, Antonette, Agbandje-McKenna, Mavis, Muzyczka, Nicholas, Zolotukhin, Sergei, Heilbronn, Regine
Published in Human gene therapy (01.03.2014)
Published in Human gene therapy (01.03.2014)
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Journal Article
Arcuate NPY Controls Sympathetic Output and BAT Function via a Relay of Tyrosine Hydroxylase Neurons in the PVN
Shi, Yan-Chuan, Lau, Jackie, Lin, Zhou, Zhang, Hui, Zhai, Lei, Sperk, Guenther, Heilbronn, Regine, Mietzsch, Mario, Weger, Stefan, Huang, Xu-Feng, Enriquez, Ronaldo F., Baldock, Paul A., Zhang, Lei, Sainsbury, Amanda, Herzog, Herbert, Lin, Shu
Published in Cell metabolism (05.02.2013)
Published in Cell metabolism (05.02.2013)
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Journal Article
Selective Silencing of Hippocampal Parvalbumin Interneurons Induces Development of Recurrent Spontaneous Limbic Seizures in Mice
Drexel, Meinrad, Romanov, Roman A, Wood, James, Weger, Stefan, Heilbronn, Regine, Wulff, Peer, Tasan, Ramon O, Harkany, Tibor, Sperk, Günther
Published in The Journal of neuroscience (23.08.2017)
Published in The Journal of neuroscience (23.08.2017)
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Journal Article
Loss of mGluR5 in D1 Receptor-Expressing Neurons Improves Stress Coping
Zangrandi, Luca, Schmuckermair, Claudia, Ghareh, Hussein, Castaldi, Federico, Heilbronn, Regine, Zernig, Gerald, Ferraguti, Francesco, Ramos-Prats, Arnau
Published in International journal of molecular sciences (01.08.2021)
Published in International journal of molecular sciences (01.08.2021)
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Journal Article
Dynorphin‐based “release on demand” gene therapy for drug‐resistant temporal lobe epilepsy
Agostinho, Alexandra S, Mietzsch, Mario, Zangrandi, Luca, Kmiec, Iwona, Mutti, Anna, Kraus, Larissa, Fidzinski, Pawel, Schneider, Ulf C, Holtkamp, Martin, Heilbronn, Regine, Schwarzer, Christoph
Published in EMBO molecular medicine (01.10.2019)
Published in EMBO molecular medicine (01.10.2019)
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Journal Article
Evaluation of the SH-SY5Y cell line as an in vitro model for potency testing of a neuropeptide-expressing AAV vector
Zanker, Jeanette, Hüser, Daniela, Savy, Adrien, Lázaro-Petri, Sara, Hammer, Eva-Maria, Schwarzer, Christoph, Heilbronn, Regine
Published in Frontiers in molecular neuroscience (30.11.2023)
Published in Frontiers in molecular neuroscience (30.11.2023)
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Journal Article
CART neurons in the arcuate nucleus and lateral hypothalamic area exert differential controls on energy homeostasis
Lau, Jackie, Farzi, Aitak, Qi, Yue, Heilbronn, Regine, Mietzsch, Mario, Shi, Yan-Chuan, Herzog, Herbert
Published in Molecular metabolism (Germany) (01.01.2018)
Published in Molecular metabolism (Germany) (01.01.2018)
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Journal Article
Autonomous zinc-finger nuclease pairs for targeted chromosomal deletion
Söllü, Cem, Pars, Kaweh, Cornu, Tatjana I, Thibodeau-Beganny, Stacey, Maeder, Morgan L, Joung, J Keith, Heilbronn, Regine, Cathomen, Toni
Published in Nucleic acids research (01.12.2010)
Published in Nucleic acids research (01.12.2010)
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Journal Article
Adeno-Associated Virus (AAV) Capsid Stability and Liposome Remodeling During Endo/Lysosomal pH Trafficking
Lins-Austin, Bridget, Patel, Saajan, Mietzsch, Mario, Brooke, Dewey, Bennett, Antonette, Venkatakrishnan, Balasubramanian, Van Vliet, Kim, Smith, Adam N, Long, Joanna R, McKenna, Robert, Potter, Mark, Byrne, Barry, Boye, Sanford L, Bothner, Brian, Heilbronn, Regine, Agbandje-McKenna, Mavis
Published in Viruses (20.06.2020)
Published in Viruses (20.06.2020)
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Journal Article
Comprehensive Small RNA-Seq of Adeno-Associated Virus (AAV)-Infected Human Cells Detects Patterns of Novel, Non-Coding AAV RNAs in the Absence of Cellular miRNA Regulation
Stutika, Catrin, Mietzsch, Mario, Gogol-Döring, Andreas, Weger, Stefan, Sohn, Madlen, Chen, Wei, Heilbronn, Regine
Published in PloS one (09.09.2016)
Published in PloS one (09.09.2016)
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Journal Article
Automated Glycan Assembly of Oligo-N-Acetyllactosamine and Keratan Sulfate Probes to Study Virus-Glycan Interactions
Hahm, Heung Sik, Broecker, Felix, Kawasaki, Fumiko, Mietzsch, Mario, Heilbronn, Regine, Fukuda, Minoru, Seeberger, Peter H.
Published in Chem (12.01.2017)
Published in Chem (12.01.2017)
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Journal Article
Integration preferences of wildtype AAV-2 for consensus rep-binding sites at numerous loci in the human genome
Hüser, Daniela, Gogol-Döring, Andreas, Lutter, Timo, Weger, Stefan, Winter, Kerstin, Hammer, Eva-Maria, Cathomen, Toni, Reinert, Knut, Heilbronn, Regine
Published in PLoS pathogens (01.07.2010)
Published in PLoS pathogens (01.07.2010)
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Journal Article
Roles of E4orf6 and VA I RNA in Adenovirus-Mediated Stimulation of Human Parvovirus B19 DNA Replication and Structural Gene Expression
WINTER, Kerstin, VON KIETZELL, Kristina, HEILBRONN, Regine, POZZUTO, Tanja, FECHNER, Henry, WEGER, Stefan
Published in Journal of Virology (01.05.2012)
Published in Journal of Virology (01.05.2012)
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Journal Article
Methylation Status of the Adeno-Associated Virus Type 2 (AAV2)
Tóth, Renáta, Mészáros, István, Hüser, Daniela, Forró, Barbara, Marton, Szilvia, Olasz, Ferenc, Bányai, Krisztián, Heilbronn, Regine, Zádori, Zoltán
Published in Viruses (09.01.2019)
Published in Viruses (09.01.2019)
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Journal Article
A simplified purification protocol for recombinant adeno-associated virus vectors
Potter, Mark, Lins, Bridget, Mietzsch, Mario, Heilbronn, Regine, Van Vliet, Kim, Chipman, Paul, Agbandje-McKenna, Mavis, Cleaver, Brian D, Clément, Nathalie, Byrne, Barry J, Zolotukhin, Sergei
Published in Molecular therapy. Methods & clinical development (01.01.2014)
Published in Molecular therapy. Methods & clinical development (01.01.2014)
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Journal Article
DNA-Binding Activity of Adeno-Associated Virus Rep Is Required for Inverted Terminal Repeat-Dependent Complex Formation with Herpes Simplex Virus ICP8
ALEX, Martin, WEGER, Stefan, MIETZSCH, Mario, SLANINA, Heiko, CATHOMEN, Toni, HEILBRONN, Regine
Published in Journal of Virology (01.03.2012)
Published in Journal of Virology (01.03.2012)
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