Clinically important change for the FACIT-Fatigue scale in paroxysmal nocturnal hemoglobinuria: a derivation from international PNH registry patient data
Cella, David, Johansson, Peter, Ueda, Yasutaka, Tomazos, Ioannis, Gustovic, Philippe, Wang, Alice, Patel, Ami S., Schrezenmeier, Hubert
Published in Journal of patient-reported outcomes (05.07.2023)
Published in Journal of patient-reported outcomes (05.07.2023)
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Long-Term Survival Benefit of Eculizumab Treatment in Patients with Paroxysmal Nocturnal Hemoglobinuria: Data from the International PNH Registry
Terriou, Louis, Patriquin, Christopher J., Griffin, Morag, Lee, Jong Wook, Gustovic, Philippe, Patel, Ami S., Szer, Jeff
Published in Blood (23.11.2021)
Published in Blood (23.11.2021)
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Journal Article
Clinically Important Difference for the FACIT-Fatigue Scale in Paroxysmal Nocturnal Hemoglobinuria: A Derivation from International PNH Registry Patient Data
Cella, David, Johansson, Peter, Ueda, Yasutaka, Tomazos, Ioannis, Gustovic, Philippe, Wang, Alice, Patel, Ami S., Schrezenmeier, Hubert
Published in Blood (23.11.2021)
Published in Blood (23.11.2021)
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Journal Article
Long‐term effectiveness of eculizumab: Data from the International PNH Registry
Terriou, Louis, Lee, Jong Wook, Forsyth, Cecily, Griffin, Morag, Szer, Jeff, Röth, Alexander, Gustovic, Philippe, Metzger, Jesse, Patel, Ami S., Patriquin, Christopher J.
Published in European journal of haematology (01.11.2023)
Published in European journal of haematology (01.11.2023)
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Predictors for Improvement in Patient-Reported Outcomes: Post-Hoc Analysis of a Phase 3 Randomized, Open-Label Study of Eculizumab and Ravulizumab in Complement Inhibitor-Naïve Patients with Paroxysmal Nocturnal Hemoglobinuria (PNH)
Schrezenmeier, Hubert, Kulasekararaj, Austin G., Mitchell, Lindsay, Peffault De Latour, Regis, Devos, Timothy, Okamoto, Shinichiro, Wells, Richard, Johnston, Karissa, Popoff, Evan, Cheung, Antoinette, Wang, Jimmy, Gustovic, Philippe, Wang, Alice, Tomazos, Ioannis, Patel, Yogesh, Lee, Jong Wook
Published in Blood (23.11.2021)
Published in Blood (23.11.2021)
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Relationship of paroxysmal nocturnal hemoglobinuria (PNH) granulocyte clone size to disease burden and risk of major vascular events in untreated patients: results from the International PNH Registry
Dingli, David, Maciejewski, Jaroslaw P., Larratt, Loree, Go, Ronald S., Höchsmann, Britta, Zu, Ke, Gustovic, Philippe, Kulagin, Alexander D.
Published in Annals of hematology (01.07.2023)
Published in Annals of hematology (01.07.2023)
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Interim Analysis of Safety Outcomes during Treatment with Eculizumab: Results from the International Paroxysmal Nocturnal Hemoglobinuria Registry
Hill, Anita, Roeth, Alexander, Socié, Gérard, Caby-Tosi, Marie-Pierre, Wilson, Amanda, Gustovic, Philippe, Bedrosian, Camille L., Brodsky, Robert A.
Published in Blood (08.12.2017)
Published in Blood (08.12.2017)
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Efficacy of Eculizumab in Pediatric Patients with Paroxysmal Nocturnal Hemoglobinuria in the International PNH Registry
Urbano-Ispizua, Álvaro, Kulasekararaj, Austin G., Bartels, Marije, Patriquin, Christopher J., Hoechsmann, Britta, Maschan, Alexey A., Wilson, Amanda, Gustovic, Philippe, Schrezenmeier, Hubert
Published in Blood (29.11.2018)
Published in Blood (29.11.2018)
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Journal Article
Prognostic Value of Clone Size in Paroxysmal Nocturnal Hemoglobinuria (PNH) for Thrombotic Events in Untreated Patients in the International PNH Registry
Peffault De Latour, Regis, Maciejewski, Jaroslaw P., Kulasekararaj, Austin G., Larratt, Loree, Go, Ronald S., Dingli, David, Wilson, Amanda, Gustovic, Philippe, Kulagin, Aleksandr
Published in Blood (29.11.2018)
Published in Blood (29.11.2018)
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Journal Article
Concomitant Immunosuppressive Therapy and Eculizumab Use in Patients with Paroxysmal Nocturnal Hemoglobinuria: An International PNH Registry Analysis
Hill, Anita, de Latour, Régis Peffault, Kulasekararaj, Austin G., Griffin, Morag, Brodsky, Robert A., Maciejewski, Jaroslaw P., Marantz, Jing L., Gustovic, Philippe, Schrezenmeier, Hubert
Published in Acta haematologica (01.01.2023)
Published in Acta haematologica (01.01.2023)
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Beneficial effects of eculizumab regardless of prior transfusions or bone marrow disease: Results of the International Paroxysmal Nocturnal Hemoglobinuria Registry
Röth, Alexander, Araten, David J., Larratt, Loree, Kulasekararaj, Austin G., Maciejewski, Jaroslaw P., Wilson, Amanda, Gustovic, Philippe, Kanakura, Yuzuru
Published in European journal of haematology (01.11.2020)
Published in European journal of haematology (01.11.2020)
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