A plasma microRNA signature as a biomarker for acquired aplastic anemia
Hosokawa, Kohei, Kajigaya, Sachiko, Feng, Xingmin, Desierto, Marie J, Fernandez Ibanez, Maria Del Pilar, Rios, Olga, Weinstein, Barbara, Scheinberg, Phillip, Townsley, Danielle M, Young, Neal S
Published in Haematologica (Roma) (01.01.2017)
Published in Haematologica (Roma) (01.01.2017)
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Journal Article
Abnormal RNA splicing and genomic instability after induction of DNMT3A mutations by CRISPR/Cas9 gene editing
Banaszak, Lauren G., Giudice, Valentina, Zhao, Xin, Wu, Zhijie, Gao, Shouguo, Hosokawa, Kohei, Keyvanfar, Keyvan, Townsley, Danielle M., Gutierrez-Rodrigues, Fernanda, Fernandez Ibanez, Maria del Pilar, Kajigaya, Sachiko, Young, Neal S.
Published in Blood cells, molecules, & diseases (01.03.2018)
Published in Blood cells, molecules, & diseases (01.03.2018)
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Journal Article
Single-cell RNA-seq reveals a distinct transcriptome signature of aneuploid hematopoietic cells
Zhao, Xin, Gao, Shouguo, Wu, Zhijie, Kajigaya, Sachiko, Feng, Xingmin, Liu, Qingguo, Townsley, Danielle M., Cooper, James, Chen, Jinguo, Keyvanfar, Keyvan, Fernandez Ibanez, Maria del Pilar, Wang, Xujing, Young, Neal S.
Published in Blood (21.12.2017)
Published in Blood (21.12.2017)
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Journal Article
Circulating S100A8 and S100A9 protein levels in plasma of patients with acquired aplastic anemia and myelodysplastic syndromes
Giudice, Valentina, Wu, Zhijie, Kajigaya, Sachiko, Fernandez Ibanez, Maria del Pilar, Rios, Olga, Cheung, Foo, Ito, Sawa, Young, Neal S.
Published in Cytokine (Philadelphia, Pa.) (01.01.2019)
Published in Cytokine (Philadelphia, Pa.) (01.01.2019)
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Journal Article
Deep sequencing and flow cytometric characterization of expanded effector memory CD8 + CD57 + T cells frequently reveals T-cell receptor Vβ oligoclonality and CDR3 homology in acquired aplastic anemia
Giudice, Valentina, Feng, Xingmin, Lin, Zenghua, Hu, Wei, Zhang, Fanmao, Qiao, Wangmin, Ibanez, Maria Del Pilar Fernandez, Rios, Olga, Young, Neal S
Published in Haematologica (Roma) (01.05.2018)
Published in Haematologica (Roma) (01.05.2018)
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Journal Article
Circulating exosomal microRNAs in acquired aplastic anemia and myelodysplastic syndromes
Giudice, Valentina, Banaszak, Lauren G, Gutierrez-Rodrigues, Fernanda, Kajigaya, Sachiko, Panjwani, Reema, Ibanez, Maria Del Pilar Fernandez, Rios, Olga, Bleck, Christopher K, Stempinski, Erin S, Raffo, Diego Quinones, Townsley, Danielle M, Young, Neal S
Published in Haematologica (Roma) (01.07.2018)
Published in Haematologica (Roma) (01.07.2018)
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Journal Article
Oligoclonal Expansion of Effector Memory CD8+CD57+ T Cells May Sustain Bone Marrow Destruction in Aplastic Anemia
Giudice, Valentina, Feng, Xingmin, Zenghua, Lin, Fernandez Ibanez, Maria del Pilar, Keyvanfar, Keyvan, Selleri, Carmine, Young, Neal S.
