Effectiveness of lumacaftor/ivacaftor initiation in children with cystic fibrosis aged 2 through 5 years on disease progression: Interim results from an ongoing registry-based study
Kim, Claire, Higgins, Mark, Liu, Lingyun, Volkova, Nataliya, Zolin, Anna, Naehrlich, Lutz, Andreas, Pfleger (AT), Elise, Lammertijn (BE), Duška, Tješić-Drinković (HR), Pavel, Dřevínek (CZ), Milan, Macek, Hanne, Vebert Olesen (DK), Nathalie, Senecal (FR), Pierre-Régis, Burgel (FR), Godfrey, Fletcher (IE), Rita, Padoan (IT), Annalisa, Orenti (IT), Federico, Ambrogi (IT), Simone, Gambazza (IT), Elīna, Aleksejeva (LV), Anna-Maria, Charatsi (LU), Domenique, Zomer (NL), Egil, Bakkeheim (NO), Lukasz, Woźniacki (PL), Uroš, Krivec (SI), Christina, Krantz (SE), Anders, Lindblad (SE), Andreas, Jung (CH), Sarah, Clarke (UK), Siobhán B․, Carr (UK)
Published in Journal of cystic fibrosis (01.05.2024)
Published in Journal of cystic fibrosis (01.05.2024)
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