Base Editor Correction of COL7A1 in Recessive Dystrophic Epidermolysis Bullosa Patient-Derived Fibroblasts and iPSCs
Osborn, Mark J., Newby, Gregory A., McElroy, Amber N., Knipping, Friederike, Nielsen, Sarah C., Riddle, Megan J., Xia, Lily, Chen, Weili, Eide, Cindy R., Webber, Beau R., Wandall, Hans H., Dabelsteen, Sally, Blazar, Bruce R., Liu, David R., Tolar, Jakub
Published in Journal of investigative dermatology (01.02.2020)
Published in Journal of investigative dermatology (01.02.2020)
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A multitask clustering approach for single-cell RNA-seq analysis in Recessive Dystrophic Epidermolysis Bullosa
Zhang, Huanan, Lee, Catherine A A, Li, Zhuliu, Garbe, John R, Eide, Cindy R, Petegrosso, Raphael, Kuang, Rui, Tolar, Jakub
Published in PLoS computational biology (01.04.2018)
Published in PLoS computational biology (01.04.2018)
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Rapid Induction of Cerebral Organoids From Human Induced Pluripotent Stem Cells Using a Chemically Defined Hydrogel and Defined Cell Culture Medium
Lindborg, Beth A., Brekke, John H., Vegoe, Amanda L., Ulrich, Connor B., Haider, Kerri T., Subramaniam, Sandhya, Venhuizen, Scott L., Eide, Cindy R., Orchard, Paul J., Chen, Weili, Wang, Qi, Pelaez, Francisco, Scott, Carolyn M., Kokkoli, Efrosini, Keirstead, Susan A., Dutton, James R., Tolar, Jakub, O'Brien, Timothy D.
Published in Stem cells translational medicine (01.07.2016)
Published in Stem cells translational medicine (01.07.2016)
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Rapid generation of Col7a1−/− mouse model of recessive dystrophic epidermolysis bullosa and partial rescue via immunosuppressive dermal mesenchymal stem cells
Webber, Beau R, O'Connor, Kyle T, McElmurry, Ron T, Durgin, Elise N, Eide, Cindy R, Lees, Christopher J, Riddle, Megan J, Mathews, Wendy E, Frank, Natasha Y, Kluth, Mark A, Ganss, Christoph, Moriarity, Branden S, Frank, Markus H, Osborn, Mark J, Tolar, Jakub
Published in Laboratory investigation (01.10.2017)
Published in Laboratory investigation (01.10.2017)
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CRISPR/Cas9-Based Cellular Engineering for Targeted Gene Overexpression
Osborn, Mark J, Lees, Christopher J, McElroy, Amber N, Merkel, Sarah C, Eide, Cindy R, Mathews, Wendy, Feser, Colby J, Tschann, Madison, McElmury, Ron T, Webber, Beau R, Kim, Chong Jai, Blazar, Bruce R, Tolar, Jakub
Published in International journal of molecular sciences (22.03.2018)
Published in International journal of molecular sciences (22.03.2018)
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Somatic Mosaicism in Fanconi Anemia: Evidence of Genotypic Reversion in Lymphohematopoietic Stem Cells
Gregory, John J., Wagner, John E., Verlander, Peter C., Levran, Orna, Batish, Sat Dev, Eide, Cindy R., Steffenhagen, Amy, Hirsch, Betsy, Auerbach, Arleen D.
Published in Proceedings of the National Academy of Sciences - PNAS (27.02.2001)
Published in Proceedings of the National Academy of Sciences - PNAS (27.02.2001)
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CXCR4 expression in CD34+ cells and unit predominance after double umbilical cord blood transplantation
Ramirez, P, Wagner, J E, DeFor, T E, Eide, C R, Miller, J S, Weisdorf, D J, Brunstein, C G
Published in Leukemia (01.05.2013)
Published in Leukemia (01.05.2013)
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Integrating Porous Silicon Nanoneedles within Medical Devices for Nucleic Acid Nanoinjection
Wang, Cong, Gu, Chenlei, Popp, Courtney, Vashisth, Priya, Mustfa, Salman Ahmad, Martella, Davide Alessandro, Spiteri, Chantelle, McLennan, Samuel, Sun, Ningjia, Riddle, Megan, Eide, Cindy R., Parsons, Maddy, Tolar, Jakub, McGrath, John A., Chiappini, Ciro
Published in ACS nano (10.05.2024)
Published in ACS nano (10.05.2024)
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Decreasing time to baccalaureate degree in the United States
Denning, Jeffrey T., Eide, Eric R., Mumford, Kevin J., Sabey, Daniel J.
Published in Economics of education review (01.10.2022)
Published in Economics of education review (01.10.2022)
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Disruption of HIV-1 co-receptors CCR5 and CXCR4 in primary human T cells and hematopoietic stem and progenitor cells using base editing
Knipping, Friederike, Newby, Gregory A., Eide, Cindy R., McElroy, Amber N., Nielsen, Sarah C., Smith, Kyle, Fang, Yongxing, Cornu, Tatjana I., Costa, Caroline, Gutierrez-Guerrero, Alejandra, Bingea, Samuel P., Feser, Colby J., Steinbeck, Benjamin, Hippen, Keli L., Blazar, Bruce R., McCaffrey, Anton, Mussolino, Claudio, Verhoeyen, Els, Tolar, Jakub, Liu, David R., Osborn, Mark J.
Published in Molecular therapy (05.01.2022)
Published in Molecular therapy (05.01.2022)
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Journal Article
Twin Prime Editing Mediated Exon Skipping/Reinsertion for Restored Collagen VII Expression in Recessive Dystrophic Epidermolysis Bullosa
Steinbeck, Benjamin J., Gao, Xin D., McElroy, Amber N., Pandey, Smriti, Doman, Jordan L., Riddle, Megan J., Xia, Lily, Chen, Weili, Eide, Cindy R., Lengert, Andre H., Han, Sang Won, Blazar, Bruce R., Wandall, Hans H., Dabelsteen, Sally, Liu, David R., Tolar, Jakub, Osborn, Mark J.
Published in Journal of investigative dermatology (17.05.2024)
Published in Journal of investigative dermatology (17.05.2024)
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Alloengraftment without significant toxicity or GVHD in CD45 antibody-drug conjugate–conditioned Fanconi anemia mice
Saha, Asim, Palchaudhuri, Rahul, Lanieri, Leanne, Hyzy, Sharon, Riddle, Megan J., Panthera, Jamie, Eide, Cindy R., Tolar, Jakub, Panoskaltsis-Mortari, Angela, Gorfinkel, Lev, Tkachev, Victor, Gerdemann, Ulrike, Alvarez-Calderon, Francesca, Palato, Elisa Rojas, MacMillan, Margaret L., Wagner, John E., Kean, Leslie S., Osborn, Mark J., Kiem, Hans-Peter, Scadden, David T., Olson, Lisa M., Blazar, Bruce R.
Published in Blood (23.05.2024)
Published in Blood (23.05.2024)
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Induced Pluripotent Stem Cells from Individuals with Recessive Dystrophic Epidermolysis Bullosa
Tolar, Jakub, Xia, Lily, Riddle, Megan J., Lees, Chris J., Eide, Cindy R., McElmurry, Ron T., Titeux, Matthias, Osborn, Mark J., Lund, Troy C., Hovnanian, Alain, Wagner, John E., Blazar, Bruce R.
Published in Journal of investigative dermatology (01.04.2011)
Published in Journal of investigative dermatology (01.04.2011)
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