Cross‐sectional analysis of the Myasthenia Gravis Patient Registry: Disability and treatment
Cutter, Gary, Xin, Haichang, Aban, Inmaculada, Burns, Ted M., Allman, Phillip H., Farzaneh‐Far, Ramin, Duda, Petra W., Kaminski, Henry J.
Published in Muscle & nerve (01.12.2019)
Published in Muscle & nerve (01.12.2019)
Get full text
Journal Article
Zilucoplan: An Investigational Complement C5 Inhibitor for the Treatment of Acetylcholine Receptor Autoantibody-Positive Generalized Myasthenia Gravis
Howard, James F., Vissing, John, Gilhus, Nils E., Leite, M. Isabel, Utsugisawa, Kimiaki, Duda, Petra W., Farzaneh-Far, Ramin, Murai, Hiroyuki, Wiendl, Heinz
Published in Expert opinion on investigational drugs (04.05.2021)
Published in Expert opinion on investigational drugs (04.05.2021)
Get full text
Journal Article
Long-term safety and effectiveness of natalizumab redosing and treatment in the STRATA MS Study
O'Connor, Paul, Goodman, Andrew, Kappos, Ludwig, Lublin, Fred, Polman, Chris, Rudick, Richard A, Hauswirth, Kathy, Cristiano, Lynda M, Forrestal, Fiona, Duda, Petra
Published in Neurology (01.07.2014)
Published in Neurology (01.07.2014)
Get more information
Journal Article
Correlation of Quantitative Myasthenia Gravis and Myasthenia Gravis Activities of Daily Living scales in the MGTX study
McPherson, Tarrant, Aban, Inmaculada, Duda, Petra W., Farzaneh‐Far, Ramin, Wolfe, Gil I., Kaminski, Henry J., Cutter, Gary, Lee, Ikjae
Published in Muscle & nerve (01.08.2020)
Published in Muscle & nerve (01.08.2020)
Get full text
Journal Article
Phase II trials of zilucoplan in paroxysmal nocturnal hemoglobinuria
Kulasekararaj, Austin G, Lehtinen, Anna-Elina, Forsyth, Cecily, Gandhi, Shreyans, Griffin, Morag, Körper, Sixten, Mikala, Gabor, Muus, Petra, Overgaard, Ulrik, Patriquin, Christopher J, Pullon, Humphrey, Shen, Yu-Min, Spearing, Ruth, Szer, Jeff, De la Borderie, Guillemette, Duda, Petra W, Farzaneh-Far, Ramin, Ragunathan, Sharan, Sayegh, Camil E, Vadysirisack, Douangsone D, Schrezenmeier, Hubert
Published in Haematologica (Roma) (01.03.2024)
Published in Haematologica (Roma) (01.03.2024)
Get full text
Journal Article
Zilucoplan, a macrocyclic peptide inhibitor of human complement component 5, uses a dual mode of action to prevent terminal complement pathway activation
Tang, Guo-Qing, Tang, Yalan, Dhamnaskar, Ketki, Hoarty, Michelle D., Vyasamneni, Rohit, Vadysirisack, Douangsone D., Ma, Zhong, Zhu, Nanqun, Wang, Jian-Guo, Bu, Charlie, Cong, Bestine, Palmer, Elizabeth, Duda, Petra W., Sayegh, Camil, Ricardo, Alonso
Published in Frontiers in immunology (09.08.2023)
Published in Frontiers in immunology (09.08.2023)
Get full text
Journal Article
Corrigendum: Zilucoplan, a macrocyclic peptide inhibitor of human complement component 5, uses a dual mode of action to prevent terminal complement pathway activation
Tang, Guo-Qing, Tang, Yalan, Dhamnaskar, Ketki, Hoarty, Michelle D., Vyasamneni, Rohit, Vadysirisack, Douangsone D., Ma, Zhong, Zhu, Nanqun, Wang, Jian-Guo, Bu, Charlie, Cong, Bestine, Palmer, Elizabeth, Duda, Petra W., Sayegh, Camil, Ricardo, Alonso
Published in Frontiers in immunology (25.09.2023)
Published in Frontiers in immunology (25.09.2023)
Get full text
Journal Article
Long-term safety and efficacy of zilucoplan in patients with generalized myasthenia gravis: interim analysis of the RAISE-XT open-label extension study
Howard, Jr, James F, Bresch, Saskia, Farmakidis, Constantine, Freimer, Miriam, Genge, Angela, Hewamadduma, Channa, Hinton, John, Hussain, Yessar, Juntas-Morales, Raul, Kaminski, Henry J, Maniaol, Angelina, Mantegazza, Renato, Masuda, Masayuki, Nowak, Richard J, Sivakumar, Kumaraswamy, Śmiłowski, Marek, Utsugisawa, Kimiaki, Vu, Tuan, Weiss, Michael D, Zajda, Małgorzata, Bloemers, Jos, Boroojerdi, Babak, Brock, Melissa, de la Borderie, Guillemette, Duda, Petra W, Vanderkelen, Mark, Leite, M Isabel
