Recombination-activating gene 1 ( Rag1 )–deficient mice with severe combined immunodeficiency treated with lentiviral gene therapy demonstrate autoimmune Omenn-like syndrome
van Til, Niek P., PhD, Sarwari, Roya, MSc, Visser, Trudi P., BSc, Hauer, Julia, MD, Lagresle-Peyrou, Chantal, PhD, van der Velden, Guus, BSc, Malshetty, Vidyasagar, PhD, Cortes, Patricia, PhD, Jollet, Arnaud, PhD, Danos, Olivier, PhD, Cassani, Barbara, PhD, Zhang, Fang, PhD, Thrasher, Adrian J., MD, PhD, Fontana, Elena, PhD, Poliani, Pietro L., MD, PhD, Cavazzana, Marina, MD, PhD, Verstegen, Monique M.A., PhD, Villa, Anna, MD, PhD, Wagemaker, Gerard, PhD
Published in Journal of allergy and clinical immunology (01.04.2014)
Published in Journal of allergy and clinical immunology (01.04.2014)
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In vivo expansion of co-transplanted T cells impacts on tumor re-initiating activity of human acute myeloid leukemia in NSG mice
von Bonin, Malte, Wermke, Martin, Cosgun, Kadriye Nehir, Thiede, Christian, Bornhauser, Martin, Wagemaker, Gerard, Waskow, Claudia
Published in PloS one (09.04.2013)
Published in PloS one (09.04.2013)
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Lentiviral Hematopoietic Stem Cell Gene Therapy Corrects Murine Pompe Disease
Stok, Merel, de Boer, Helen, Huston, Marshall W., Jacobs, Edwin H., Roovers, Onno, Visser, Trudi P., Jahr, Holger, Duncker, Dirk J., van Deel, Elza D., Reuser, Arnold J.J., van Til, Niek P., Wagemaker, Gerard
Published in Molecular therapy. Methods & clinical development (12.06.2020)
Published in Molecular therapy. Methods & clinical development (12.06.2020)
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Lentiviral gene therapy of murine hematopoietic stem cells ameliorates the Pompe disease phenotype
van Til, Niek P., Stok, Merel, Aerts Kaya, Fatima S.F., de Waard, Monique C., Farahbakhshian, Elnaz, Visser, Trudi P., Kroos, Marian A., Jacobs, Edwin H., Willart, Monique A., van der Wegen, Pascal, Scholte, Bob J., Lambrecht, Bart N., Duncker, Dirk J., van der Ploeg, Ans T., Reuser, Arnold J.J., Verstegen, Monique M., Wagemaker, Gerard
Published in Blood (01.07.2010)
Published in Blood (01.07.2010)
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Mobilization of hepatic mesenchymal stem cells from human liver grafts
Pan, Qiuwei, Fouraschen, Suomi M. G., Kaya, Fatima S. F. Aerts, Verstegen, Monique M., Pescatori, Mario, Stubbs, Andrew P., van IJcken, Wilfred, van der Sloot, Antoine, Smits, Ron, Kwekkeboom, Jaap, Metselaar, Herold J., Kazemier, Geert, de Jonge, Jeroen, Tilanus, Hugo W., Wagemaker, Gerard, Janssen, Harry L. A., van der Laan, Luc J. W.
