Loading…
Sono‐Controllable and ROS‐Sensitive CRISPR‐Cas9 Genome Editing for Augmented/Synergistic Ultrasound Tumor Nanotherapy
Pu, Yinying, Yin, Haohao, Dong, Caihong, Xiang, Huijing, Wu, Wencheng, Zhou, Bangguo, Du, Dou, Chen, Yu, Xu, Huixiong
Published in Advanced materials (Weinheim) (01.11.2021)
Published in Advanced materials (Weinheim) (01.11.2021)
Get full text
Journal Article
Loading…
Loading…
CRISPR/Cas9 opens new horizon of crop improvement under stress condition
Patra, Sanjib, Chatterjee, Debdatta, Basak, Shrabani, Sen, Susmi, Mandal, Arunava
Published in Biochimica et biophysica acta. General subjects (01.10.2024)
Published in Biochimica et biophysica acta. General subjects (01.10.2024)
Get full text
Journal Article
Loading…
Multilevel analyses of SCN5A mutations in arrhythmogenic right ventricular dysplasia/cardiomyopathy suggest non-canonical mechanisms for disease pathogenesis
te Riele, Anneline S.J.M., Agullo-Pascual, Esperanza, James, Cynthia A., Leo-Macias, Alejandra, Cerrone, Marina, Zhang, Mingliang, Lin, Xianming, Lin, Bin, Rothenberg, Eli, Sobreira, Nara L., Amat-Alarcon, Nuria, Marsman, Roos F., Murray, Brittney, Tichnell, Crystal, van der Heijden, Jeroen F., Dooijes, Dennis, van Veen, Toon A.B., Tandri, Harikrishna, Fowler, Steven J., Hauer, Richard N.W., Tomaselli, Gordon, van den Berg, Maarten P., Taylor, Matthew R.G., Brun, Francesca, Sinagra, Gianfranco, Wilde, Arthur A.M., Mestroni, Luisa, Bezzina, Connie R., Calkins, Hugh, Peter van Tintelen, J., Bu, Lei, Delmar, Mario, Judge, Daniel P.
Published in Cardiovascular research (01.01.2017)
Published in Cardiovascular research (01.01.2017)
Get full text
Journal Article
Loading…
Enhanced homology-directed repair for highly efficient gene editing in hematopoietic stem/progenitor cells
De Ravin, Suk See, Brault, Julie, Meis, Ronald J., Liu, Siyuan, Li, Linhong, Pavel-Dinu, Mara, Lazzarotto, Cicera R., Liu, Taylor, Koontz, Sherry M., Choi, Uimook, Sweeney, Colin L., Theobald, Narda, Lee, GaHyun, Clark, Aaron B., Burkett, Sandra S., Kleinstiver, Benjamin P., Porteus, Matthew H., Tsai, Shengdar, Kuhns, Douglas B., Dahl, Gary A., Headey, Stephen, Wu, Xiaolin, Malech, Harry L.
Published in Blood (13.05.2021)
Published in Blood (13.05.2021)
Get full text
Journal Article
Loading…
NgAgo possesses guided DNA nicking activity
Lee, Kok Zhi, Mechikoff, Michael A, Kikla, Archana, Liu, Arren, Pandolfi, Paula, Fitzgerald, Kevin, Gimble, Frederick S, Solomon, Kevin V
Published in Nucleic acids research (27.09.2021)
Published in Nucleic acids research (27.09.2021)
Get full text
Journal Article
Loading…
Human-mediated outdoor genome editing is not possible so therefore poses no risk to the environment
Allan, Andrew C., Scott, Barry, Tate, Warren, Jameson, Paula E., MacRae, Elspeth, Conner, Anthony J., Drummond, Revel, Foster, Alec, Martin, Cathie, Caradus, John
Published in Ecotoxicology and environmental safety (01.09.2025)
Published in Ecotoxicology and environmental safety (01.09.2025)
Get full text
Journal Article
Loading…
Elimination of Calm1 long 3′-UTR mRNA isoform by CRISPR–Cas9 gene editing impairs dorsal root ganglion development and hippocampal neuron activation in mice
Bae, Bongmin, Gruner, Hannah N., Lynch, Maebh, Feng, Ting, So, Kevin, Oliver, Daniel, Mastick, Grant S., Yan, Wei, Pieraut, Simon, Miura, Pedro
Published in RNA (Cambridge) (01.10.2020)
Published in RNA (Cambridge) (01.10.2020)
Get full text
Journal Article
Loading…
Targeted removal of epigenetic barriers during transcriptional reprogramming
Baumann, Valentin, Wiesbeck, Maximilian, Breunig, Christopher T., Braun, Julia M., Köferle, Anna, Ninkovic, Jovica, Götz, Magdalena, Stricker, Stefan H.
