Elexacaftor–Tezacaftor–Ivacaftor for Cystic Fibrosis with a Single Phe508del Allele
Middleton, Peter G, Mall, Marcus A, Dřevínek, Pavel, Lands, Larry C, McKone, Edward F, Polineni, Deepika, Ramsey, Bonnie W, Taylor-Cousar, Jennifer L, Tullis, Elizabeth, Vermeulen, François, Marigowda, Gautham, McKee, Charlotte M, Moskowitz, Samuel M, Nair, Nitin, Savage, Jessica, Simard, Christopher, Tian, Simon, Waltz, David, Xuan, Fengjuan, Rowe, Steven M, Jain, Raksha
Published in The New England journal of medicine (07.11.2019)
Published in The New England journal of medicine (07.11.2019)
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VX-445–Tezacaftor–Ivacaftor in Patients with Cystic Fibrosis and One or Two Phe508del Alleles
Keating, Dominic, Marigowda, Gautham, Burr, Lucy, Daines, Cori, Mall, Marcus A, McKone, Edward F, Ramsey, Bonnie W, Rowe, Steven M, Sass, Laura A, Tullis, Elizabeth, McKee, Charlotte M, Moskowitz, Samuel M, Robertson, Sarah, Savage, Jessica, Simard, Christopher, Van Goor, Fredrick, Waltz, David, Xuan, Fengjuan, Young, Tim, Taylor-Cousar, Jennifer L
Published in The New England journal of medicine (25.10.2018)
Published in The New England journal of medicine (25.10.2018)
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Lumacaftor–Ivacaftor in Patients with Cystic Fibrosis Homozygous for Phe508del CFTR
Wainwright, Claire E, Elborn, J. Stuart, Ramsey, Bonnie W, Marigowda, Gautham, Huang, Xiaohong, Cipolli, Marco, Colombo, Carla, Davies, Jane C, De Boeck, Kris, Flume, Patrick A, Konstan, Michael W, McColley, Susanna A, McCoy, Karen, McKone, Edward F, Munck, Anne, Ratjen, Felix, Rowe, Steven M, Waltz, David, Boyle, Michael P
Published in The New England journal of medicine (16.07.2015)
Published in The New England journal of medicine (16.07.2015)
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Efficacy and safety of lumacaftor and ivacaftor in patients aged 6-11 years with cystic fibrosis homozygous for F508del-CFTR: a randomised, placebo-controlled phase 3 trial
Ratjen, Felix, Hug, Christopher, Marigowda, Gautham, Tian, Simon, Huang, Xiaohong, Stanojevic, Sanja, Milla, Carlos E, Robinson, Paul D, Waltz, David, Davies, Jane C
Published in The lancet respiratory medicine (01.07.2017)
Published in The lancet respiratory medicine (01.07.2017)
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Active Albuterol or Placebo, Sham Acupuncture, or No Intervention in Asthma
Wechsler, Michael E, Kelley, John M, Boyd, Ingrid O.E, Dutile, Stefanie, Marigowda, Gautham, Kirsch, Irving, Israel, Elliot, Kaptchuk, Ted J
Published in The New England journal of medicine (14.07.2011)
Published in The New England journal of medicine (14.07.2011)
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Assessment of safety and efficacy of long-term treatment with combination lumacaftor and ivacaftor therapy in patients with cystic fibrosis homozygous for the F508del-CFTR mutation (PROGRESS): a phase 3, extension study
Konstan, Michael W, McKone, Edward F, Moss, Richard B, Marigowda, Gautham, Tian, Simon, Waltz, David, Huang, Xiaohong, Lubarsky, Barry, Rubin, Jaime, Millar, Stefanie J, Pasta, David J, Mayer-Hamblett, Nicole, Goss, Christopher H, Morgan, Wayne, Sawicki, Gregory S
Published in The lancet respiratory medicine (01.02.2017)
Published in The lancet respiratory medicine (01.02.2017)
