Modeling antisense oligonucleotide therapy in MECP2 duplication syndrome human iPSC-derived neurons reveals gene expression programs responsive to MeCP2 levels
Bajikar, Sameer S, Sztainberg, Yehezkel, Trostle, Alexander J, Tirumala, Harini P, Wan, Ying-Wooi, Harrop, Caroline L, Bengtsson, Jesse D, Carvalho, Claudia M B, Pehlivan, Davut, Suter, Bernhard, Neul, Jeffrey L, Liu, Zhandong, Jafar-Nejad, Paymaan, Rigo, Frank, Zoghbi, Huda Y
Published in Human molecular genetics (15.09.2024)
Published in Human molecular genetics (15.09.2024)
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