A Phase 3 Randomized Trial of Voxelotor in Sickle Cell Disease
Vichinsky, Elliott, Hoppe, Carolyn C, Ataga, Kenneth I, Ware, Russell E, Nduba, Videlis, El-Beshlawy, Amal, Hassab, Hoda, Achebe, Maureen M, Alkindi, Salam, Brown, R. Clark, Diuguid, David L, Telfer, Paul, Tsitsikas, Dimitris A, Elghandour, Ashraf, Gordeuk, Victor R, Kanter, Julie, Abboud, Miguel R, Lehrer-Graiwer, Joshua, Tonda, Margaret, Intondi, Allison, Tong, Barbara, Howard, Jo
Published in The New England journal of medicine (08.08.2019)
Published in The New England journal of medicine (08.08.2019)
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Journal Article
Crizanlizumab for the Prevention of Pain Crises in Sickle Cell Disease
Ataga, Kenneth I, Kutlar, Abdullah, Kanter, Julie, Liles, Darla, Cancado, Rodolfo, Friedrisch, João, Guthrie, Troy H, Knight-Madden, Jennifer, Alvarez, Ofelia A, Gordeuk, Victor R, Gualandro, Sandra, Colella, Marina P, Smith, Wally R, Rollins, Scott A, Stocker, Jonathan W, Rother, Russell P
Published in The New England journal of medicine (02.02.2017)
Published in The New England journal of medicine (02.02.2017)
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Journal Article
Erythrocytic ferroportin reduces intracellular iron accumulation, hemolysis, and malaria risk
Zhang, De-Liang, Wu, Jian, Shah, Binal N, Greutélaers, Katja C, Ghosh, Manik C, Ollivierre, Hayden, Su, Xin-Zhuan, Thuma, Philip E, Bedu-Addo, George, Mockenhaupt, Frank P, Gordeuk, Victor R, Rouault, Tracey A
Published in Science (American Association for the Advancement of Science) (30.03.2018)
Published in Science (American Association for the Advancement of Science) (30.03.2018)
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Journal Article
Low hemoglobin increases risk for cerebrovascular disease, kidney disease, pulmonary vasculopathy, and mortality in sickle cell disease: A systematic literature review and meta-analysis
Ataga, Kenneth I, Gordeuk, Victor R, Agodoa, Irene, Colby, Jennifer A, Gittings, Kimberly, Allen, Isabel E
Published in PloS one (03.04.2020)
Published in PloS one (03.04.2020)
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Journal Article
An Official American Thoracic Society Clinical Practice Guideline: Diagnosis, Risk Stratification, and Management of Pulmonary Hypertension of Sickle Cell Disease
KLINGS, Elizabeth S, MACHADO, Roberto F, ROSENZWEIG, Erika B, SOOD, Namita, HSU, Lewis, WILSON, Kevin C, TELEN, Marilyn J, DECASTRO, Laura M, KRISHNAMURTI, Lakshmanan, STEINBERG, Martin H, BADESCH, David B, GLADWIN, Mark T, BARST, Robyn J, MORRIS, Claudia R, MUBARAK, Kamal K, GORDEUK, Victor R, KATO, Gregory J, ATAGA, Kenneth I, GIBBS, J. Simon, CASTRO, Oswaldo
Published in American journal of respiratory and critical care medicine (15.03.2014)
Published in American journal of respiratory and critical care medicine (15.03.2014)
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Journal Article
Prevalence of iron deficiency in 62,685 women of seven race/ethnicity groups: The HEIRS Study
Barton, James C, Wiener, Howard H, Acton, Ronald T, Adams, Paul C, Eckfeldt, John H, Gordeuk, Victor R, Harris, Emily L, McLaren, Christine E, Harrison, Helen, McLaren, Gordon D, Reboussin, David M
Published in PloS one (23.04.2020)
Published in PloS one (23.04.2020)
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Journal Article
Sex-based differences in the manifestations and complications of sickle cell disease: Report from the Sickle Cell Disease Implementation Consortium
Masese, Rita V, Bulgin, Dominique, Knisely, Mitchell R, Preiss, Liliana, Stevenson, Eleanor, Hankins, Jane S, Treadwell, Marsha J, King, Allison A, Gordeuk, Victor R, Kanter, Julie, Gibson, Robert, Glassberg, Jeffrey A, Tanabe, Paula, Shah, Nirmish
Published in PloS one (29.10.2021)
Published in PloS one (29.10.2021)
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Journal Article
Soluble urokinase plasminogen activator receptor is associated with kidney disease and its progression in sickle cell anemia
Zahr, Rima S, Rashkin, Sara R, Ruiz, Maria Armila, Elsherif, Laila, Ren, Guohui, Salas, Guadalupe, Ataga, Kenneth I, Gordeuk, Victor R, Lebensburger, Jeffrey, Zhang, Xu, Saraf, Santosh L
Published in Haematologica (Roma) (02.05.2024)
Published in Haematologica (Roma) (02.05.2024)
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Journal Article
Thrombotic risk in congenital erythrocytosis due to up-regulated hypoxia sensing is not associated with elevated hematocrit
Gordeuk, Victor R, Miasnikova, Galina Y, Sergueeva, Adelina I, Lorenzo, Felipe R, Zhang, Xu, Song, Jihyun, Stockton, David W, Prchal, Josef T
