AP-3-dependent targeting of flippase ATP8A1 to lamellar bodies suppresses activation of YAP in alveolar epithelial type 2 cells
Kook, Seunghyi, Wang, Ping, Meng, Shufang, Jetter, Christopher S, Sucre, Jennifer M S, Benjamin, John T, Gokey, Jason J, Hanby, Hayley A, Jaume, Alexa, Goetzl, Laura, Marks, Michael S, Guttentag, Susan H
Published in Proceedings of the National Academy of Sciences - PNAS (18.05.2021)
Published in Proceedings of the National Academy of Sciences - PNAS (18.05.2021)
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High-resolution epitope mapping by HX MS reveals the pathogenic mechanism and a possible therapy for autoimmune TTP syndrome
Casina, Veronica C., Hu, Wenbing, Mao, Jian-Hua, Lu, Rui-Nan, Hanby, Hayley A., Pickens, Brandy, Kan, Zhong-Yuan, Lim, Woon K., Mayne, Leland, Ostertag, Eric M., Kacir, Stephen, Siegel, Don L., Englander, S. Walter, Zheng, X. Long
Published in Proceedings of the National Academy of Sciences - PNAS (04.08.2015)
Published in Proceedings of the National Academy of Sciences - PNAS (04.08.2015)
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Identifying and enriching platelet-producing human stem cell–derived megakaryocytes using factor V uptake
Sim, Xiuli, Jarocha, Danuta, Hayes, Vincent, Hanby, Hayley A., Marks, Michael S., Camire, Rodney M., French, Deborah L., Poncz, Mortimer, Gadue, Paul
Published in Blood (13.07.2017)
Published in Blood (13.07.2017)
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IgG-cleaving endopeptidase enables in vivo gene therapy in the presence of anti-AAV neutralizing antibodies
Leborgne, Christian, Barbon, Elena, Alexander, Jeffrey M, Hanby, Hayley, Delignat, Sandrine, Cohen, Daniel M, Collaud, Fanny, Muraleetharan, Saghana, Lupo, Dan, Silverberg, Joseph, Huang, Karen, van Wittengerghe, Laetitia, Marolleau, Béatrice, Miranda, Adeline, Fabiano, Anna, Daventure, Victoria, Beck, Heena, Anguela, Xavier M, Ronzitti, Giuseppe, Armour, Sean M, Lacroix-Desmazes, Sebastien, Mingozzi, Federico
Published in Nature Medicine (01.07.2020)
Published in Nature Medicine (01.07.2020)
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IgG-cleaving endopeptidase enables in vivo gene therapy in the presence of anti-AAV neutralizing antibodies
Leborgne, Christian, Barbon, Elena, Alexander, Jeffrey, Hanby, Hayley, Delignat, Sandrine, Cohen, Daniel, Collaud, Fanny, Muraleetharan, Saghana, Lupo, Dan, Silverberg, Joseph, Huang, Karen, van Wittengerghe, Laetitia, Marolleau, Béatrice, Miranda, Adeline, Fabiano, Anna, Daventure, Victoria, Beck, Heena, Anguela, Xavier, Ronzitti, Giuseppe, Armour, Sean, Lacroix-Desmazes, Sebastien, Mingozzi, Federico
Published in Nature Medicine (01.06.2020)
Published in Nature Medicine (01.06.2020)
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IdeS: An enabling technology to overcome the limitation of neutralizing antibodies to AAV gene therapy
Alexander, Jeffrey M., Hanby, Hayley, Lupo, Daniel, Muraleetharan, Saghana, Rizzo, Christopher, Cohen, Daniel M., Silverberg, Joseph, Beck, Heena, Anguela, Xavier, Armour, Sean M., Mingozzi, Federico
Published in Molecular genetics and metabolism (01.02.2021)
Published in Molecular genetics and metabolism (01.02.2021)
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Investigational liver gene transfer of alpha galactosidase for the treatment of Fabry disease
