Risdiplam treatment has not led to retinal toxicity in patients with spinal muscular atrophy
Sergott, Robert C., Amorelli, Giulia M., Baranello, Giovanni, Barreau, Emmanuel, Beres, Shannon, Kane, Steven, Mercuri, Eugenio, Orazi, Lorenzo, SantaMaria, Melissa, Tremolada, Gemma, Santarsiero, Diletta, Waskowska, Agnieszka, Yashiro, Shigeko, Denk, Nora, Fürst‐Recktenwald, Sabine, Gerber, Marianne, Gorni, Ksenija, Jaber, Birgit, Jacobsen, Bjoern, Mueller, Lutz, Nave, Stephane, Scalco, Renata S., Marzoli, Stefania B.
Published in Annals of clinical and translational neurology (01.01.2021)
Published in Annals of clinical and translational neurology (01.01.2021)
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Journal Article
Integrated analysis of long‐term growth and bone development in pediatric and adolescent patients receiving bevacizumab
Müller, Hermann L., Merks, Johannes H.M., Geoerger, Birgit, Grill, Jacques, Hargrave, Darren, Glade Bender, Julia, Gururangan, Sridharan, Navid, Fariba, Johnston, Michael, Bachir, Jeanette, Elze, Markus C., Fürst‐Recktenwald, Sabine
Published in Pediatric blood & cancer (01.02.2019)
Published in Pediatric blood & cancer (01.02.2019)
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Journal Article
Inhibition of 11β-HSD1 with RO5093151 for non-alcoholic fatty liver disease: a multicentre, randomised, double-blind, placebo-controlled trial
Stefan, Norbert, Prof, Ramsauer, Markus, PhD, Jordan, Paul, PhD, Nowotny, Bettina, MD, Kantartzis, Konstantinos, MD, Machann, Jürgen, PhD, Hwang, Jong-Hee, PhD, Nowotny, Peter, PhD, Kahl, Sabine, MD, Harreiter, Jürgen, MD, Hornemann, Silke, MD, Sanyal, Arun J, Prof, Stewart, Paul M, Prof, Pfeiffer, Andreas F, Prof, Kautzky-Willer, Alexandra, Prof, Roden, Michael, Prof, Häring, Hans-Ulrich, Prof, Fürst-Recktenwald, Sabine, MD
Published in The lancet. Diabetes & endocrinology (01.05.2014)
Published in The lancet. Diabetes & endocrinology (01.05.2014)
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Open-label, multicentre, randomised, phase II study of the EpSSG and the ITCC evaluating the addition of bevacizumab to chemotherapy in childhood and adolescent patients with metastatic soft tissue sarcoma (the BERNIE study)
Chisholm, Julia C., Merks, Johannes H.M., Casanova, Michela, Bisogno, Gianni, Orbach, Daniel, Gentet, Jean-Claude, Thomassin-Defachelles, Anne-Sophie, Chastagner, Pascal, Lowis, Stephen, Ronghe, Milind, McHugh, Kieran, van Rijn, Rick R., Hilton, Magalie, Bachir, Jeanette, Fürst-Recktenwald, Sabine, Geoerger, Birgit, Oberlin, Odile
Published in European journal of cancer (1990) (01.09.2017)
Published in European journal of cancer (1990) (01.09.2017)
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Journal Article
The Impact of Radiation Therapy in Children and Adolescents With Metastatic Rhabdomyosarcoma
Cameron, Alison L., Elze, Markus C., Casanova, Michela, Geoerger, Birgit, Gaze, Mark N., Minard-Colin, Veronique, McHugh, Kieran, van Rijn, Rick R., Kelsey, Anna, Martelli, Hélène, Mandeville, Henry, Bisogno, Gianni, Lowis, Stephen, Ronghe, Milind, Orbach, Daniel, Guizani, Cecile, Fürst-Recktenwald, Sabine, Chisholm, Julia C., Merks, Johannes H.M.
