Selexipag: an oral, selective prostacyclin receptor agonist for the treatment of pulmonary arterial hypertension
SIMONNEAU, Gérald, TORBICKI, Adam, GIORGINO, Ruben, LANG, Irene M, HOEPER, Marius M, DELCROIX, Marion, KARLOCAI, Kristóf, GALIE, Nazzareno, DEGANO, Bruno, BONDERMAN, Diana, KURZYNA, Marcin, EFFICACE, Michela
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Published in The European respiratory journal (01.10.2012)
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High prevalence of asymptomatic vertebral fractures in post-menopausal women receiving chronic glucocorticoid therapy: A cross-sectional outpatient study
Angeli, Alberto, Guglielmi, Giuseppe, Dovio, Andrea, Capelli, Giovanni, de Feo, Daniela, Giannini, Sandro, Giorgino, Ruben, Moro, Luigi, Giustina, Andrea
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Published in Bone (New York, N.Y.) (01.08.2006)
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Evaluation of miglustat as maintenance therapy after enzyme therapy in adults with stable type 1 Gaucher disease: a prospective, open-label non-inferiority study
Cox, Timothy M, Amato, Dominick, Hollak, Carla Em, Luzy, Cecile, Silkey, Mariabeth, Giorgino, Ruben, Steiner, Robert D
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The effect of age, weight, and lifestyle factors on calcaneal quantitative ultrasound: the ESOPO study
ADAMI, Silvano, GIANNINI, Sandro, GIORGINO, Ruben, ISAIA, Giancarlo, MAGGI, Stefania, SINIGAGLIA, Luigi, FILIPPONI, Paolo, CREPALDI, Gaetano, DI MUNNO, Ombretta
Published in Osteoporosis international (01.03.2003)
Published in Osteoporosis international (01.03.2003)
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First-in-human single-dose study of nizubaglustat, a dual inhibitor of ceramide glucosyltransferase and non-lysosomal glucosylceramidase: Safety, tolerability, pharmacokinetics, and pharmacodynamics of single ascending and multiple doses in healthy adults
Paquet Luzy, Cecile, Doppler, Emilie, Polasek, Thomas M., Giorgino, Ruben
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Published in Molecular genetics and metabolism (01.01.2024)
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Miglustat in adult and juvenile patients with Niemann–Pick disease type C: Long-term data from a clinical trial
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Published in Molecular genetics and metabolism (01.04.2010)
Published in Molecular genetics and metabolism (01.04.2010)
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Bingaman, Amanda, Waggoner, Christine, Andrews, Sara M., Pangonis, Diana, Trad, Marie, Giugliani, Roberto, Giorgino, Ruben, Jarnes, Jeanine, Vakili, Rojan, Ballard, Victoria, Peay, Holly L.
Published in American journal of medical genetics. Part A (01.02.2023)
Published in American journal of medical genetics. Part A (01.02.2023)
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Elsiglutide in the primary prevention of chemotherapy (CT)-induced diarrhea in patients with colorectal cancer (CRC) receiving 5-fluorouracil (5-FU)-based CT: A multinational, randomized, double-blind, placebo-controlled study
Karthaus, Meinolf, Fedyanin, Mikhail, Bondarenko, Igor, Chessari, Salvatore, Spezia, Riccardo, Giorgino, Ruben
Published in Journal of clinical oncology (20.05.2017)
Published in Journal of clinical oncology (20.05.2017)
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Body weight response with anamorelin in advanced non-small cell lung cancer (NSCLC) patients with anorexia/cachexia: Pooled analysis of two phase III trials
Currow, David Christopher, Temel, Jennifer S., Abernethy, Amy Pickar, Friend, John, Giorgino, Ruben
Published in Journal of clinical oncology (20.05.2017)
Published in Journal of clinical oncology (20.05.2017)
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Long-term miglustat therapy in children with Niemann-Pick disease type C
Patterson, Marc C, Vecchio, Darleen, Jacklin, Elizabeth, Abel, Larry, Chadha-Boreham, Harbajan, Luzy, Cecile, Giorgino, Ruben, Wraith, James E
Published in Journal of child neurology (01.03.2010)
Published in Journal of child neurology (01.03.2010)
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Efficacy of anamorelin in cachectic patients with non-small cell lung cancer (NSCLC) and low BMI (< 20 kg/m 2 ): Post-hoc analysis of two phase III studies
Currow, David Christopher, Temel, Jennifer S., Abernethy, Amy Pickar, Giorgino, Ruben, Friend, John, Fearon, Kenneth
Published in Journal of clinical oncology (09.10.2016)
Published in Journal of clinical oncology (09.10.2016)
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Anamorelin in cachectic patients with non-small cell lung cancer (NSCLC) and low BMI (< 20 kg/m 2 ): A pooled efficacy data analysis of two phase 3 studies
Currow, David Christopher, Temel, Jennifer S., Giorgino, Ruben, Abernethy, Amy Pickar, Friend, John, Fearon, Kenneth
Published in Journal of clinical oncology (20.05.2016)
Published in Journal of clinical oncology (20.05.2016)
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Pracinostat plus azacitidine in older patients with newly diagnosed acute myeloid leukemia: results of a phase 2 study
Garcia-Manero, Guillermo, Abaza, Yasmin, Takahashi, Koichi, Medeiros, Bruno C., Arellano, Martha, Khaled, Samer K., Patnaik, Mrinal, Odenike, Olatoyosi, Sayar, Hamid, Tummala, Mohan, Patel, Prapti, Maness-Harris, Lori, Stuart, Robert, Traer, Elie, Karamlou, Kasra, Yacoub, Abdulraheem, Ghalie, Richard, Giorgino, Ruben, Atallah, Ehab
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Published in Blood advances (26.02.2019)
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종양의 치료를 위한 4-아미노-N-[4--7H-피롤로[2,3-d]피리미딘-5-카르복스아미드의 사용 방법
KATO MASANORI, DORIA SIMONA, GIULIANO CLAUDIO, MIYAZAKI ISAO, BONIFACIO ANNALISA, GIORGINO RUBEN, IGARASHI MIHARU, BERNAREGGI ALBERTO, LOVATI EMANUELA
Year of Publication 24.07.2023
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Year of Publication 24.07.2023
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MEDICAL TREATMENTS BASED ON ANAMORELIN
LU MING, BARONI ENRICO, MANN WILLIAM, FRIEND JOHN, POLVINO WILLIAM, GIORGINO RUBEN, ALLEN SUZAN, DUUS ELIZABETH
Year of Publication 01.04.2021
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Year of Publication 01.04.2021
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MEDICAL TREATMENTS BASED ON ANAMORELIN
LU MING, BARONI ENRICO, MANN WILLIAM, FRIEND JOHN, POLVINO WILLIAM, GIORGINO RUBEN, ALLEN SUZAN, DUUS ELIZABETH
Year of Publication 25.07.2018
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Year of Publication 25.07.2018
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Miglustat Therapy in Type 1 Gaucher Disease: Long-Term Treatment Experience From a Multicenter, Retrospective Cohort Study
Kuter, David J., Mehta, Atul, Hollak, Carla, Giraldo, Pilar, Hughes, Derralynn, Belmatoug, Nadia, Brand, Monika, Muller, Audrey, Schaaf, Berthold, Giorgino, Ruben, Zimran, Ari
Published in Blood (18.11.2011)
Published in Blood (18.11.2011)
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