Shyng, Charles, Chagin, Umut, Coachys, Cayse, Ioele, Stephen, Nowrouzi, Ali, Rohacek, Alex, Elliott, Sarah, Hanby, Hayley, Ashley, Scott, Peed, Lindsey C., Howard, Victor G., Ault, Mary, Huang, Karen, Jones, Gabrielle, Beck, Heena, Meng, Ronghua, Saykhedkar, Sayali, Culbert, Andria, Stevens, Dale, Alatsis, Kathila, Cohen, Daniel M., Crosariol, Marco, Armour, Sean, Mingozzi, Federico, Riling, Chris
Published in Molecular genetics and metabolism (01.02.2023)
Published in Molecular genetics and metabolism (01.02.2023)
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Preclinical development of , an investigational liver-directed AAV gene therapy for the treatment of Pompe disease
Armour, Sean M., Nordin, Jayme M.L., Verdera, Helena Costa, Sellier, Pauline, Preston, George M., Riling, Christopher, Cohen, Daniel M., Collaud, Fanny, Crosariol, Marco, Quinn, William J., Hanby, Hayley, Cagin, Umut, Puzzo, Francesco, Haurigot, Virginia, Ronzitti, Giuseppe, Colella, Pasqualina, Anguela, Xavier M., Mingozzi, Federico
Published in Molecular genetics and metabolism (01.02.2020)
Published in Molecular genetics and metabolism (01.02.2020)
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Preclinical development of SPK-3006, an investigational liver-directed AAV gene therapy for the treatment of Pompe disease
Armour, Sean M., Nordin, Jayme M.L., Verdera, Helena Costa, Sellier, Pauline, Preston, George M., Riling, Christopher, Cohen, Daniel M., Collaud, Fanny, Crosariol, Marco, Quinn, William J., Hanby, Hayley, Cagin, Umut, Puzzo, Francesco, Haurigot, Virginia, Ronzitti, Giuseppe, Colella, Pasqualina, Anguela, Xavier M., Mingozzi, Federico
Published in Molecular genetics and metabolism (01.02.2020)
Published in Molecular genetics and metabolism (01.02.2020)
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Autoantibody Epitope Mapping By Hydrogen-Deuterium Exchange Mass Spectrometry at Nearly Single Amino Acid Residue Resolution Reveals Novel Exosites on ADAMTS13 Critical for Substrate Recognition and Mechanism of Autoimmune Thrombotic Thrombocytopenic Purpura
Casina, Veronica C., Hu, Wenbing, Hanby, Hayley A., Pickens, Brandy, Mayne, Leland, Ostertag, Eric, Kacir, Stephen, Siegel, Don L., Englander, S. Walter, Zheng, X. Long
Published in Blood (06.12.2014)
Published in Blood (06.12.2014)
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Deuterium-Hydrogen Exchange Coupled With Mass Spectrometry Revealed A Novel Autoantibody Binding Epitope and Substrate Recognition Site In ADAMTS13 Protease
Casina, Veronica C., Hu, Wenbing, Hanby, Hayley A., Siegel, Don L., Mayne, Leland, Englander, S. Walter, Zheng, X. Long
Published in Blood (15.11.2013)
Published in Blood (15.11.2013)
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Increased ADAM28 Levels In Plasma and Bone Marrow Cells of Patients With Adult Acute Leukemia
Zhang, Xiaohui, Wang, Qianming, Hanby, Hayley A, Zhou, Shiyuan, Zhou, Yi, Wang, Min, Zhao, Jingzhong, Huang, Xiao-Jun, Zheng, Long
Published in Blood (15.11.2013)
Published in Blood (15.11.2013)
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Knockdown of epigenetic transcriptional co-regulator Brd2a disrupts apoptosis and proper formation of hindbrain and midbrain-hindbrain boundary (MHB) region in zebrafish
Murphy, Tami, Melville, Heather, Fradkin, Eliza, Bistany, Giana, Branigan, Gregory, Olsen, Kelly, Comstock, Catharine R., Hanby, Hayley, Garbade, Ellie, DiBenedetto, Angela J.
Published in Mechanisms of development (01.08.2017)
Published in Mechanisms of development (01.08.2017)
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