A small-molecule inhibitor and degrader of the RNF5 ubiquitin ligase
Ruan, Jingjing, Liang, Dongdong, Yan, Wenjing, Zhong, Yongwang, Talley, Daniel C, Rai, Ganesha, Tao, Dingyin, LeClair, Christopher A, Simeonov, Anton, Zhang, Yinghua, Chen, Feihu, Quinney, Nancy L, Boyles, Susan E, Cholon, Deborah M, Gentzsch, Martina, Henderson, Mark J, Xue, Fengtian, Fang, Shengyun
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Published in Molecular biology of the cell (01.11.2022)
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Small-molecule eRF3a degraders rescue CFTR nonsense mutations by promoting premature termination codon readthrough
Lee, Rhianna E, Lewis, Catherine A, He, Lihua, Bulik-Sullivan, Emily C, Gallant, Samuel C, Mascenik, Teresa M, Dang, Hong, Cholon, Deborah M, Gentzsch, Martina, Morton, Lisa C, Minges, John T, Theile, Jonathan W, Castle, Neil A, Knowles, Michael R, Kimple, Adam J, Randell, Scott H
Published in The Journal of clinical investigation (15.09.2022)
Published in The Journal of clinical investigation (15.09.2022)
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A Novel Co-Culture Model Reveals Enhanced CFTR Rescue in Primary Cystic Fibrosis Airway Epithelial Cultures with Persistent IPseudomonas aeruginosa/I Infection
Cholon, Deborah M, Greenwald, Matthew A, Higgs, Matthew G, Quinney, Nancy L, Boyles, Susan E, Meinig, Suzanne L, Minges, John T, Chaubal, Ashlesha, Tarran, Robert, Ribeiro, Carla M. P, Wolfgang, Matthew C, Gentzsch, Ma
Published in Cells (Basel, Switzerland) (01.11.2023)
Published in Cells (Basel, Switzerland) (01.11.2023)
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AAV exploits subcellular stress associated with inflammation, endoplasmic reticulum expansion, and misfolded proteins in models of cystic fibrosis
Johnson, Jarrod S, Gentzsch, Martina, Zhang, Liqun, Ribeiro, Carla M P, Kantor, Boris, Kafri, Tal, Pickles, Raymond J, Samulski, R Jude
Published in PLoS pathogens (01.05.2011)
Published in PLoS pathogens (01.05.2011)
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