First-in-Human Dose-Finding Study of AAVhu37 Vector-Based Gene Therapy: BAY 2599023 Has Stable and Sustained Expression of FVIII over 2 Years
Pipe, Steven W, Sheehan, John P, Coppens, Michiel, Eichler, Hermann, Linardi, Camila, Wiegmann, Sara, Hay, Charles RM, Lissitchkov, Toshko
Published in Blood (23.11.2021)
Published in Blood (23.11.2021)
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Emicizumab prophylaxis in haemophilia A with inhibitors: Three years follow‐up from the UK Haemophilia Centre Doctors’ Organisation (UKHCDO)
Wall, Caroline, Xiang, Hua, Palmer, Ben, Chalmers, Elizabeth, Chowdary, Pratima, Collins, Peter W., Fletcher, Simon, Hall, Georgina W., Hart, Daniel P., Mathias, Mary, Sartain, Paul, Shapiro, Susan, Stephensen, David, Talks, Kate, Hay, Charles R.M.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2023)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2023)
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101HEMB01 Is a Phase 1/2 Open-Label, Single Ascending Dose-Finding Trial of DTX101 (AAVrh10FIX) in Patients with Moderate/Severe Hemophilia B That Demonstrated Meaningful but Transient Expression of Human Factor IX (hFIX)
Pipe, Steven, Stine, Kimo, Rajasekhar, Anita, Everington, Tamara, Poma, Allen, Crombez, Eric, Hay, Charles RM
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Recombinant factor VIII products and inhibitor development in previously untreated patients with severe haemophilia A: Combined analysis of three studies
Volkers, Peter, Hanschmann, Kay‐Martin, Calvez, Thierry, Chambost, Hervé, Collins, Peter W., Demiguel, Virginie, Hart, Daniel P., Hay, Charles R.M., Goudemand, Jenny, Ljung, Rolf, Palmer, Ben P., Santagostino, Elena, van Hardeveld, Ella M., van den Berg, Marijke, Keller‐Stanislawski, Brigitte
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2019)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2019)
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Prospective Observation on the Use of Von Willebrand Factor (VWF) Concentrates in a Large Cohort of Type 3 Von Willebrand Disease (VWD): Interim (18-months) Analyses on 149 Cases Enrolled into the 3Winters-Ips Project
Federici, Augusto B, Badiee, Zahra, Baghaipour, Mohammad-Reza, Castaman, Giancarlo, Eshghi, Peyman, Goudemand, Jenny, Hay, Charles RM, Hoorfar, Hamid, Karimi, Mehran, Keikhaei, Bijan, Lassila, Riitta, Leebeek, Frank, Lopez Fernandez, Maria Fernanda, Marino, Renato, Peake, Ian, Parra Lòpez, Rafael, Peyvandi, Flora, Santoro, Cristina, Siboni, Simona Maria, Tosetto, Alberto, Trossaert, Marc, Eikenboom, Jeroen C.J.
Published in Blood (29.11.2018)
Published in Blood (29.11.2018)
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FVIII inhibitor development according to concentrate: data from the EUHASS registry excluding overlap with other studies
Fischer, K., Iorio, A., Hollingsworth, R., Makris, M.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2016)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2016)
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Integrated analysis of safety and efficacy of a plasma- and albumin-free recombinant factor VIII (rAHF-PFM) from six clinical studies in patients with hemophilia A
Shapiro, Amy, Gruppo, Ralph, Pabinger, Ingrid, Collins, Peter W, Hay, Charles R M, Schroth, Phillip, Casey, Kathleen, Patrone, Lisa, Ehrlich, Hartmut, Ewenstein, Bruce M
Published in Expert opinion on biological therapy (01.03.2009)
Published in Expert opinion on biological therapy (01.03.2009)
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Aplasia cutis congenita and low molecular weight heparin
Sharif, Saba, Hay, Charles R.M., Clayton‐Smith, Jill
Published in BJOG : an international journal of obstetrics and gynaecology (01.02.2005)
Published in BJOG : an international journal of obstetrics and gynaecology (01.02.2005)
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