Published in Blood (02.12.2016)
Published in Blood (02.12.2016)
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Journal Article
Eltrombopag Improves Hematopoiesis in Patients with Low to Intermediate-2 Risk Myelodysplastic Syndrome (MDS)
Vicente, Alana, Gutierrez-Rodrigues, Fernanda, Giudice, Valentina, Wu, Zhijie, Kajigaya, Sachiko, Fernandez Ibanez, Maria del Pilar, Albitar, Maher, Weinstein, Barbara, Calvo, Katherine R., Townsley, Danielle M., Scheinberg, Phillip, Dunbar, Cynthia E., Young, Neal S., Winkler, Thomas
Published in Blood (29.11.2018)
Published in Blood (29.11.2018)
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Journal Article
Eltrombopag for Moderate Aplastic Anemia and Unilineage Cytopenias: Dosing, Long-Term Follow-up, Clonal Evolution and Somatic Mutation Profiling
Fan, Xing, Winkler, Thomas, Desmond, Ronan, Dumitriu, Bogdan, Townsley, Danielle M., Fernandez Ibanez, Maria del Pilar, Gutierrez-Rodrigues, Fernanda, Grasmeder, Sophia, Barranta, Ma Evette, Madey, Diane, Lotter, Jennifer, Valdez, Janet, Calvo, Katherine R., Wu, Colin, Young, Neal S., Dunbar, Cynthia E.
Published in Blood (29.11.2018)
Published in Blood (29.11.2018)
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Journal Article
Somatic TERT promoter Mutations in a Broad Spectrum of Telomeropathies
Gutierrez-Rodrigues, Fernanda, Donaires, Flávia S, Pinto, André, Vicente, Alana, Dillon, Laura, Clé, Diego V, Santana, Bárbara, Fernandez Ibanez, Maria del Pilar, Townsley, Danielle M., Kajigaya, Sachiko, Hourigan, Christopher S., Cooper, James N., Calado, Rodrigo T., Young, Neal S.
Published in Blood (29.11.2018)
Published in Blood (29.11.2018)
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Journal Article
T Cell Transcriptomes from Paroxysmal Nocturnal Hemoglobinuria Patients Reveal Novel Signaling Pathways
Hosokawa, Kohei, Kajigaya, Sachiko, Keyvanfar, Keyvan, Wangmin, Qiao, Xie, Yanling, Rios, Olga, Weinstein, Barbara, Fernandez Ibanez, Maria del Pilar, Townsley, Danielle M., Feng, Xingmin, Young, Neal S.
Published in Blood (02.12.2016)
Published in Blood (02.12.2016)
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Journal Article
A Plasma microRNA Signature As a Biomarker for Acquired Aplastic Anemia
Hosokawa, Kohei, Kajigaya, Sachiko, Feng, Xingmin, Desierto, Marie J., Fernandez Ibanez, Maria del Pilar, Rios, Olga, Weinstein, Barbara, Scheinberg, Phillip, Townsley, Danielle M., Young, Neal S.
Published in Blood (02.12.2016)
Published in Blood (02.12.2016)
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Journal Article
Towards Improved Decision-Making Based on Genomics in Bone Marrow Failure
Gutierrez-Rodrigues, Fernanda, Diamond, Carrie, Shalhoub, Ruba, Pinto, André, Donaires, Flávia S, Clé, Diego V, Darrigo, Luiz Guilherme, Catto, Luiz Fernando, Fan, Xing, Fernandez Ibanez, Maria del Pilar, Kajigaya, Sachiko, Dunbar, Cynthia E., Bonfim, Carmem M.S., Townsley, Danielle M., Calado, Rodrigo T., Young, Neal S.
Published in Blood (29.11.2018)
Published in Blood (29.11.2018)
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Journal Article
Myeloid Neoplasm Gene Somatic Mutations in Patients with Severe Aplastic Anemia Treated with Eltrombopag and Standard Immunosuppression
Townsley, Danielle M., Cooper, James N., Winkler, Thomas, Scheinberg, Phillip, Rios, Olga, Weinstein, Barbara, Valdez, Janet, Lotter, Jennifer, Desierto, Marie J., Fernandez Ibanez, Maria del Pilar, Wu, Colin, Dunbar, Cynthia E., Ma, Wanlong, Albitar, Maher, Young, Neal S.
Published in Blood (02.12.2016)
Published in Blood (02.12.2016)
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Journal Article
Heterozygous RTEL1 variants in Patients with Bone Marrow Failure Associate with Telomere Dysfunction in the Absence of Telomere Shortening
Gutierrez-Rodrigues, Fernanda, Kajigaya, Sachiko, Feng, Xingmin, Fernandez Ibanez, Maria del Pilar, Desierto, Marie J., Keyvanfar, Keyvan, Li, Zejuan, Das, Soma, Calado, Rodrigo T., Townsley, Danielle M., Young, Neal S.
Published in Blood (02.12.2016)
Published in Blood (02.12.2016)
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Journal Article