Published in Therapeutic advances in neurological disorders (01.01.2024)
Published in Therapeutic advances in neurological disorders (01.01.2024)
Get full text
Journal Article
Long-Term Pulmonary Function in Duchenne Muscular Dystrophy: Comparison of Eteplirsen-Treated Patients to Natural History
Kinane, T Bernard, Mayer, Oscar H, Duda, Petra W, Lowes, Linda P, Moody, Stephanie L, Mendell, Jerry R
Published in Journal of neuromuscular diseases (2018)
Published in Journal of neuromuscular diseases (2018)
Get more information
Journal Article
A study of mefloquine treatment for progressive multifocal leukoencephalopathy: results and exploration of predictors of PML outcomes
Clifford, David B., Nath, Avindra, Cinque, Paola, Brew, Bruce J., Zivadinov, Robert, Gorelik, Leonid, Zhao, Zhenming, Duda, Petra
Published in Journal of neurovirology (01.08.2013)
Published in Journal of neurovirology (01.08.2013)
Get full text
Journal Article
Human and Murine CD4 T Cell Reactivity to a Complex Antigen: Recognition of the Synthetic Random Polypeptide Glatiramer Acetate
Duda, Petra W, Krieger, Jeffrey I, Schmied, Mascha C, Balentine, Courtney, Hafler, David A
Published in The Journal of immunology (1950) (15.12.2000)
Published in The Journal of immunology (1950) (15.12.2000)
Get full text
Journal Article
Clinical Effects of the Self-administered Subcutaneous Complement Inhibitor Zilucoplan in Patients With Moderate to Severe Generalized Myasthenia Gravis: Results of a Phase 2 Randomized, Double-Blind, Placebo-Controlled, Multicenter Clinical Trial
Howard, Jr, James F, Nowak, Richard J, Wolfe, Gil I, Freimer, Miriam L, Vu, Tuan H, Hinton, John L, Benatar, Michael, Duda, Petra W, MacDougall, James E, Farzaneh-Far, Ramin, Kaminski, Henry J, Barohn, Richard, Dimachkie, Mazen, Pasnoor, Mamatha, Farmakidis, Constantine, Liu, Tina, Colgan, Samantha, Benatar, Michael G, Bertorini, Tulio, Pillai, Rekha, Henegar, Robert, Bromberg, Mark, Gibson, Summer, Janecki, Teresa, Freimer, Miriam, Elsheikh, Bakri, Matisak, Paige, Genge, Angela, Guidon, Amanda, David, William, Habib, Ali A, Mathew, Veena, Mozaffar, Tahseen, Hewitt, William, Barnett, Deborah, Sullivan, Patricia, Ho, Doreen, Traub, Rebecca E, Chopra, Manisha, Aly, Radwa, Bayat, Elham, Abu-Rub, Mohammad, Khan, Shaida, Lange, Dale, Holzberg, Shara, Khatri, Bhupendra, Lindman, Emily, Olapo, Tayo, Sershon, Lisa M, Lisak, Robert P, Bernitsas, Evanthia, Jia, Kelly, Malik, Rabia, Lewis-Collins, Tiffany D, Nicolle, Michael, Sharma, Aditi, Roy, Bhaskar, Nye, Joan, Pulley, Michael, Berger, Alan, Shabbir, Yasmeen, Sachdev, Amit, Patterson, Kimberly, Siddiqi, Zaeem, Sivak, Mark, Bratton, Joan, Small, George, Kohli, Anem, Fetter, Mary, Vu, Tuan, Lam, Lucy, Harvey, Brittany, Silvestri, Nicholas, Patrick, Kara, Zakalik, Karen, MacDougall, James, Pontius, Angela, Hoarty, Michelle
Published in Archives of neurology (Chicago) (01.05.2020)
Published in Archives of neurology (Chicago) (01.05.2020)
Get full text
Journal Article
Safety and efficacy of zilucoplan in patients with generalised myasthenia gravis (RAISE): a randomised, double-blind, placebo-controlled, phase 3 study
Hewamadduma, Channa, Hinton, John, Juntas-Morales, Raul, Mantegazza, Renato, Sivakumar, Kumaraswamy, Śmiłowski, Marek, Utsugisawa, Kimiaki, Vu, Tuan, Weiss, Michael D, Brock, Melissa, Vanderkelen, Mark, Sembinelli, Dylan, Teitelbaum, Jeanne, Bernard, Emilien, Svahn, Juliette, Stojkovic, Tanya, Demeret, Sophie, Tranchant, Christine, Nadaj-Pakleza, Aleksandra, Chanson, Jean-Baptiste, Lecointe, Peggy, Schmidt, Jens, Zeng, Rachel, Kowarik, Markus, Ziemann, Ulf, Krumbholz, Markus, Martin, Pascal, Dünschede, Jutta, Berger, Benjamin, Stolte, Benjamin, Iorio, Raffaele, Falso, Silvia, Antozzi, Carlo, Frangiamore, Rita, Vanoli, Fiammetta, Rinaldi, Elena, Deguchi, Kazushi, Ishida, Sayaka, Suzuki, Shigeaki, Nakahara, Jin, Nagaoka, Astushi, Uzawa, Akiyuki, Kubota, Tomoya, Takahashi, Masanori, Okuno, Tatsusada, Murai, Hiroyuki, Chyrchel-Paszkiewicz, Urszula, Kumor, Klaudiusz, Błaż, Michał, Szczudlik, Andrzej, Paśko, Aneta, Szczechowski, Lech, Ilkowski, Jan, Kapetanovic