Prevalence and Relevance of Pre-Existing Anti-Adeno-Associated Virus Immunity in the Context of Gene Therapy for Crigler-Najjar Syndrome
Aronson, Sem J, Veron, Philippe, Collaud, Fanny, Hubert, Aurélie, Delahais, Virginie, Honnet, Géraldine, de Knegt, Robert J, Junge, Norman, Baumann, Ulrich, Di Giorgio, Angelo, D'Antiga, Lorenzo, Ginocchio, Virginia M, Brunetti-Pierri, Nicola, Labrune, Philippe, Beuers, Ulrich, Bosma, Piter J, Mingozzi, Federico
Published in Human gene therapy (01.10.2019)
Published in Human gene therapy (01.10.2019)
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Disease burden and management of Crigler‐Najjar syndrome: Report of a world registry
Aronson, Sem J., Junge, Norman, Trabelsi, Mediha, Kelmemi, Wided, Hubert, Aurelie, Brigatti, Karlla W., Fox, Michael D., Knegt, Robert J., Escher, Johanna C., Ginocchio, Virginia M., Iorio, Raffaele, Zhu, Yan, Özçay, Figen, Rahim, Fakher, El‐Shabrawi, Mortada H.F., Shteyer, Eyal, Di Giorgio, Angelo, D'Antiga, Lorenzo, Mingozzi, Federico, Brunetti‐Pierri, Nicola, Strauss, Kevin A., Labrune, Philippe, Mrad, Ridha, Baumann, Ulrich, Beuers, Ulrich, Bosma, Piter J.
Published in Liver international (01.07.2022)
Published in Liver international (01.07.2022)
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Sonic Hedgehog deletion and distal trisomy 3p in a patient with microphthalmia and microcephaly, lacking cerebral anomalies typical of holoprosencephaly
Ginocchio, Virginia M, De Brasi, Daniele, Genesio, Rita, Ciccone, Roberto, Gimelli, Stefania, Fimiani, Francesco, de Berardinis, Teresa, Nitsch, Lucio, Banfi, Sandro, Magli, Adriano, Della Casa, Roberto
Published in European journal of medical genetics (01.11.2008)
Published in European journal of medical genetics (01.11.2008)
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