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Efficacy and safety of lumacaftor/ivacaftor combination therapy in patients with cystic fibrosis homozygous for Phe508del CFTR by pulmonary function subgroup: a pooled analysis
Elborn, J Stuart, Ramsey, Bonnie W, Boyle, Michael P, Konstan, Michael W, Huang, Xiaohong, Marigowda, Gautham, Waltz, David, Wainwright, Claire E
Published in The lancet respiratory medicine (01.08.2016)
Published in The lancet respiratory medicine (01.08.2016)
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Exhaled breath condensate eicosanoid levels associate with asthma and its severity
Kazani, Shamsah, MD, Planaguma, Anna, PhD, Ono, Emiko, PhD, Bonini, Matteo, MD, Zahid, Muhammad, MBBS, Marigowda, Gautham, MBBS, Wechsler, Michael E., MD, Levy, Bruce D., MD, Israel, Elliot, MD
Published in Journal of allergy and clinical immunology (01.09.2013)
Published in Journal of allergy and clinical immunology (01.09.2013)
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Clinical development of triple-combination CFTR modulators for cystic fibrosis patients with one or two F508del alleles
Taylor-Cousar, Jennifer L, Mall, Marcus A, Ramsey, Bonnie W, McKone, Edward F, Tullis, Elizabeth, Marigowda, Gautham, McKee, Charlotte M, Waltz, David, Moskowitz, Samuel M, Savage, Jessica, Xuan, Fengjuan, Rowe, Steven M
Published in ERJ open research (01.04.2019)
Published in ERJ open research (01.04.2019)
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Natural killer T cells in the lungs of patients with asthma
Matangkasombut, Ponpan, MD, Marigowda, Gautham, MD, MPH, Ervine, Aaron, MD, Idris, Luaie, MD, Pichavant, Muriel, PhD, Kim, Hye Young, PhD, Yasumi, Takahiro, MD, PhD, Wilson, S. Brian, MD, PhD, DeKruyff, Rosemarie H., PhD, Faul, John L., MD, Israel, Elliot, MD, Akbari, Omid, PhD, Umetsu, Dale T., MD, PhD
Published in Journal of allergy and clinical immunology (01.05.2009)
Published in Journal of allergy and clinical immunology (01.05.2009)
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Lumacaftor/Ivacaftor in Patients Aged 6-11 Years with Cystic Fibrosis and Homozygous for F508del-CFTR
Milla, Carlos E, Ratjen, Felix, Marigowda, Gautham, Liu, Fang, Waltz, David, Rosenfeld, Margaret
Published in American journal of respiratory and critical care medicine (01.04.2017)
Published in American journal of respiratory and critical care medicine (01.04.2017)
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Efficacy and safety of the elexacaftor plus tezacaftor plus ivacaftor combination regimen in people with cystic fibrosis homozygous for the F508del mutation: a double-blind, randomised, phase 3 trial
Heijerman, Harry G M, McKone, Edward F, Downey, Damian G, Van Braeckel, Eva, Rowe, Steven M, Tullis, Elizabeth, Mall, Marcus A, Welter, John J, Ramsey, Bonnie W, McKee, Charlotte M, Marigowda, Gautham, Moskowitz, Samuel M, Waltz, David, Sosnay, Patrick R, Simard, Christopher, Ahluwalia, Neil, Xuan, Fengjuan, Zhang, Yaohua, Taylor-Cousar, Jennifer L, McCoy, Karen S, McCoy, Karen, Donaldson, Scott, Walker, Seth, Chmiel, James, Rubenstein, Ronald, Froh, Deborah K., Neuringer, Isabel, Jain, Manu, Moffett, Kathryn, Taylor-Cousar, Jennifer L., Barnett, Bruce, Mueller, Gary, Flume, Patrick, Livingston, Floyd, Mehdi, Nighat, Teneback, Charlotte, Welter, John, Jain, Raksha, Kissner, Dana, Patel, Kapilkumar, Calimano, Francisco J., Johannes, Jimmy, Daines, Cori, Keens, Thomas, Scher, Herschel, Chittivelu, Subramanyam, Reddivalam, Sudhakar, Klingsberg, Ross Carl, Johnson, Larry G., Verhulst, Stijn, Macedo, Patricia, Downey, Damien, Connett, Gary, Nash, Edward, Withers, Nicholas, Lee, Timothy, Bakker, Marleen, Heijerman, Harry, Vermeulen, Francois, Van Braeckel, Eva, Knoop, Christiane, De Wachter, Elke, van der Meer, Renske, Merkus, Petrus, Majoor, Christof
