In-Frame Deletion of Dystrophin Exons 8-50 Results in DMD Phenotype
Egorova, Tatiana V, Galkin, Ivan I, Velyaev, Oleg A, Vassilieva, Svetlana G, Savchenko, Irina M, Loginov, Vyacheslav A, Dzhenkova, Marina A, Korshunova, Diana S, Kozlova, Olga S, Ivankov, Dmitry N, Polikarpova, Anna V
Published in International journal of molecular sciences (23.05.2023)
Published in International journal of molecular sciences (23.05.2023)
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CRISPR-Cas9 correction in the DMD mouse model is accompanied by upregulation of Dp71f protein
Egorova, Tatiana V., Polikarpova, Anna V., Vassilieva, Svetlana G., Dzhenkova, Marina A., Savchenko, Irina M., Velyaev, Oleg A., Shmidt, Anna A., Soldatov, Vladislav O., Pokrovskii, Mikhail V., Deykin, Alexey V., Bardina, Maryana V.
Published in Molecular therapy. Methods & clinical development (14.09.2023)
Published in Molecular therapy. Methods & clinical development (14.09.2023)
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RNA Interference Effectors Selectively Silence the Pathogenic Variant GNAO1 c.607 G > A In Vitro
Klementieva, Natalia V, Lunev, Evgenii A, Shmidt, Anna A, Loseva, Elizaveta M, Savchenko, Irina M, Svetlova, Ekaterina A, Galkin, Ivan I, Polikarpova, Anna V, Usachev, Evgeny V, Vassilieva, Svetlana G, Marina, Valeria I, Dzhenkova, Marina A, Romanova, Anna D, Agutin, Anton V, Timakova, Anna A, Reshetov, Denis A, Egorova, Tatiana V, Bardina, Maryana V
Published in Nucleic acid therapeutics (01.04.2024)
Published in Nucleic acid therapeutics (01.04.2024)
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