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Liu, Pengpeng, Liang, Shun-Qing, Zheng, Chunwei, Mintzer, Esther, Zhao, Yan G., Ponnienselvan, Karthikeyan, Mir, Aamir, Sontheimer, Erik J., Gao, Guangping, Flotte, Terence R., Wolfe, Scot A., Xue, Wen
Published in Nature communications (09.04.2021)
Published in Nature communications (09.04.2021)
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Results at 2 Years after Gene Therapy for RPE65-Deficient Leber Congenital Amaurosis and Severe Early-Childhood–Onset Retinal Dystrophy
Weleber, Richard G., MD, Pennesi, Mark E., MD, PhD, Wilson, David J., MD, Kaushal, Shalesh, MD, PhD, Erker, Laura R., PhD, Jensen, Lauren, MS, RN, McBride, Maureen T., BS, Flotte, Terence R., MD, Humphries, Margaret, RN, Calcedo, Roberto, PhD, Hauswirth, William W., PhD, Chulay, Jeffrey D., MD, Stout, J. Timothy, MD, PhD
Published in Ophthalmology (Rochester, Minn.) (01.07.2016)
Published in Ophthalmology (Rochester, Minn.) (01.07.2016)
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Women's Representation Among Members and Leaders of National Medical Specialty Societies
Jagsi, Reshma, Means, Olivia, Lautenberger, Diana, Jones, Rochelle D, Griffith, Kent A, Flotte, Terence R, Gordon, Lynn K, Rexrode, Kathryn M, Wagner, Lori W, Chatterjee, Archana
Published in Academic medicine (01.07.2020)
Published in Academic medicine (01.07.2020)
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Common pathways to Dean of Medicine at U.S. medical schools
Jacobson, Clare E, Beeler, Whitney H, Griffith, Kent A, Flotte, Terence R, Byington, Carrie L, Jagsi, Reshma
Published in PloS one (25.03.2021)
Published in PloS one (25.03.2021)
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Human gene therapy for RPE65 isomerase deficiency activates the retinoid cycle of vision but with slow rod kinetics
Cideciyan, Artur V, Aleman, Tomas S, Boye, Sanford L, Schwartz, Sharon B, Kaushal, Shalesh, Roman, Alejandro J, Pang, Ji-jing, Sumaroka, Alexander, Windsor, Elizabeth A.M, Wilson, James M, Flotte, Terence R, Fishman, Gerald A, Heon, Elise, Stone, Edwin M, Byrne, Barry J, Jacobson, Samuel G, Hauswirth, William W
Published in Proceedings of the National Academy of Sciences - PNAS (30.09.2008)
Published in Proceedings of the National Academy of Sciences - PNAS (30.09.2008)
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Long-term, efficient inhibition of microRNA function in mice using rAAV vectors
Xie, Jun, Ameres, Stefan L, Friedline, Randall, Hung, Jui-Hung, Zhang, Yu, Xie, Qing, Zhong, Li, Su, Qin, He, Ran, Li, Mengxin, Li, Huapeng, Mu, Xin, Zhang, Hongwei, Broderick, Jennifer A, Kim, Jason K, Weng, Zhiping, Flotte, Terence R, Zamore, Phillip D, Gao, Guangping
Published in Nature methods (04.03.2012)
Published in Nature methods (04.03.2012)
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Sustained transgene expression despite T lymphocyte responses in a clinical trial of rAAV1-AAT gene therapy
Brantly, Mark L, Chulay, Jeffrey D, Wang, Lili, Mueller, Christian, Humphries, Margaret, Spencer, L. Terry, Rouhani, Farshid, Conlon, Thomas J, Calcedo, Roberto, Betts, Michael R, Spencer, Carolyn, Byrne, Barry J, Wilson, James M, Flotte, Terence R
Published in Proceedings of the National Academy of Sciences - PNAS (22.09.2009)
Published in Proceedings of the National Academy of Sciences - PNAS (22.09.2009)
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Adeno-Associated Virus Type 2 and Hepatocellular Carcinoma?
Berns, Kenneth I, Byrne, Barry J, Flotte, Terence R, Gao, Guangping, Hauswirth, William W, Herzog, Roland W, Muzyczka, Nicholas, VandenDriessche, Thierry, Xiao, Xiao, Zolotukhin, Sergei, Srivastava, Arun
Published in Human gene therapy (01.12.2015)
Published in Human gene therapy (01.12.2015)
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MicroRNA-regulated, Systemically Delivered rAAV9: A Step Closer to CNS-restricted Transgene Expression
Xie, Jun, Xie, Qing, Zhang, Hongwei, Ameres, Stefan L, Hung, Jui-Hung, Su, Qin, He, Ran, Mu, Xin, Seher Ahmed, Seemin, Park, Soyeon, Kato, Hiroki, Li, Chengjian, Mueller, Christian, Mello, Craig C, Weng, Zhiping, Flotte, Terence R, Zamore, Phillip D, Gao, Guangping
Published in Molecular therapy (01.03.2011)
Published in Molecular therapy (01.03.2011)
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Modulating immune responses to AAV by expanded polyclonal T-regs and capsid specific chimeric antigen receptor T-regulatory cells
Arjomandnejad, Motahareh, Sylvia, Katelyn, Blackwood, Meghan, Nixon, Thomas, Tang, Qiushi, Muhuri, Manish, Gruntman, Alisha M., Gao, Guangping, Flotte, Terence R., Keeler, Allison M.
Published in Molecular therapy. Methods & clinical development (10.12.2021)
Published in Molecular therapy. Methods & clinical development (10.12.2021)
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Liver-directed SERPINA1 gene therapy attenuates progression of spontaneous and tobacco smoke-induced emphysema in α1-antitrypsin null mice
Zieger, Marina, Borel, Florie, Greer, Cynthia, Gernoux, Gwladys, Blackwood, Meghan, Flotte, Terence R., Mueller, Christian
Published in Molecular therapy. Methods & clinical development (09.06.2022)
Published in Molecular therapy. Methods & clinical development (09.06.2022)
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Adeno-Associated Virus Neutralizing Antibodies in Large Animals and Their Impact on Brain Intraparenchymal Gene Transfer
Wang, Dan, Zhong, Li, Li, Mengxin, Li, Jia, Tran, Karen, Ren, Lingzhi, He, Ran, Xie, Jun, Moser, Richard P, Fraser, Cara, Kuchel, Tim, Sena-Esteves, Miguel, Flotte, Terence R, Aronin, Neil, Gao, Guangping
Published in Molecular therapy. Methods & clinical development (14.12.2018)
Published in Molecular therapy. Methods & clinical development (14.12.2018)
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