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Clinical Proof of Concept for a Novel Hepatocyte-Targeting GalNAc-siRNA Conjugate
Zimmermann, Tracy S., Karsten, Verena, Chan, Amy, Chiesa, Joseph, Boyce, Malcolm, Bettencourt, Brian R., Hutabarat, Renta, Nochur, Saraswathy, Vaishnaw, Akshay, Gollob, Jared
Published in Molecular therapy (04.01.2017)
Published in Molecular therapy (04.01.2017)
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First-in-human study to evaluate the safety, pharmacokinetics (PK), and pharmacodynamics (PD) of RBD4059, a GalNAc-siRNA drug targeting coagulation factor XI (FXI), in healthy subjects
Gabrielsen, A, Feng, Z, Fu, J, Ueckert, S, Egnell, L, Wikstrom, J, Wei, W, Chen, G, Friend, R, Zhan, H, Liang, Z, Gao, S, Gan, L
Published in European heart journal (28.10.2024)
Published in European heart journal (28.10.2024)
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Preclinical and Clinical Pharmacokinetics of JNJ-75220795, an siRNA Therapeutic Targeting PNPLA3, for Metabolic Dysfunction-Associated Steatohepatitis
Jeon, Jae Yoon, Ayyar, Vivaswath S, Ouchi, Shohei, Fabbrini, Elisa, Koshkina, Anastasiya, Prusakiewicz, Jeffery J, Dallas, Jed, Yang, Txheng, Jian, Wenying, Kang, Lijuan, Cofsky, Korin, Rady, Brian, Tamamura, Ryo, Saito, Yuki, Yamashita, Aimi, Vaughan, Tamisha, Wendel, Susan, Makimura, Hideo, Csonka, Dénes, Goyal, Navin
Published in Journal of clinical pharmacology (01.05.2025)
Published in Journal of clinical pharmacology (01.05.2025)
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SLN124, a GalNAc conjugated 19‐mer siRNA targeting tmprss6, reduces plasma iron and increases hepcidin levels of healthy volunteers
Porter, John B., Scrimgeour, Alison, Martinez, Alberto, James, Leo, Aleku, Manuela, Wilson, Rosamund, Muckenthaler, Martina, Boyce, Malcolm, Wilkes, Denise, Schaeper, Ute, Campion, Giles V.
Published in American journal of hematology (01.09.2023)
Published in American journal of hematology (01.09.2023)
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The Nonclinical Safety Profile of GalNAc-conjugated RNAi Therapeutics in Subacute Studies
Janas, Maja M., Harbison, Carole E., Perry, Victoria K., Carito, Brenda, Sutherland, Jessica E., Vaishnaw, Akshay K., Keirstead, Natalie D., Warner, Garvin
Published in Toxicologic pathology (01.10.2018)
Published in Toxicologic pathology (01.10.2018)
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Alnylam Pharmaceuticals Reports 4Q and Full Year 2013 Financial Results
Published in Health & Beauty Close - Up
(18.02.2014)
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BioMedReports: Alnylam Receives European Medicines Agency PRIME Designation for Accelerated Assessment of
Published in Newstex Trade & Industry Blogs
(01.03.2017)
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Alnylam and Collaborators Release Clinical Trial Results in The Lancet
Published in Health & Beauty Close - Up
(08.10.2013)
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