Published in Nature communications (09.05.2019)
Published in Nature communications (09.05.2019)
Get full text
Journal Article
Loading…
Engineering Saccharomyces boulardii for Probiotic Supplementation of l-Ergothioneine
Tang, Chaoqun, Zhang, Lu, Wang, Junyi, Zou, Congjia, Zhang, Yalin, Yuan, Jifeng
Published in Biotechnology journal (01.11.2024)
Published in Biotechnology journal (01.11.2024)
Get more information
Journal Article
Loading…
One small edit for humans, one giant edit for humankind? Points and questions to consider for a responsible way forward for gene editing in humans
Howard, Heidi C., van El, Carla G., Forzano, Francesca, Radojkovic, Dragica, Rial-Sebbag, Emmanuelle, de Wert, Guido, Borry, Pascal, Cornel, Martina C.
Published in European journal of human genetics : EJHG (01.01.2018)
Published in European journal of human genetics : EJHG (01.01.2018)
Get full text
Journal Article
Loading…
Reversing Mechanoinductive DSP Expression by CRISPR/dCas9–mediated Epigenome Editing
Qu, Jing, Zhu, Lanyan, Zhou, Zijing, Chen, Ping, Liu, Shuyan, Locy, Morgan L., Thannickal, Victor J., Zhou, Yong
Published in American journal of respiratory and critical care medicine (01.09.2018)
Published in American journal of respiratory and critical care medicine (01.09.2018)
Get full text
Journal Article
Loading…
Comparison of dystrophin expression following gene editing and gene replacement in an aged preclinical DMD animal model
Bengtsson, Niclas E., Crudele, Julie M., Klaiman, Jordan M., Halbert, Christine L., Hauschka, Stephen D., Chamberlain, Jeffrey S.
Published in Molecular therapy (01.06.2022)
Published in Molecular therapy (01.06.2022)
Get full text
Journal Article
Loading…
Loading…
Loading…
Loading…
An innovative CRISPR/Cas9 mouse model of human isolated microtia indicates the potential contribution of CNVs near HMX1 gene
Xing, Wenshan, Zhang, Jiao, Liu, Tun, Wang, Yue, Qian, Jin, Wang, Bingqing, Zhang, Yongbiao, Zhang, Qingguo
Published in International journal of pediatric otorhinolaryngology (01.12.2024)
Published in International journal of pediatric otorhinolaryngology (01.12.2024)
Get full text
Journal Article
Loading…
HIV-1 mRNA knockdown with CRISPR/CAS9 enhances neurocognitive function
McLaurin, Kristen A., Li, Hailong, Khalili, Kamel, Mactutus, Charles F., Booze, Rosemarie M.
Published in Journal of neurovirology (01.02.2024)
Published in Journal of neurovirology (01.02.2024)
Get full text
Journal Article
Loading…
Generation and Genetic Correction of USH2A c.2299delG Mutation in Patient-Derived Induced Pluripotent Stem Cells
Liu, Xuezhong, Lillywhite, Justin, Zhu, Wenliang, Huang, Zaohua, Clark, Anna M, Gosstola, Nicholas, Maguire, Colin T., Dykxhoorn, Derek, Chen, Zheng-Yi, Yang, Jun
Published in Genes (25.05.2021)
Published in Genes (25.05.2021)
Get full text
Journal Article