Search Results - "GRAY, STEVEN JAMES" :: K.UTB vyhledávací portál

Recent progress and considerations for AAV gene therapies targeting the central nervous system

by Lykken, Erik Allen, Shyng, Charles, Edwards, Reginald James, Rozenberg, Alejandra, Gray, Steven James
Published in Journal of neurodevelopmental disorders (18.05.2018)

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Combination therapy utilizing shRNA knockdown and an optimized resistant transgene for rescue of diseases caused by misfolded proteins

by Li, Chengwen, Xiao, Pingjie, Gray, Steven James, Weinberg, Marc Scott, Samulski, R. Jude
Published in Proceedings of the National Academy of Sciences - PNAS (23.08.2011)

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피드백이 가능한 합성 유전자, 표적 시드 매치 카세트, 및 그 용도

by GRAY STEVEN JAMES, SINNETT SARAH
Year of Publication 09.04.2021

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Patent

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UBE3A 유전자 및 발현 카세트 및 이들의 용도

by JUDSON MATTHEW, PHILPOT BENJAMIN DAVID, GRAY STEVEN JAMES, SHYNG CHARLES
Year of Publication 31.12.2021

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Patent

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Gene therapy and neurodevelopmental disorders

by Gray, Steven James
Published in Neuropharmacology (01.05.2013)

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Viral expression cassette elements to enhance transgene target specificity and expression in gene therapy

by Powell, Sara Kathleen, Rivera-Soto, Ricardo, Gray, Steven James
Published in Discovery medicine (01.01.2015)

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Enhancing geospatial data : collecting and visualising user-generated content through custom toolkits and cloud computing workflows

by Gray, Steven James
Year of Publication 2023

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Dissertation

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Insights into the Pathogenesis and Treatment of Krabbe Disease

by Bongarzone, Ernesto Roque, Escolar, Maria Luisa, Gray, Steven James, Kafri, Tal, Vite, Charles Herman, Sands, Mark Steven
Published in Pediatric endocrinology reviews : PER (01.06.2016)

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Journal Article