Genome-wide distribution of linker histone H1.0 is independent of MeCP2
Ito-Ishida, Aya, Yamalanchili, Hari Krishna, Shao, Yingyao, Baker, Steven A., Heckman, Laura D., Lavery, Laura A., Kim, Ji-yoen, Lombardi, Laura M., Sun, Yaling, Liu, Zhandong, Zoghbi, Huda Y.
Published in Nature neuroscience (01.06.2018)
Published in Nature neuroscience (01.06.2018)
Get full text
Journal Article
PR001 gene therapy increased GCase activity and improved Gaucher disease type 1 phenotypes in mouse models
Sheehan, Patty, Heckman, Laura D., Wong, Li Chin, Yang, Zhaohui, Lin, Hsuan-Ni, Kamalakaran, Sid, Garimalla, Swetha, Politi, Jason, Dai, Yong, Hefti, Franz, Abeliovich, Asa
Published in Molecular genetics and metabolism (01.02.2021)
Published in Molecular genetics and metabolism (01.02.2021)
Get full text
Journal Article
PR001 gene therapy increased GCase activity and improved neuronopathic Gaucher disease phenotypes
Sheehan, Patty, Heckman, Laura D., Fenn, Tim, Wong, Li Chin, Nelson, Stuart, Garimalla, Swetha, Haller, Jorge, Daily, Jennifer, Politi, Jason, Dai, Yong, Hefti, Franz, Abeliovich, Asa
Published in Molecular genetics and metabolism (01.02.2021)
Published in Molecular genetics and metabolism (01.02.2021)
Get full text
Journal Article
PR001 gene therapy increased GCase activity and improved Gaucher disease type 1 phenotypes in mouse models
Sheehan, Patty, Heckman, Laura D., Wong, Li Chin, Kamalakaran, Sid, Yang, Zhaohui, Lin, Hsuan-Ni, Garimalla, Swetha, Biezonski, Dominik, Hendricks, Jeremiah, Raghunathan, Rekha, Zhao, Zoe, Raut, Priyam, Politi, Jason, Dai, Yong, Abeliovich, Asa, Hefti, Franz
Published in Molecular genetics and metabolism (01.02.2022)
Published in Molecular genetics and metabolism (01.02.2022)
Get full text
Journal Article
PR001 gene therapy improved phenotypes in models of Parkinson’s disease with GBA1 mutation: Molecular and cell biology/endosomal‐lysosomal dysfunction
Sheehan, Patty, Heckman, Laura D., Fenn, Tim, Wong, Li Chin, Nelson, Stuart, Garimalla, Swetha, Haller, Jorge, Daily, Jenn, Politi, Jason, Dai, Yong, Hefti, Franz, Abeliovich, Asa
Published in Alzheimer's & dementia (01.12.2020)
Published in Alzheimer's & dementia (01.12.2020)
Get full text
Journal Article
PR001 gene therapy improved phenotypes in models of Parkinson’s disease with GBA1 mutation
Sheehan, Patty, Heckman, Laura D., Fenn, Tim, Wong, Li Chin, Nelson, Stuart, Garimalla, Swetha, Haller, Jorge, Daily, Jenn, Politi, Jason, Dai, Yong, Hefti, Franz, Abeliovich, Asa
Published in Alzheimer's & dementia (01.12.2020)
Published in Alzheimer's & dementia (01.12.2020)
Get full text
Journal Article
Gene therapy PR001 increased GCase activity and improved neuronopathic Gaucher disease phenotypes in mouse models
Heckman, Laura D., Sheehan, Patty, Fenn, Tim, Wong, Li Chin, Nelson, Stuart, Garimalla, Swetha, Haller, Jorge, Daily, Jennifer, Politi, Jason, Dai, Yong, Hefti, Franz, Abeliovich, Asa
Published in Molecular genetics and metabolism (01.02.2020)
Published in Molecular genetics and metabolism (01.02.2020)
Get full text
Journal Article
Preclinical development of PR006, a gene therapy for the treatment of frontotemporal dementia with progranulin mutations
Heckman, Laura D., Burstein, Suzanne R., Brandes, Alissa, Wong, Li Chin, Yang, Zhaohui, Lin, Hsuan‐Ni, Fenn, Tim, Nelson, Stuart, Aziz, Zarah, Kamalakaran, Sid, Garimalla, Swetha, Haller, Jorge, Daily, Jenn, Politi, Jason, Dai, Yong, Hefti, Franz, Abeliovich, Asa
Published in Alzheimer's & dementia (01.12.2020)
Published in Alzheimer's & dementia (01.12.2020)
Get full text
Journal Article
Preclinical development of PR006, a gene therapy for the treatment of frontotemporal dementia with progranulin mutations: Molecular and cell biology/endosomal‐lysosomal dysfunction
Heckman, Laura D., Burstein, Suzanne R., Brandes, Alissa, Wong, Li Chin, Yang, Zhaohui, Lin, Hsuan‐Ni, Fenn, Tim, Nelson, Stuart, Aziz, Zarah, Kamalakaran, Sid, Garimalla, Swetha, Haller, Jorge, Daily, Jenn, Politi, Jason, Dai, Yong, Hefti, Franz, Abeliovich, Asa
Published in Alzheimer's & dementia (01.12.2020)
Published in Alzheimer's & dementia (01.12.2020)
Get full text
Journal Article
Gene therapy PR006 increased progranulin levels and improved lysosomal related phenotypes in model systems
Brandes, Alissa, Heckman, Laura D., Wong, Li Chin, Yang, Zhaohui, Fenn, Tim, Nelson, Stuart, Aziz, Zarah, Kamalakaran, Sid, Garimalla, Swetha, Burstein, Suzanne, Haller, Jorge, Politi, Jason, Dai, Yong, Hefti, Franz, Abeliovich, Asa
Published in Molecular genetics and metabolism (01.02.2020)
Published in Molecular genetics and metabolism (01.02.2020)
Get full text
Journal Article