Published in International journal of radiation oncology, biology, physics (15.11.2021)
Published in International journal of radiation oncology, biology, physics (15.11.2021)
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Journal Article
Phase I Trial of Anti-Vascular Endothelial Growth Factor/Anti-angiopoietin 2 Bispecific Antibody RG7716 for Neovascular Age-Related Macular Degeneration
Chakravarthy, Usha, Bailey, Clare, Brown, David, Campochiaro, Peter, Chittum, Mark, Csaky, Karl, Tufail, Adnan, Yates, Paul, Cech, Patrick, Giraudon, Mylene, Delmar, Paul, Szczesny, Piotr, Sahni, Jayashree, Boulay, Anne, Nagel, Sandra, Fürst-Recktenwald, Sabine, Schwab, Dietmar
Published in Ophthalmology retina (01.11.2017)
Published in Ophthalmology retina (01.11.2017)
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Journal Article
Better Medicines for Children: Lessons Learnt and Share Learnings at the EFGCP Annual Paediatric Conferences
Corriol-Rohou, Solange, Fürst-Recktenwald, Sabine Ingeborg, Davies, Elin-Haf, Dehlinger-Kremer, Martine, Turner, Mark A
Published in Therapeutic innovation & regulatory science (13.11.2024)
Published in Therapeutic innovation & regulatory science (13.11.2024)
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Journal Article
Abstract B029: Studies in human bone cell co-cultures reveal a potential mechanism underlying bone fractures in children treated with entrectinib and suggest a positive association with vitamin D
Ehnert, Sabrina, Schulz, Kevin A., Cardenas, Alison K., Meneses-Lorente, Georgina, Roth, Adrian, Fürst-Recktenwald, Sabine
Published in Cancer research (Chicago, Ill.) (05.09.2024)
Published in Cancer research (Chicago, Ill.) (05.09.2024)
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Journal Article
Analysis and reporting of pediatric growth and development assessment from clinical trials: overview and challenges
Choi, YounJeong, Barbier, Nathalie, Fürst-Recktenwald, Sabine, Ye, Jingjing, Wajsbrot, Dalia Ballas, Ishida, Eiji, Gamalo, Margaret
Published in Journal of biopharmaceutical statistics (02.11.2023)
Published in Journal of biopharmaceutical statistics (02.11.2023)
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Journal Article
Development of a neonatal adverse event severity scale through a Delphi consensus approach
Salaets, Thomas, Turner, Mark A, Short, Mary, Ward, Robert M, Ariagno, Ronald L, Wade, Kelly, Thomson, Merran, Roberts, Eve, Harrison, Judy, Baer, Gerri, Allegaert, Karel, Allen, Marilee, Allen, Albert, Freimane, Dina Apele, Aschner, Judy, Ballard, Roberta, Belew, Yodit, Bellflower, Bobby, Bhatt-Mehta, Varsha, Blum, Mike, Bonardi, Chiara, Bondurant, Patti, Boylan, Geraldine, Buracchio, Teresa, Burnett, Amber, Burnham, Janelle, Chen, Alice, Clay, Bob, Connolly, Eamonn, Darsey, Edress, Lisa, Roberto De, Degl, Jennifer, Dempsey, Eugene, Diacovo, Tom, Dionne, Janis, Duchon, Jennifer, Eklund, Wakako, Fabbri, Laura, Fielder, Alistair, Freilich, Emily, Fürst-Recktenwald, Sabine, Graham, Tamorah, Green, Dionna, Grogan, Cristal, Heiselman, Darell, Hellström, Ann, Herold, Ralf, Hibbs, Anna Maria, Hirschfeld, Steven, Brown, Mary Hise, Holberton, Jim, Iveli, Pablo, Jobe, Alan, Kayton, Allyson, Kenner, Carole, Kraft, Walter, Kusuda, Satoshi, Lewis, Tamorah, Lui, Kei, Lutsar, Irja, Mangili, Alexandra, McCune, Susan, McDonald, Karen, McPherson, Christopher, Miller, Washington