Adherence to Prophylaxis in Adolescents and Young Adults with Severe Haemophilia: A Quantitative Study with Patients
van Os, Sandra B, Troop, Nick A, Sullivan, Keith R, Hart, Daniel P
Published in PloS one (19.01.2017)
Published in PloS one (19.01.2017)
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Journal Article
Optimizing language for effective communication of gene therapy concepts with hemophilia patients: a qualitative study
Hart, Daniel P, Branchford, Brian R, Hendry, Sarah, Ledniczky, Robert, Sidonio, Jr, Robert F, Négrier, Claude, Kim, Michelle, Rice, Michelle, Minshall, Matthew, Arcé, Claire, Prince, Steve, Kelleher, Maria, Lee, Sharon
Published in Orphanet journal of rare diseases (28.04.2021)
Published in Orphanet journal of rare diseases (28.04.2021)
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Journal Article
Rare variants in GP1BB are responsible for autosomal dominant macrothrombocytopenia
Sivapalaratnam, Suthesh, Westbury, Sarah K., Stephens, Jonathan C., Greene, Daniel, Downes, Kate, Kelly, Anne M., Lentaigne, Claire, Astle, William J., Huizinga, Eric G., Nurden, Paquita, Papadia, Sofia, Peerlinck, Kathelijne, Penkett, Christopher J., Perry, David J., Roughley, Catherine, Simeoni, Ilenia, Stirrups, Kathleen, Hart, Daniel P., Tait, R.Campbell, Mumford, Andrew D., Laffan, Michael A., Freson, Kathleen, Ouwehand, Willem H., Kunishima, Shinji, Turro, Ernest
Published in Blood (26.01.2017)
Published in Blood (26.01.2017)
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Journal Article
Identification of a homozygous recessive variant in PTGS1 resulting in a congenital aspirin-like defect in platelet function
Chan, Melissa V, Hayman, Melissa A, Sivapalaratnam, Suthesh, Crescente, Marilena, Allan, Harriet E, Edin, Matthew L, Zeldin, Darryl C, Milne, Ginger L, Stephens, Jonathan, Greene, Daniel, Hanif, Moghees, O'Donnell, Valerie B, Dong, Liang, Malkowski, Michael G, Lentaigne, Claire, Wedderburn, Katherine, Stubbs, Matthew, Downes, Kate, Ouwehand, Willem H, Turro, Ernest, BioResource, Nihr, Hart, Daniel P, Freson, Kathleen, Laffan, Michael A, Warner, Timothy D
Published in Haematologica (Roma) (01.05.2021)
Published in Haematologica (Roma) (01.05.2021)
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Journal Article
Factor VIII cross-matches to the human proteome reduce the predicted inhibitor risk in missense mutation hemophilia A
Hart, Daniel P, Uzun, Nazmiye, Skelton, Stuart, Kakoschke, Alison, Househam, Jacob, Moss, David S, Shepherd, Adrian J
Published in Haematologica (Roma) (01.03.2019)
Published in Haematologica (Roma) (01.03.2019)
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Journal Article
Considerations for shared decision management in previously untreated patients with hemophilia A or B
Astermark, Jan, Blatný, Jan, Königs, Christoph, Hermans, Cédric, Jiménez-Yuste, Victor, Hart, Daniel P.
