Production and purification of serotype 1, 2, and 5 recombinant adeno-associated viral vectors
Zolotukhin, Sergei, Potter, Mark, Zolotukhin, Irene, Sakai, Yoshihisa, Loiler, Scott, Fraites, Thomas J, Chiodo, Vince A, Phillipsberg, Tina, Muzyczka, Nicholas, Hauswirth, William W, Flotte, Terance R, Byrne, Barry J, Snyder, Richard O
Published in Methods (San Diego, Calif.) (01.10.2002)
Published in Methods (San Diego, Calif.) (01.10.2002)
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Journal Article
Gel-mediated Delivery of AAV1 Vectors Corrects Ventilatory Function in Pompe Mice With Established Disease
Mah, Cathryn S, Falk, Darin J, Germain, Sean A, Kelley, Jeffry S, Lewis, Melissa A, Cloutier, Denise A, DeRuisseau, Lara R, Conlon, Thomas J, Cresawn, Kerry O, Fraites Jr, Thomas J, Campbell-Thompson, Martha, Fuller, David D, Byrne, Barry J
Published in Molecular therapy (01.03.2010)
Published in Molecular therapy (01.03.2010)
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Journal Article
Improved Method of Recombinant AAV2 Delivery for Systemic Targeted Gene Therapy
Mah, Cathryn, Fraites, Thomas J., Zolotukhin, Irene, Song, Sihong, Flotte, Terence R., Dobson, Jon, Batich, Christopher, Byrne, Barry J.
Published in Molecular therapy (01.07.2002)
Published in Molecular therapy (01.07.2002)
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Journal Article
Correction of the Enzymatic and Functional Deficits in a Model of Pompe Disease Using Adeno-associated Virus Vectors
Fraites, Thomas J., Schleissing, Mary R., Shanely, R.Andrew, Walter, Glenn A., Cloutier, Denise A., Zolotukhin, Irene, Pauly, Daniel F., Raben, Nina, Plotz, Paul H., Powers, Scott K., Kessler, Paul D., Byrne, Barry J.
Published in Molecular therapy (01.05.2002)
Published in Molecular therapy (01.05.2002)
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Journal Article
Rescue of enzyme deficiency in embryonic diaphragm in a mouse model of metabolic myopathy: Pompe disease
Rucker, Mary, Fraites, Jr, Thomas J, Porvasnik, Stacy L, Lewis, Melissa A, Zolotukhin, Irene, Cloutier, Denise A, Byrne, Barry J
Published in Development (Cambridge) (01.06.2004)
Published in Development (Cambridge) (01.06.2004)
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Journal Article
A New Method for Recombinant Adeno-associated Virus Vector Delivery to Murine Diaphragm
Mah, Cathryn, Fraites, Thomas J, Cresawn, Kerry O, Zolotukhin, Irene, Lewis, Melissa A, Byrne, Barry J
Published in Molecular therapy (01.03.2004)
Published in Molecular therapy (01.03.2004)
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Journal Article
Impact of humoral immune response on distribution and efficacy of recombinant adeno-associated virus-derived acid alpha-glucosidase in a model of glycogen storage disease type II
Cresawn, Kerry O, Fraites, Thomas J, Wasserfall, Clive, Atkinson, Mark, Lewis, Melissa, Porvasnik, Stacy, Liu, Chen, Mah, Cathryn, Byrne, Barry J
Published in Human gene therapy (01.01.2005)
Published in Human gene therapy (01.01.2005)
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Journal Article
Intercellular transfer of the virally derived precursor form of acid alpha-glucosidase corrects the enzyme deficiency in inherited cardioskeletal myopathy Pompe disease
Pauly, D F, Fraites, T J, Toma, C, Bayes, H S, Huie, M L, Hirschhorn, R, Plotz, P H, Raben, N, Kessler, P D, Byrne, B J
Published in Human gene therapy (20.03.2001)
Published in Human gene therapy (20.03.2001)
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Journal Article
TRANSFER DEVICE FOR USE WITH INFUSION LIQUID CONTAINER
Mosler, Theodore J, Batchelor, Stanton D, Korogi, Todd M, McCall, JR., Charles E, Zignego, Jay C, Fraites, Jr., Thomas J, Wang, Gonghao, Guala, Gianni
Year of Publication 05.05.2022
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Year of Publication 05.05.2022
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