Prevalence and pharmacological modulation of humoral immunity to AAV vectors in gene transfer to synovial tissue
Mingozzi, F, Chen, Y, Edmonson, S C, Zhou, S, Thurlings, R M, Tak, P P, High, K A, Vervoordeldonk, M J
Published in Gene therapy (01.04.2013)
Published in Gene therapy (01.04.2013)
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Journal Article
High AAV vector purity results in serotype- and tissue-independent enhancement of transduction efficiency
Ayuso, E, Mingozzi, F, Montane, J, Leon, X, Anguela, X M, Haurigot, V, Edmonson, S A, Africa, L, Zhou, S, High, K A, Bosch, F, Wright, J F
Published in Gene therapy (01.04.2010)
Published in Gene therapy (01.04.2010)
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Journal Article
Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector
High, Katherine A, Kay, Mark A, Manno, Catherine S, Ragni, Margaret V, Larson, Peter J, Couto, Linda B, McClelland, Alan, Glader, Bertil, Chew, Amy J, J Tai, Shing, Herzog, Roland W, Arruda, Valder, Johnson, Fred, Scallan, Ciaran, Skarsgard, Erik, Flake, Alan W
Published in Nature genetics (01.03.2000)
Published in Nature genetics (01.03.2000)
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Journal Article
Targeted disruption of the mouse factor VIII gene produces a model of haemophilia A
Bi, L, Lawler, A.M, Antonarakis, S.E, High, K.A, Gearhart, J.D, Kazazian, H.H
Published in Nature genetics (01.05.1995)
Published in Nature genetics (01.05.1995)
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Journal Article
A viable mouse model of factor X deficiency provides evidence for maternal transfer of factor X
Tai, S J, Herzog, R W, Margaritis, P, Arruda, V R, Chu, K, Golden, J A, Labosky, P A, High, K A
Published in Journal of thrombosis and haemostasis (01.02.2008)
Published in Journal of thrombosis and haemostasis (01.02.2008)
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Journal Article
Progress in the molecular biology of inherited bleeding disorders
PIPE, S. W., HIGH, K. A., OHASHI, K., URAL, A. U., LILLICRAP, D.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.07.2008)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.07.2008)
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Journal Article
Prevalence of the factor V Leiden mutation in children and neonates with thromboembolic disease
Hagstrom, J.Nathan, Walter, Johannes, Bluebond-Langner, Rachel, Amatniek, Joan C., Manno, Catherine S., High, Katherine A.
Published in The Journal of pediatrics (01.12.1998)
Published in The Journal of pediatrics (01.12.1998)
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Journal Article
Intravenous administration of an E1/E3-deleted adenoviral vector induces tolerance to factor IX in C57BL/6 mice
FIELDS, P. A, ARMSTRONG, E, HAGSTROM, J. N, ARRUDA, V. R, MURPHY, M. L, FARRELL, J. P, HIGH, K. A, HERZOG, R. W
Published in Gene therapy (01.03.2001)
Published in Gene therapy (01.03.2001)
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Journal Article
Gene therapy in haemophilia - going for cure?
MARGARITIS, P., HIGH, K. A.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2010)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.05.2010)
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Journal Article
A mutation in the propeptide of Factor IX leads to warfarin sensitivity by a novel mechanism
Chu, K, Wu, S M, Stanley, T, Stafford, D W, High, K A
Published in The Journal of clinical investigation (01.10.1996)
Published in The Journal of clinical investigation (01.10.1996)
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Journal Article
Gene therapy: a 2001 perspective
High, K.A.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2001)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.01.2001)
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Journal Article
Special lectures in haemophilia management
BATOROVA, A., HIGH, K. A., GRINGERI, A.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.07.2010)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.07.2010)
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Journal Article
Progress and Prospects: Gene Therapy Clinical Trials (Part 2)
MENEGUZZI, G, BACHOUD-LEVI, A-C, CATTANEO, F, RONCAROLO, M. G, LEEN, A. M, BRENNER, M. K, MCNEISH, I. A, LEMOINE, N. R, CHIOCCA, E. A, WAXMAN, D. J, PESCHANSKI, M, BLESCH, A, TUSZYNSKI, M. H, STRAYER, D. S, GAO, G, WILSON, J. M, HIGH, K. A, AIUTI, A
Published in Gene therapy (01.11.2007)
Published in Gene therapy (01.11.2007)
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Journal Article
AAV-mediated factor IX gene transfer to skeletal muscle in patients with severe hemophilia B
Manno, Catherine S., Chew, Amy J., Hutchison, Sylvia, Larson, Peter J., Herzog, Roland W., Arruda, Valder R., Tai, Shing Jen, Ragni, Margaret V., Thompson, Arthur, Ozelo, Margareth, Couto, Linda B., Leonard, Debra G.B., Johnson, Frederick A., McClelland, Alan, Scallan, Ciaran, Skarsgard, Erik, Flake, Alan W., Kay, Mark A., High, Katherine A., Glader, Bertil
Published in Blood (15.04.2003)
Published in Blood (15.04.2003)
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