Biological drivers of clinical phenotype in myelofibrosis
Mascarenhas, John, Gleitz, Hélène F. E., Chifotides, Helen T., Harrison, Claire N., Verstovsek, Srdan, Vannucchi, Alessandro Maria, Rampal, Raajit K., Kiladjian, Jean-Jacques, Vainchenker, William, Hoffman, Ronald, Schneider, Rebekka K., List, Alan F.
Published in Leukemia (01.02.2023)
Published in Leukemia (01.02.2023)
Get full text
Journal Article
Increased CXCL4 expression in hematopoietic cells links inflammation and progression of bone marrow fibrosis in MPN
Gleitz, Hélène F.E., Dugourd, Aurélien J.F., Leimkühler, Nils B., Snoeren, Inge A.M., Fuchs, Stijn N.R., Menzel, Sylvia, Ziegler, Susanne, Kröger, Nicolaus, Triviai, Ioanna, Büsche, Guntram, Kreipe, Hans, Banjanin, Bella, Pritchard, Jessica E., Hoogenboezem, Remco, Bindels, Eric M., Schumacher, Neele, Rose-John, Stefan, Elf, Shannon, Saez-Rodriguez, Julio, Kramann, Rafael, Schneider, Rebekka K.
Published in Blood (29.10.2020)
Published in Blood (29.10.2020)
Get full text
Journal Article
Brain‐targeted stem cell gene therapy corrects mucopolysaccharidosis type II via multiple mechanisms
Gleitz, Hélène FE, Liao, Ai Yin, Cook, James R, Rowlston, Samuel F, Forte, Gabriella MA, D'Souza, Zelpha, O'Leary, Claire, Holley, Rebecca J, Bigger, Brian W
Published in EMBO molecular medicine (01.07.2018)
Published in EMBO molecular medicine (01.07.2018)
Get full text
Journal Article
Collaborative effect of Csnk1a1 haploinsufficiency and mutant p53 in Myc induction can promote leukemic transformation
Fuchs, Stijn N. R., Stalmann, Ursula S. A., Snoeren, Inge A. M., Bindels, Eric, Schmitz, Stephani, Banjanin, Bella, Hoogenboezem, Remco M., van Herk, Stanley, Saad, Mohamed, Walter, Wencke, Haferlach, Torsten, Seillier, Lancelot, Saez-Rodriguez, Julio, Dugourd, Aurélien J. F., Lehmann, Kjong-Van, Ben-Neriah, Yinon, Gleitz, Hélène F. E., Schneider, Rebekka K.
Published in Blood advances (13.02.2024)
Published in Blood advances (13.02.2024)
Get full text
Journal Article
Macrophage enzyme and reduced inflammation drive brain correction of mucopolysaccharidosis IIIB by stem cell gene therapy
Holley, Rebecca J, Ellison, Stuart M, Fil, Daniel, O'Leary, Claire, McDermott, John, Senthivel, Nishanthi, Langford-Smith, Alexander W W, Wilkinson, Fiona L, D'Souza, Zelpha, Parker, Helen, Liao, Aiyin, Rowlston, Samuel, Gleitz, Hélène F E, Kan, Shih-Hsin, Dickson, Patricia I, Bigger, Brian W
Published in Brain (London, England : 1878) (01.01.2018)
Published in Brain (London, England : 1878) (01.01.2018)
Get full text
Journal Article
Heterogeneous bone-marrow stromal progenitors drive myelofibrosis via a druggable alarmin axis
Leimkühler, Nils B., Gleitz, Hélène F.E., Ronghui, Li, Snoeren, Inge A.M., Fuchs, Stijn N.R., Nagai, James S., Banjanin, Bella, Lam, King H., Vogl, Thomas, Kuppe, Christoph, Stalmann, Ursula S.A., Büsche, Guntram, Kreipe, Hans, Gütgemann, Ines, Krebs, Philippe, Banz, Yara, Boor, Peter, Tai, Evelyn Wing-Yin, Brümmendorf, Tim H., Koschmieder, Steffen, Crysandt, Martina, Bindels, Eric, Kramann, Rafael, Costa, Ivan G., Schneider, Rebekka K.
Published in Cell stem cell (01.04.2021)
Published in Cell stem cell (01.04.2021)
Get full text
Journal Article
Genetic barcoding systematically compares genes in del(5q) MDS and reveals a central role for CSNK1A1 in clonal expansion
Stalmann, Ursula S.A., Ticconi, Fabio, Snoeren, Inge A.M., Li, Ronghui, Gleitz, Hélène F.E., Cowley, Glenn S., McConkey, Marie E., Wong, Aaron B., Schmitz, Stephani, Fuchs, Stijn N.R., Sood, Shubhankar, Leimkühler, Nils B., Martinez-Høyer, Sergio, Banjanin, Bella, Root, David, Brümmendorf, Tim H., Pearce, Juliette E., Schuppert, Andreas, Bindels, Eric M.J., Essers, Marieke A., Heckl, Dirk, Stiehl, Thomas, Costa, Ivan G., Ebert, Benjamin L., Schneider, Rebekka K.
Published in Blood advances (22.03.2022)
Published in Blood advances (22.03.2022)
Get full text
Journal Article
Fibrosis driving myofibroblast precursors in MPN and new therapeutic pathways
Gleitz, Hélène F.E., Pritchard, Jessica E., Kramann, Rafael, Schneider, Rebekka K.
Published in HemaSphere (01.06.2019)
Published in HemaSphere (01.06.2019)
Get full text
Journal Article
Non-canonical Hedgehog signaling mediates profibrotic hematopoiesis-stroma crosstalk in myeloproliferative neoplasms
Pritchard, Jessica E., Pearce, Juliette E., Snoeren, Inge A.M., Fuchs, Stijn N.R., Götz, Katrin, Peisker, Fabian, Wagner, Silke, Benabid, Adam, Lutterbach, Niklas, Klöker, Vanessa, Nagai, James S., Hannani, Monica T., Galyga, Anna K., Sistemich, Ellen, Banjanin, Bella, Flosdorf, Niclas, Bindels, Eric, Olschok, Kathrin, Biaesch, Katharina, Chatain, Nicolas, Bhagwat, Neha, Dunbar, Andrew, Sarkis, Rita, Naveiras, Olaia, Berres, Marie-Luise, Koschmieder, Steffen, Levine, Ross L., Costa, Ivan G., Gleitz, Hélène F.E., Kramann, Rafael, Schneider, Rebekka K.
Published in Cell reports (Cambridge) (23.01.2024)
Published in Cell reports (Cambridge) (23.01.2024)
Get full text
Journal Article
Sustained long-term disease correction in a murine model of MPSII following stem cell gene therapy
Ellison, Stuart, Liao, Aiyin, Gleitz, Hélène F.E., Parker, Helen, Booth, Laura, Robinson, John, Wood, Shaun, Taylor, Jessica, Holley, Rebecca, Bigger, Brian W.
Published in Molecular therapy. Methods & clinical development (14.12.2023)
Published in Molecular therapy. Methods & clinical development (14.12.2023)
Get full text
Journal Article