UniversityThomas, Ming, Jeffrey, Modi, Neena, Morrison, Maya, Mulugeta, Lily, Nakamura, Hide, Noel, Gary, Olshansky, Miki, Oschman, Alex, Padula, Mike, Peiris, Vasum, Koplowitz, Luana Pesco, Pham, Josh, Pilon, Aprile, Portman, Ron, Pressler, Ronit, Rabe, Heike, Raju, Tonse, Savani, Rashmin, Segal, Robert, Senterre, Thibault, Shah, Prakesh, Sheridan, Philip, Sherwin, Catherine, Singh, Rajendra, Soul, Janet, Spence, Kaye, Storari, Linda, Taminiau, Jan, Anker, John Van Den, Venkataraman, Preeti, Walker, Karen, Wilson, Janice, Zajicek, Anne, Zaloga, Gary, Zeldis, Stav
Published in Archives of disease in childhood (01.12.2019)
Published in Archives of disease in childhood (01.12.2019)
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Journal Article
Integration of pharmacogenetics and pharmacogenomics in drug development: implications for regulatory and medical decision making in pediatric diseases
Piana, Chiara, Surh, Linda, Furst-Recktenwald, Sabine, Iolascon, Achille, Jacqz-Aigrain, Evelyne M, Jonker, Ineke, Russo, Roberta, van Schaik, Ron H N, Wessels, Judith, Della Pasqua, Oscar E
Published in Journal of clinical pharmacology (01.05.2012)
Published in Journal of clinical pharmacology (01.05.2012)
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Journal Article
Role of radiotherapy to primary/metastatic sites in pediatric patients with metastatic rhabdomyosarcoma in the BERNIE study
Cameron, Alison, Chisholm, Julia, Elze, Markus C., Casanova, Michela, Geoerger, Birgit, Gaze, Mark, Oberlin, Odile, Bachir, Jeanette, Fürst-Recktenwald, Sabine, Merks, Johannes H.M.
Published in Journal of clinical oncology (20.05.2017)
Published in Journal of clinical oncology (20.05.2017)
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Journal Article
Long-term growth and development in 268 bevacizumab (BEV)-treated and 135 control pediatric/adolescent patients (pts): An integrated analysis
Müller, Hermann L., Merks, Johannes H.M., Geoerger, Birgit, Grill, Jacques, Hargrave, Darren, Glade Bender, Julia Lynne, Gururangan, Sridharan, Navid, Fariba, Johnston, Michael, Bachir, Jeanette, Hilton, Magalie, Fürst-Recktenwald, Sabine
Published in Journal of clinical oncology (20.05.2017)
Published in Journal of clinical oncology (20.05.2017)
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Journal Article
BERNIE: Open-label, randomized, phase II study of bevacizumab plus chemotherapy in pediatric metastatic rhabdomyosarcoma (RMS) and non-rhabdomyosarcoma soft tissue sarcoma (NRSTS)
Chisholm, Julia C., Merks, Johannes H., Casanova, Michela, Bisogno, Gianni, Orbach, Daniel, Gentet, Jean-Claude, Thomassin Defachelles, Anne-Sophie, Chastagner, Pascal B., Lowis, Steve, Ronghe, Milind, McHugh, Kieran, van Rijn, Rick R., Hilton, Magalie, Bachir, Jeanette, Fürst-Recktenwald, Sabine, Geoerger, Birgit, Oberlin, Odile
Published in Journal of clinical oncology (20.05.2016)
Published in Journal of clinical oncology (20.05.2016)
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Journal Article
Is there sufficient evidence to consider the use of 11[beta]-hydroxysteroid dehydrogenase type 1 inhibition in children?
Furst-Recktenwald, Sabine, Dorr, Helmuth G, Quinkler, Marcus, Dotsch, Jörg, Stewart, Paul M
Published in Clinical endocrinology (Oxford) (01.08.2012)
Published in Clinical endocrinology (Oxford) (01.08.2012)
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