Successful Regional Delivery and Long-term Expression of a Dystrophin Gene in Canine Muscular Dystrophy: A Preclinical Model for Human Therapies
Wang, Zejing, Storb, Rainer, Halbert, Christine L, Banks, Glen B., Butts, Tiffany M., Finn, Eric E., Allen, James M., Miller, A. Dusty, Chamberlain, Jeffrey S., Tapscott, Stephen J.
Published in Molecular therapy (01.08.2012)
Published in Molecular therapy (01.08.2012)
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Prevalence of neutralizing antibodies against adeno-associated virus (AAV) types 2, 5, and 6 in cystic fibrosis and normal populations: Implications for gene therapy using AAV vectors
Halbert, Christine L, Miller, A Dusty, McNamara, Sharon, Emerson, Julia, Gibson, Ronald L, Ramsey, Bonnie, Aitken, Moira L
Published in Human gene therapy (01.04.2006)
Published in Human gene therapy (01.04.2006)
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Efficient Transduction of Skeletal Muscle using Vectors based on Adeno-associated Virus Serotype 6
Blankinship, Michael J, Gregorevic, Paul, Allen, James M, Harper, Scott Q, Harper, Hollie, Halbert, Christine L, Miller, A Dusty, Miller, Dusty A, Chamberlain, Jeffrey S
Published in Molecular therapy (01.10.2004)
Published in Molecular therapy (01.10.2004)
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Journal Article
Expression of Human α1-Antitrypsin in Mice and Dogs Following AAV6 Vector-mediated Gene Transfer to the Lungs
Halbert, Christine L, Madtes, David K, Vaughan, Andrew E, Wang, Zejing, Storb, Rainer, Tapscott, Stephen J, Miller, A Dusty
Published in Molecular therapy (01.06.2010)
Published in Molecular therapy (01.06.2010)
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Journal Article
Jaagsiekte Sheep Retrovirus and Enzootic Nasal Tumor Virus Promoters Drive Gene Expression in All Airway Epithelial Cells of Mice but Only Induce Tumors in the Alveolar Region of the Lungs
Yu, Darrick L, Linnerth-Petrik, Nicolle M, Halbert, Christine L, Walsh, Scott R, Miller, A Dusty, Wootton, Sarah K
Published in Journal of Virology (01.08.2011)
Published in Journal of Virology (01.08.2011)
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Journal Article
Persistent Expression of Human Clotting Factor IX from Mouse Liver after Intravenous Injection of Adeno-Associated Virus Vectors
Koeberl, Dwight D., Alexander, Ian E., Halbert, Christine L., Russell, David W., Miller, A. Dusty
Published in Proceedings of the National Academy of Sciences - PNAS (18.02.1997)
Published in Proceedings of the National Academy of Sciences - PNAS (18.02.1997)
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Comparison of dystrophin expression following gene editing and gene replacement in an aged preclinical DMD animal model
Bengtsson, Niclas E., Crudele, Julie M., Klaiman, Jordan M., Halbert, Christine L., Hauschka, Stephen D., Chamberlain, Jeffrey S.
Published in Molecular therapy (01.06.2022)
Published in Molecular therapy (01.06.2022)
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Journal Article
Split intein-mediated protein trans-splicing to express large dystrophins
Tasfaout, Hichem, Halbert, Christine L., McMillen, Timothy S., Allen, James M., Reyes, Theodore R., Flint, Galina V., Grimm, Dirk, Hauschka, Stephen D., Regnier, Michael, Chamberlain, Jeffrey S.
Published in Nature (London) (01.08.2024)
Published in Nature (London) (01.08.2024)
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Journal Article
Reduction in apolipoprotein-mediated removal of cellular lipids by immortalization of human fibroblasts and its reversion by cAMP: lack of effect with Tangier disease cells
Oram, J F, Mendez, A J, Lymp, J, Kavanagh, T J, Halbert, C L
Published in Journal of lipid research (01.10.1999)
Published in Journal of lipid research (01.10.1999)
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Journal Article
Lung cancer in mice induced by the jaagsiekte sheep retrovirus envelope protein is not maintained by rare cancer stem cells, but tumorigenicity does correlate with Wnt pathway activation
Vaughan, Andrew E, Halbert, Christine L, Wootton, Sarah K, Miller, A Dusty
Published in Molecular cancer research (01.01.2012)
Published in Molecular cancer research (01.01.2012)
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Journal Article
Adeno-associated virus types 5 and 6 use distinct receptors for cell entry
Seiler, Michael P, Miller, A Dusty, Zabner, Joseph, Halbert, Christine L
Published in Human gene therapy (01.01.2006)
Published in Human gene therapy (01.01.2006)
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Journal Article
Repeat Transduction in the Mouse Lung by Using Adeno-Associated Virus Vectors with Different Serotypes
Halbert, C L, Rutledge, E A, Allen, J M, Russell, D W, Miller, A D
Published in Journal of Virology (01.02.2000)
Published in Journal of Virology (01.02.2000)
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