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Targeted genome editing in human repopulating haematopoietic stem cells
Genovese, Pietro, Schiroli, Giulia, Escobar, Giulia, Di Tomaso, Tiziano, Firrito, Claudia, Calabria, Andrea, Moi, Davide, Mazzieri, Roberta, Bonini, Chiara, Holmes, Michael C., Gregory, Philip D., van der Burg, Mirjam, Gentner, Bernhard, Montini, Eugenio, Lombardo, Angelo, Naldini, Luigi
Published in Nature (London) (12.06.2014)
Published in Nature (London) (12.06.2014)
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NON-DISRUPTIVE GENE TARGETING
Barker, Jenny, Checketts, Josh, Barzel, Adi, Voit, Richard, Porteus, Matthew, Kay, Mark A
Year of Publication 15.07.2021
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Year of Publication 15.07.2021
Patent
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NON-DISRUPTIVE GENE TARGETING
BARKER, Jenny, KAY, Mark A, CHECKETTS, Josh, BARZEL, Adi, PORTEUS, Matthew, VOIT, Richard
Year of Publication 23.06.2021
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Year of Publication 23.06.2021
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CRISPR/Cas Applications in Myotonic Dystrophy: Expanding Opportunities
Raaijmakers, Renée H.L., Ripken, Lise, Ausems, C. Rosanne M., Wansink, Derick G.
Published in International journal of molecular sciences (27.07.2019)
Published in International journal of molecular sciences (27.07.2019)
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NON-DISRUPTIVE GENE TARGETING
BARKER, Jenny, KAY, Mark A, CHECKETTS, Josh, BARZEL, Adi, PORTEUS, Matthew, VOIT, Richard
Year of Publication 26.08.2020
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Year of Publication 26.08.2020
Patent
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A stress-free strategy to correct point mutations in patient iPS cells
Cai, Jingli, Kropf, Elizabeth, Hou, Ya-Ming, Iacovitti, Lorraine
Published in Stem cell research (01.05.2021)
Published in Stem cell research (01.05.2021)
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Genomic and lipidomic analyses differentiate the compensatory roles of two COX isoforms during systemic inflammation in mice1,2[S]
Li, Xinzhi, Mazaleuskaya, Liudmila L., Ballantyne, Laurel L., Meng, Hu, FitzGerald, Garret A., Funk, Colin D.
Published in Journal of lipid research (01.01.2018)
Published in Journal of lipid research (01.01.2018)
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A method to sequence and quantify DNA integration for monitoring outcome in gene therapy
Brady, Troy, Roth, Shoshannah L., Malani, Nirav, Wang, Gary P., Berry, Charles C., Leboulch, Philippe, Hacein-Bey-Abina, Salima, Cavazzana-Calvo, Marina, Papapetrou, Eirini P., Sadelain, Michel, Savilahti, Harri, Bushman, Frederic D.
Published in Nucleic acids research (01.06.2011)
Published in Nucleic acids research (01.06.2011)
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Let-7f Regulates the Hypoxic Response in Cerebral Ischemia by Targeting NDRG3
Yao, Yaobing, Wang, Weiwei, Jing, Lijun, Wang, Yiwen, Li, Mingzhe, Hou, Xiaocan, Wang, Jing, Peng, Tao, Teng, Junfang, Jia, Yanjie
Published in Neurochemical research (01.02.2017)
Published in Neurochemical research (01.02.2017)
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An atherogenic diet decreases liver FXR gene expression and causes severe hepatic steatosis and hepatic cholesterol accumulation: effect of endurance training
Côté, Isabelle, Ngo Sock, Emilienne Tudor, Lévy, Émile, Lavoie, Jean-Marc
Published in European journal of nutrition (01.08.2013)
Published in European journal of nutrition (01.08.2013)
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