Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott–Aldrich syndrome
Magnani, A., Semeraro, M., Adam, F., Booth, C., Dupré, L., Morris, E. C., Gabrion, A., Roudaut, C., Borgel, D., Toubert, A., Clave, E., Abdo, C., Gorochov, G., Petermann, R., Guiot, M., Miyara, M., Moshous, D., Magrin, E., Denis, A., Suarez, F., Lagresle, C., Roche, A. M., Everett, J., Trinquand, A., Guisset, M., Bayford, J. Xu, Hacein-Bey-Abina, S., Kauskot, A., Elfeky, R., Rivat, C., Abbas, S., Gaspar, H. B., Macintyre, E., Picard, C., Bushman, F. D., Galy, A., Fischer, A., Six, E., Thrasher, A. J., Cavazzana, M.
Published in Nature Medicine (01.01.2022)
Published in Nature Medicine (01.01.2022)
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Allogeneic and autologous transplantation for haematological diseases, solid tumours and immune disorders: current practice in Europe 2009
Ljungman, P, Bregni, M, Brune, M, Cornelissen, J, Witte, T de, Dini, G, Einsele, H, Gaspar, H B, Gratwohl, A, Passweg, J, Peters, C, Rocha, V, Saccardi, R, Schouten, H, Sureda, A, Tichelli, A, Velardi, A, Niederwieser, D
Published in Bone marrow transplantation (Basingstoke) (01.02.2010)
Published in Bone marrow transplantation (Basingstoke) (01.02.2010)
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Hematopoietic SCT in Europe: data and trends in 2012 with special consideration of pediatric transplantation
Passweg, J R, Baldomero, H, Peters, C, Gaspar, H B, Cesaro, S, Dreger, P, Duarte, R F, Falkenburg, J H F, Farge-Bancel, D, Gennery, A, Halter, J, Kröger, N, Lanza, F, Marsh, J, Mohty, M, Sureda, A, Velardi, A, Madrigal, A
Published in Bone marrow transplantation (Basingstoke) (01.06.2014)
Published in Bone marrow transplantation (Basingstoke) (01.06.2014)
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Impact of viral reactivations in the era of pre-emptive antiviral drug therapy following allogeneic haematopoietic SCT in paediatric recipients
Hiwarkar, P, Gaspar, H B, Gilmour, K, Jagani, M, Chiesa, R, Bennett-Rees, N, Breuer, J, Rao, K, Cale, C, Goulden, N, Davies, G, Amrolia, P, Veys, P, Qasim, W
Published in Bone marrow transplantation (Basingstoke) (01.06.2013)
Published in Bone marrow transplantation (Basingstoke) (01.06.2013)
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Author Correction: Long-term safety and efficacy of lentiviral hematopoietic stem/progenitor cell gene therapy for Wiskott–Aldrich syndrome
Magnani, A., Semeraro, M., Adam, F., Booth, C., Dupré, L., Morris, E. C., Gabrion, A., Roudaut, C., Borgel, D., Toubert, A., Clave, E., Abdo, C., Gorochov, G., Petermann, R., Guiot, M., Miyara, M., Moshous, D., Magrin, E., Denis, A., Suarez, F., Lagresle, C., Roche, A. M., Everett, J., Trinquand, A., Guisset, M., Bayford, J. Xu, Hacein-Bey-Abina, S., Kauskot, A., Elfeky, R., Rivat, C., Abbas, S., Gaspar, H. B., Macintyre, E., Picard, C., Bushman, F. D., Galy, A., Fischer, A., Six, E., Thrasher, A. J., Cavazzana, M.
Published in Nature Medicine (01.10.2022)
Published in Nature Medicine (01.10.2022)
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The Case for Mandatory Newborn Screening for Severe Combined Immunodeficiency (SCID)
Gaspar, H. B., Hammarström, L., Mahlaoui, N., Borte, M., Borte, S.
Published in Journal of clinical immunology (01.05.2014)
Published in Journal of clinical immunology (01.05.2014)
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Social outcome in children treated by haematopoietic cell transplant for congenital immunodeficiency
Skucek, E, Butler, S, Gaspar, H B, Titman, P
Published in Bone marrow transplantation (Basingstoke) (01.10.2011)
Published in Bone marrow transplantation (Basingstoke) (01.10.2011)
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Outcomes of splenectomy in patients with common variable immunodeficiency (CVID): a survey of 45 patients
Wong, G. K., Goldacker, S., Winterhalter, C., Grimbacher, B., Chapel, H., Lucas, M., Alecsandru, D., McEwen, D., Quinti, I., Martini, H., Schmidt, R. E., Ernst, D., Espanol, T., Vidaller, A., Carbone, J., Fernandez‐Cruz, E., Lougaris, V., Plebani, A., Kutukculer, N., Gonzalez‐Granado, L. I., Contreras, R., Kiani‐Alikhan, S., Ibrahim, M. A. A., Litzman, J., Jones, A., Gaspar, H. B., Hammarstrom, L., Baumann, U., Warnatz, K., Huissoon, A. P.
Published in Clinical and experimental immunology (01.04.2013)
Published in Clinical and experimental immunology (01.04.2013)
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Pathology of astrovirus associated diarrhoea in a paediatric bone marrow transplant recipient
Sebire, N J, Malone, M, Shah, N, Anderson, G, Gaspar, H B, Cubitt, W D
Published in Journal of clinical pathology (01.09.2004)
Published in Journal of clinical pathology (01.09.2004)
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Prevalence of SAP gene defects in male patients diagnosed with common variable immunodeficiency
EASTWOOD, D., GILMOUR, K. C., NISTALA, K., MEANEY, C., CHAPEL, H., SHERRELL, Z., WEBSTER, A. D., DAVIES, E. G., JONES, A., GASPAR, H. B.
Published in Clinical and experimental immunology (01.09.2004)
Published in Clinical and experimental immunology (01.09.2004)
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Allogeneic stem cell transplantation in X-linked lymphoproliferative disease: two cases in one family and review of the literature
LANKESTER, A. C, VISSER, L. F. A, HARTWIG, N. G, BREDIUS, R. G. M, GASPAR, H. B, VAN DER BURG, M, VAN TOL, M. J. D, GROSS, T. G, EGELER, R. M
Published in Bone marrow transplantation (Basingstoke) (01.07.2005)
Published in Bone marrow transplantation (Basingstoke) (01.07.2005)
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T cell transduction and suicide with an enhanced mutant thymidine kinase
QASIM, W, THRASHER, A. J, BUDDLE, J, KINNON, C, BLACK, M. E, GASPAR, H. B
Published in Gene therapy (01.06.2002)
Published in Gene therapy (01.06.2002)
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Kinase mutant Btk results in atypical X‐linked agammaglobulinaemia phenotype
Gaspar, H. B., Ferrando, M., Caragol, I., Hernandez, M., Bertran, J. M., De gracia, X., Lester, T., Kinnon, C., Ashton, E., Espanol, T.
Published in Clinical and experimental immunology (01.05.2000)
Published in Clinical and experimental immunology (01.05.2000)
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