Thrombotic Microangiopathy Following Onasemnogene Abeparvovec for Spinal Muscular Atrophy: A Case Series
Chand, Deepa H., Zaidman, Craig, Arya, Kapil, Millner, Rachel, Farrar, Michelle A., Mackie, Fiona E., Goedeker, Natalie L., Dharnidharka, Vikas R., Dandamudi, Raja, Reyna, Sandra P.
Published in The Journal of pediatrics (01.04.2021)
Published in The Journal of pediatrics (01.04.2021)
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Journal Article
Emerging therapies and challenges in spinal muscular atrophy
Farrar, Michelle A., Park, Susanna B., Vucic, Steve, Carey, Kate A., Turner, Bradley J., Gillingwater, Thomas H., Swoboda, Kathryn J., Kiernan, Matthew C.
Published in Annals of neurology (01.03.2017)
Published in Annals of neurology (01.03.2017)
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Journal Article
Rationale for targeting complement in COVID‐19
Polycarpou, Anastasia, Howard, Mark, Farrar, Conrad A, Greenlaw, Roseanna, Fanelli, Giorgia, Wallis, Russell, Klavinskis, Linda S, Sacks, Steven
Published in EMBO molecular medicine (07.08.2020)
Published in EMBO molecular medicine (07.08.2020)
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Journal Article
Collectin-11 detects stress-induced L-fucose pattern to trigger renal epithelial injury
Farrar, Conrad A, Tran, David, Li, Ke, Wu, Weiju, Peng, Qi, Schwaeble, Wilhelm, Zhou, Wuding, Sacks, Steven H
Published in The Journal of clinical investigation (01.05.2016)
Published in The Journal of clinical investigation (01.05.2016)
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Journal Article
Single-cell analysis identifies dynamic gene expression networks that govern B cell development and transformation
Lee, Robin D, Munro, Sarah A, Knutson, Todd P, LaRue, Rebecca S, Heltemes-Harris, Lynn M, Farrar, Michael A
Published in Nature communications (25.11.2021)
Published in Nature communications (25.11.2021)
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Journal Article
Complement activation is a crucial driver of acute kidney injury in rhabdomyolysis
Boudhabhay, Idris, Poillerat, Victoria, Grunenwald, Anne, Torset, Carine, Leon, Juliette, Daugan, Marie V., Lucibello, Francesca, El Karoui, Khalil, Ydee, Amandine, Chauvet, Sophie, Girardie, Patrick, Sacks, Steven, Farrar, Conrad A., Garred, Peter, Berthaud, Romain, Le Quintrec, Moglie, Rabant, Marion, de Lonlay, Pascale, Rambaud, Caroline, Gnemmi, Viviane, Fremeaux-Bacchi, Veronique, Frimat, Marie, Roumenina, Lubka T.
Published in Kidney international (01.03.2021)
Published in Kidney international (01.03.2021)
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Journal Article
Respiratory and sleep outcomes in children with SMA treated with nusinersen - real world experience
Gonski, K, Chuang, S, Teng, A, Thambipillay, G, Farrar, MA, Menezes, MP, Fitzgerald, DA
Published in Neuromuscular disorders : NMD (01.06.2023)
Published in Neuromuscular disorders : NMD (01.06.2023)
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Journal Article
Cytotoxic CD4 T cells in the mucosa and in cancer
Venkatesh, Hrishi, Tracy, Sean I, Farrar, Michael A
Published in Frontiers in immunology (16.08.2023)
Published in Frontiers in immunology (16.08.2023)
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Journal Article
B-1a cells acquire their unique characteristics by bypassing the pre-BCR selection stage
Wong, Jason B, Hewitt, Susannah L, Heltemes-Harris, Lynn M, Mandal, Malay, Johnson, Kristen, Rajewsky, Klaus, Koralov, Sergei B, Clark, Marcus R, Farrar, Michael A, Skok, Jane A
Published in Nature communications (18.10.2019)
Published in Nature communications (18.10.2019)
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Journal Article
Integrating Ethics and Equity with Economics and Effectiveness for newborn screening in the genomic age: A qualitative study protocol of stakeholder perspectives
Kariyawasam, Didu S, Scarfe, Joanne, Meagher, Christian, Farrar, Michelle A, Bhattacharya, Kaustav, Carter, Stacy M, Newson, Ainsley J, Otlowski, Margaret, Watson, Jo, Millis, Nicole, Norris, Sarah
Published in PloS one (25.03.2024)
Published in PloS one (25.03.2024)
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Journal Article
Unexpected survival after deliberate phosphine gas poisoning: An Australian experience of extracorporeal membrane oxygenation rescue in this setting
A Farrar, Ross, B Justus, Angelo, A Masurkar, Vikram, M Garrett, Peter
Published in Anaesthesia and intensive care (01.05.2022)
Published in Anaesthesia and intensive care (01.05.2022)
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Journal Article
Clinical Characteristics and Functional Motor Outcomes of Enterovirus 71 Neurological Disease in Children
Teoh, Hooi-Ling, Mohammad, Shekeeb S, Britton, Philip N, Kandula, Tejaswi, Lorentzos, Michelle S, Booy, Robert, Jones, Cheryl A, Rawlinson, William, Ramachandran, Vidiya, Rodriguez, Michael L, Andrews, P Ian, Dale, Russell C, Farrar, Michelle A, Sampaio, Hugo
Published in JAMA neurology (01.03.2016)
Published in JAMA neurology (01.03.2016)
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Journal Article
Collectin-11 Promotes the Development of Renal Tubulointerstitial Fibrosis
Wu, Weiju, Liu, Chengfei, Farrar, Conrad A, Ma, Liang, Dong, Xia, Sacks, Steven H, Li, Ke, Zhou, Wuding
Published in Journal of the American Society of Nephrology (01.01.2018)
Published in Journal of the American Society of Nephrology (01.01.2018)
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Journal Article
Health, wellbeing and lived experiences of adults with SMA: a scoping systematic review
Wan, Hamish W Y, Carey, Kate A, D'Silva, Arlene, Vucic, Steve, Kiernan, Matthew C, Kasparian, Nadine A, Farrar, Michelle A
Published in Orphanet journal of rare diseases (12.03.2020)
Published in Orphanet journal of rare diseases (12.03.2020)
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Journal Article