Published in The Lancet (British edition) (23.11.2019)
Published in The Lancet (British edition) (23.11.2019)
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Journal Article
Lumacaftor/ivacaftor in patients with cystic fibrosis and advanced lung disease homozygous for F508del-CFTR
Taylor-Cousar, Jennifer L., Jain, Manu, Barto, Tara Lynn, Haddad, Tarik, Atkinson, Jeffrey, Tian, Simon, Tang, Rui, Marigowda, Gautham, Waltz, David, Pilewski, Joseph
Published in Journal of cystic fibrosis (01.03.2018)
Published in Journal of cystic fibrosis (01.03.2018)
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Safety, pharmacokinetics, and pharmacodynamics of lumacaftor and ivacaftor combination therapy in children aged 2-5 years with cystic fibrosis homozygous for F508del-CFTR: an open-label phase 3 study
McNamara, John J, McColley, Susanna A, Marigowda, Gautham, Liu, Fang, Tian, Simon, Owen, Caroline A, Stiles, David, Li, Chonghua, Waltz, David, Wang, Linda T, Sawicki, Gregory S
Published in The lancet respiratory medicine (01.04.2019)
Published in The lancet respiratory medicine (01.04.2019)
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Lumacaftor/Ivacaftor Treatment of Patients with Cystic Fibrosis Heterozygous for F508del-CFTR
Rowe, Steven M, McColley, Susanna A, Rietschel, Ernst, Li, Xiaolei, Bell, Scott C, Konstan, Michael W, Marigowda, Gautham, Waltz, David, Boyle, Michael P
Published in Annals of the American Thoracic Society (01.02.2017)
Published in Annals of the American Thoracic Society (01.02.2017)
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Measuring recovery in health-related quality of life during and after pulmonary exacerbations in patients with cystic fibrosis
Flume, Patrick A, Suthoff, Ellison D, Kosinski, Mark, Marigowda, Gautham, Quittner, Alexandra L
Published in Journal of cystic fibrosis (01.09.2019)
Published in Journal of cystic fibrosis (01.09.2019)
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836-P: Glucose-Dependent Insulin Production and Insulin-Independence in Type 1 Diabetes from Stem Cell–Derived, Fully Differentiated Islet Cells—Updated Data from the VX-880 Clinical Trial
REICHMAN, TREVOR W., RICORDI, CAMILLO, NAJI, ALI, MARKMANN, JAMES F., PERKINS, BRUCE A., WIJKSTROM, MARTIN, PARASKEVAS, STEVEN, BRUINSMA, BOTE, MARIGOWDA, GAUTHAM, SHIH, JUDY L., WANG, CHENKUN, MELTON, DOUGLAS, PAGLIUCA, FELICIA, SANNA, BASTIANO, KEAN, LESLIE S., PETERS, ANNE L., WITKOWSKI, PIOTR, RICKELS, MICHAEL R.
Published in Diabetes (New York, N.Y.) (23.06.2023)
Published in Diabetes (New York, N.Y.) (23.06.2023)
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259-OR: Stem Cell–Derived, Fully Differentiated Islet Cells for Type 1 Diabetes
MARKMANN, JAMES F., NAJI, ALI, RICKELS, MICHAEL R., ALBA, MARIA, MARIGOWDA, GAUTHAM, ROSS, LEORAH, WANG, CHENKUN, PAGLIUCA, FELICIA, SANNA, BASTIANO, KEAN, LESLIE S., PETERS, ANNE L., WITKOWSKI, PIOTR, RICORDI, CAMILLO
Published in Diabetes (New York, N.Y.) (01.06.2022)
Published in Diabetes (New York, N.Y.) (01.06.2022)
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