Garcia, Solange, Ortiz Bagan, Patricia, Belén Cánovas Segura, Ana, Cortes Vicente, Elena, Rodrigo Armenteros, Patricia, Cavey, Ana, Liow, Kore, Barboi, Alexandru, Guingrich, Sandra, Saba, Sami, Tellez, Marco, Elsheikh, Bakri, Freimer, Miriam, Govindarajan, Raghav, Habib, Ali A, Korb, Manisha, Machemehl, Hannah, Allen, Jeffrey, Harper, Emily, Farmakidis, Constantine, Saavedra, Lilli, Dimachkie, Mazen, McIlduff, Courtney, Barnes, Benjamin, Suresh, Niraja, Shaw, Jessica, Chopra, Manisha, Traub, Rebecca E, Jones, Sarah, Wagoner, Mary, Katz, Jonathan, Jenkins, Liberty, Khan, Shaida, Khatri, Bhupendra, Li, Yuebing, Caristo, Irys B, Rube, Jacob, Lisak, Robert P, Choudhury, Aparna, Ruzhansky, Katherine, Sachdev, Amit, Shin, Susan, Fetter, Mary, McKinnon, Jonathan, Sissons-Ross, Laura, Sahu, Amos, Distad, B Jane
Published in Lancet neurology (01.05.2023)
Published in Lancet neurology (01.05.2023)
Get full text
Journal Article
Subgroup outcomes from RAISE: a randomised, Phase 3 trial of zilucoplan in generalised myasthenia gravis
Hewamadduma Channa, Bresch Saskia, Juntas-Morales Raul, Leite, Isabel, Maniaol Angelina, Zajda Malgorzata, Boroojerdi Babak, Duda Petra, de la Borderie Guillemette, Howard, James
Published in Journal of neurology, neurosurgery and psychiatry (01.11.2023)
Published in Journal of neurology, neurosurgery and psychiatry (01.11.2023)
Get full text
Journal Article
RAISE-XT: interim analysis of an open-label extension study of zilucoplan in patients with myasthenia gravis
Leite, Maria Isabel, Genge, Angela, Mantegazza Renato, Utsugisawa Kimiaki, Duda Petra, Boroojerdi Babak, Vanderkelen, Mark, de la Borderie Guillemette, Howard, James
Published in Journal of neurology, neurosurgery and psychiatry (01.11.2023)
Published in Journal of neurology, neurosurgery and psychiatry (01.11.2023)
Get full text
Journal Article
MS disease activity in RESTORE: a randomized 24-week natalizumab treatment interruption study
Fox, Robert J, Cree, Bruce A C, De Sèze, Jerome, Gold, Ralf, Hartung, Hans-Peter, Jeffery, Douglas, Kappos, Ludwig, Kaufman, Michael, Montalbán, Xavier, Weinstock-Guttman, Bianca, Anderson, Britt, Natarajan, Amy, Ticho, Barry, Duda, Petra
Published in Neurology (29.04.2014)
Published in Neurology (29.04.2014)
Get more information
Journal Article
Natalizumab treatment shows no clinically meaningful effects on immunization responses in patients with relapsing-remitting multiple sclerosis
Kaufman, Michael, Pardo, Gabriel, Rossman, Howard, Sweetser, Marianne T, Forrestal, Fiona, Duda, Petra
Published in Journal of the neurological sciences (15.06.2014)
Published in Journal of the neurological sciences (15.06.2014)
Get full text
Journal Article
Immune-mediated neuropathies: etiology and pathogenic relationship to aging processes
Pletz, Mathias W.R, Duda, Petra W, Kappos, Ludwig, Steck, Andreas J
Published in Journal of Neuroimmunology (01.04.2003)
Published in Journal of Neuroimmunology (01.04.2003)
Get full text
Book Review
Journal Article
A study of mefloquine treatment for progressive multifocal leukoencephalopathy: results and exploration of predictors of PML outcomes
Clifford, David B., Nath, Avindra, Cinque, Paola, Brew, Bruce J., Zivadinov, Robert, Gorelik, Leonid, Zhao, Zhenming, Duda, Petra
Published in Journal of neurovirology (01.08.2013)
Published in Journal of neurovirology (01.08.2013)
Get full text
Journal Article