Published in Haematologica (Roma) (01.03.2020)
Published in Haematologica (Roma) (01.03.2020)
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Journal Article
Metabolic signatures of cardiorenal dysfunction in plasma from sickle cell patients as a function of therapeutic transfusion and hydroxyurea treatment
D'Alessandro, Angelo, Nouraie, S Mehdi, Zhang, Yingze, Cendali, Francesca, Gamboni, Fabia, Reisz, Julie A, Zhang, Xu, Bartsch, Kyle W, Galbraith, Matthew D, Espinosa, Joaquin M, Gordeuk, Victor R, Gladwin, Mark T
Published in Haematologica (Roma) (01.12.2023)
Published in Haematologica (Roma) (01.12.2023)
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Journal Article
Improved health care utilization and costs in transplanted versus non-transplanted adults with sickle cell disease
Saraf, Santosh L, Ghimire, Krishna, Patel, Pritesh, Sweiss, Karen, Gowhari, Michel, Molokie, Robert E, Gordeuk, Victor R, Rondelli, Damiano
Published in PloS one (26.02.2020)
Published in PloS one (26.02.2020)
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Journal Article
Risk factors for death in 632 patients with sickle cell disease in the United States and United Kingdom
Gladwin, Mark T, Barst, Robyn J, Gibbs, J Simon R, Hildesheim, Mariana, Sachdev, Vandana, Nouraie, Mehdi, Hassell, Kathryn L, Little, Jane A, Schraufnagel, Dean E, Krishnamurti, Lakshmanan, Novelli, Enrico, Girgis, Reda E, Morris, Claudia R, Berman Rosenzweig, Erika, Badesch, David B, Lanzkron, Sophie, Castro, Oswaldo L, Taylor, 6th, James G, Goldsmith, Jonathan C, Kato, Gregory J, Gordeuk, Victor R, Machado, Roberto F
Published in PloS one (02.07.2014)
Published in PloS one (02.07.2014)
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Journal Article
Publisher Correction: Gene expression changes in sickle cell reticulocytes and their clinical associations
Zhang, Xu, Song, Jihyun, Shah, Binal N, Han, Jin, Hassan, Taif, Miasniakova, Galina, Sergueeva, Adelina, Nekhai, Sergei, Machado, Roberto F, Gladwin, Mark T, Saraf, Santosh L, Prchal, Josef T, Gordeuk, Victor R
Published in Scientific reports (14.09.2023)
Published in Scientific reports (14.09.2023)
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Journal Article
Gene expression changes in sickle cell reticulocytes and their clinical associations
Zhang, Xu, Song, Jihyun, Shah, Binal N, Han, Jin, Hassan, Taif, Miasniakova, Galina, Sergueeva, Adelina, Nekhai, Sergei, Machado, Roberto F, Gladwin, Mark T, Saraf, Santosh L, Prchal, Josef T, Gordeuk, Victor R
Published in Scientific reports (08.08.2023)
Published in Scientific reports (08.08.2023)
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Journal Article
Antimicrobial resistance is a risk factor for mortality in adults with sickle cell disease
Srisuwananukorn, Andrew, Han, Jin, Raslan, Rasha, Gowhari, Michel, Hussain, Faiz, Njoku, Franklin, Molokie, Robert E, Gordeuk, Victor R, Saraf, Santosh L
Published in Haematologica (Roma) (01.06.2021)
Published in Haematologica (Roma) (01.06.2021)
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Journal Article
Publication of data collection forms from NHLBI funded sickle cell disease implementation consortium (SCDIC) registry
Glassberg, Jeffrey A, Linton, Elizabeth A, Burson, Katrina, Hendershot, Tabitha, Telfair, Joseph, Kanter, Julie, Gordeuk, Victor R, King, Allison A, Melvin, Cathy L, Shah, Nirmish, Hankins, Jane S, Epié, Axel Yannick, Richardson, Lynne D
Published in Orphanet journal of rare diseases (07.07.2020)
Published in Orphanet journal of rare diseases (07.07.2020)
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Journal Article
APOL1, α-thalassemia, and BCL11A variants as a genetic risk profile for progression of chronic kidney disease in sickle cell anemia
Saraf, Santosh L, Shah, Binal N, Zhang, Xu, Han, Jin, Tayo, Bamidele O, Abbasi, Taimur, Ostrower, Adam, Guzman, Elizabeth, Molokie, Robert E, Gowhari, Michel, Hassan, Johara, Jain, Shivi, Cooper, Richard S, Machado, Roberto F, Lash, James P, Gordeuk, Victor R
Published in Haematologica (Roma) (01.01.2017)
Published in Haematologica (Roma) (01.01.2017)
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Journal Article
Repurposing pyridoxamine for therapeutic intervention of intravascular cell-cell interactions in mouse models of sickle cell disease
Li, Jing, Jeong, Si-Yeon, Xiong, Bei, Tseng, Alan, Mahon, Andrew B, Isaacman, Steven, Gordeuk, Victor R, Cho, Jaehyung
Published in Haematologica (Roma) (01.10.2020)
Published in Haematologica (Roma) (01.10.2020)
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