Published in Liver transplantation (01.05.2011)
Published in Liver transplantation (01.05.2011)
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Correction of Murine SCID-X1 by Lentiviral Gene Therapy Using a Codon-optimized IL2RG Gene and Minimal Pretransplant Conditioning
Huston, Marshall W, van Til, Niek P, Visser, Trudi P, Arshad, Shazia, Brugman, Martijn H, Cattoglio, Claudia, Nowrouzi, Ali, Li, Yuedan, Schambach, Axel, Schmidt, Manfred, Baum, Christopher, von Kalle, Christof, Mavilio, Fulvio, Zhang, Fang, Blundell, Mike P, Thrasher, Adrian J, Verstegen, Monique MA, Wagemaker, Gerard
Published in Molecular therapy (01.10.2011)
Published in Molecular therapy (01.10.2011)
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Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE
Yadak, Rana, Cabrera-Pérez, Raquel, Torres-Torronteras, Javier, Bugiani, Marianna, Haeck, Joost C, Huston, Marshall W, Bogaerts, Elly, Goffart, Steffi, Jacobs, Edwin H, Stok, Merel, Leonardelli, Lorena, Biasco, Luca, Verdijk, Robert M, Bernsen, Monique R, Ruijter, George, Martí, Ramon, Wagemaker, Gerard, van Til, Niek P, de Coo, Irenaeus F M
Published in Molecular therapy. Methods & clinical development (16.03.2018)
Published in Molecular therapy. Methods & clinical development (16.03.2018)
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5-Androstene-3β,17β-diol Promotes Recovery of Immature Hematopoietic Cells Following Myelosuppressive Radiation and Synergizes With Thrombopoietin
Aerts-Kaya, Fatima S.F., MD, PhD, Visser, Trudi P., BSc, Arshad, Shazia, BSc, Frincke, James, PhD, Stickney, Dwight R., MD, Reading, Chris L., PhD, Wagemaker, Gerard, PhD
Published in International journal of radiation oncology, biology, physics (01.11.2012)
Published in International journal of radiation oncology, biology, physics (01.11.2012)
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Long-Term Effects of Irradiation Before Adulthood on Reproductive Function in the Male Rhesus Monkey
DE ROOIJ, Dirk G, VAN DE KANT, Henk J. G, DOL, Roelof, WAGEMAKER, Gerard, VAN BUUL, Paul P. W, VAN DUIJN-GOEDHART, Annemarie, DE JONG, Frank H, BROERSE, Johan J
Published in Biology of reproduction (01.02.2002)
Published in Biology of reproduction (01.02.2002)
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Thrombopoietin promotes hematopoietic recovery and survival after high-dose whole body irradiation
Mouthon, Marc-André, Van der Meeren, Anne, Gaugler, Marie-Hélène, Visser, Trudi P, Squiban, Claire, Gourmelon, Patrick, Wagemaker, Gerard
Published in International journal of radiation oncology, biology, physics (01.03.1999)
Published in International journal of radiation oncology, biology, physics (01.03.1999)
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The outcome of local radiation injuries: 14 years of follow-up after the Chernobyl accident
Gottlöber, P, Steinert, M, Weiss, M, Bebeshko, V, Belyi, D, Nadejina, N, Stefani, F H, Wagemaker, G, Fliedner, T M, Peter, R U
Published in Radiation research (01.03.2001)
Published in Radiation research (01.03.2001)
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Simultaneous Infection with Retroviruses Pseudotyped with Different Envelope Proteins Bypasses Viral Receptor Interference Associated with Colocalization of gp70 and Target Cells on Fibronectin CH-296
MacNeill, E C, Hanenberg, H, Pollok, K E, van der Loo, J C, Bierhuizen, M F, Wagemaker, G, Williams, D A
Published in Journal of Virology (01.05.1999)
Published in Journal of Virology (01.05.1999)
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Ticlopidine inhibits the prothrombotic effects of thrombopoietin and ameliorates survival after supralethal total body irradiation
Mouthon, Marc-André, Gaugler, Marie-Hélène, Vandamme, Marie, Gourmelon, Patrick, Wagemaker, Gerard, Van der Meeren, Anne
Published in Thrombosis and haemostasis (01.02.2002)
Published in Thrombosis and haemostasis (01.02.2002)
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Efficacy of lentivirus-mediated gene therapy in an Omenn syndrome recombination-activating gene 2 mouse model is not hindered by inflammation and immune dysregulation
Capo, Valentina, Castiello, Maria Carmina, Fontana, Elena, Penna, Sara, Bosticardo, Marita, Draghici, Elena, Poliani, Luigi P., Sergi Sergi, Lucia, Rigoni, Rosita, Cassani, Barbara, Zanussi, Monica, Carrera, Paola, Uva, Paolo, Dobbs, Kerry, Sacchetti, Nicolò, Notarangelo, Luigi D., van Til, Niek P., Wagemaker, Gerard, Villa, Anna
Published in Journal of allergy and clinical immunology (01.09.2018)
Published in Journal of allergy and clinical immunology (01.09.2018)
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