Published in Therapeutic Advances in Hematology (01.01.2023)
Published in Therapeutic Advances in Hematology (01.01.2023)
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Book Review
Journal Article
International consensus recommendations on the management of people with haemophilia B
Hart, Daniel P., Matino, Davide, Astermark, Jan, Dolan, Gerard, d’Oiron, Roseline, Hermans, Cédric, Jiménez-Yuste, Victor, Linares, Adriana, Matsushita, Tadashi, McRae, Simon, Ozelo, Margareth C., Platton, Sean, Stafford, Darrel, Sidonio, Robert F., Tiede, Andreas
Published in Therapeutic Advances in Hematology (2022)
Published in Therapeutic Advances in Hematology (2022)
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Book Review
Journal Article
Dose-escalated donor lymphocyte infusions following reduced intensity transplantation: toxicity, chimerism, and disease responses
Peggs, Karl S., Thomson, Kirsty, Hart, Daniel P., Geary, Johanne, Morris, Emma C., Yong, Kwee, Goldstone, Anthony H., Linch, David C., Mackinnon, Stephen
Published in Blood (15.02.2004)
Published in Blood (15.02.2004)
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Journal Article
Lupus Anticoagulant and Abnormal Coagulation Tests in Patients with Covid-19
Bowles, Louise, Platton, Sean, Yartey, Nada, Dave, Minal, Lee, Kurtis, Hart, Daniel P, MacDonald, Vickie, Green, Laura, Sivapalaratnam, Suthesh, Pasi, K. John, MacCallum, Peter
Published in New England Journal of Medicine (16.07.2020)
Published in New England Journal of Medicine (16.07.2020)
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Journal Article
Web Resource
Haemophilia
Berntorp, Erik, Fischer, Kathelijn, Hart, Daniel P., Mancuso, Maria Elisa, Stephensen, David, Shapiro, Amy D., Blanchette, Victor
Published in Nature reviews. Disease primers (24.06.2021)
Published in Nature reviews. Disease primers (24.06.2021)
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Journal Article
Development of a Wilms’ tumor antigen-specific T-cell receptor for clinical trials: engineered patient’s T cells can eliminate autologous leukemia blasts in NOD/SCID mice
XUE, Shao-An, LIQUAN GAO, THOMAS, Sharyn, HART, Daniel P, ZHAO XUE, John, GILLMORE, Roopinder, VOSS, Ralf-Holger, MORRIS, Emma, STAUSS, Hans J
Published in Haematologica (Roma) (01.01.2010)
Published in Haematologica (Roma) (01.01.2010)
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Journal Article
Gene Therapy with Etranacogene Dezaparvovec for Hemophilia B
Pipe, Steven W., Leebeek, Frank W.G., Recht, Michael, Key, Nigel S., Castaman, Giancarlo, Miesbach, Wolfgang, Lattimore, Susan, Peerlinck, Kathelijne, Van der Valk, Paul, Coppens, Michiel, Kampmann, Peter, Meijer, Karina, O’Connell, Niamh, Pasi, K. John, Hart, Daniel P., Kazmi, Rashid, Astermark, Jan, Hermans, Cedric R.J.R., Klamroth, Robert, Lemons, Richard, Visweshwar, Nathan, von Drygalski, Annette, Young, Guy, Crary, Shelley E., Escobar, Miguel, Gomez, Esteban, Kruse-Jarres, Rebecca, Quon, Doris V., Symington, Emily, Wang, Michael, Wheeler, Allison P., Gut, Robert, Liu, Ying P., Dolmetsch, Ricardo E., Cooper, David L., Li, Yanyan, Goldstein, Brahm, Monahan, Paul E.
Published in The New England journal of medicine (23.02.2023)
Published in The New England journal of medicine (23.02.2023)
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Journal Article
Diagnosis and treatment of factor VIII and IX inhibitors in congenital haemophilia: (4th edition)
Collins, Peter W., Chalmers, Elizabeth, Hart, Daniel P., Liesner, Ri, Rangarajan, Savita, Talks, Kate, Williams, Mike, Hay, Charles R.
Published in British journal of haematology (01.01.2013)
Published in British journal of haematology (01.01.2013)
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Journal Article
Delivery of AAV‐based gene therapy through haemophilia centres—A need for re‐evaluation of infrastructure and comprehensive care: A Joint publication of EAHAD and EHC
Miesbach, Wolfgang, Chowdary, Pratima, Coppens, Michiel, Hart, Daniel P., Jimenez‐Yuste, Victor, Klamroth, Robert, Makris, Michael, Noone, Declan, Peyvandi, Flora
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2021)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.11.2021)
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Journal Article
Treatment regimens and outcomes in severe and moderate haemophilia A in the UK: The THUNDER study
Scott, Martin J., Xiang, Hua, Hart, Daniel P., Palmer, Benedict, Collins, Peter W., Stephensen, David, Sima, Camelia S., Hay, Charles R. M.
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.03.2019)
Published in Haemophilia : the official journal of the World Federation of Hemophilia (01.03.2019)
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Journal Article
Factor VIII brand and the incidence of factor VIII inhibitors in previously untreated UK children with severe hemophilia A, 2000-2011
Collins, Peter W., Palmer, Benedict P., Chalmers, Elizabeth A., Hart, Daniel P., Liesner, Ri, Rangarajan, Savita, Talks, Katherine, Williams, Michael, Charles Hay, R.M.
Published in Blood (27.11.2014)
Published in Blood (27.11.2014)
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Journal Article