Functional expression of complement factor I following AAV-mediated gene delivery in the retina of mice and human cells
Dreismann, Anna K, McClements, Michelle E, Barnard, Alun R, Orhan, Elise, Hughes, Jane P, Lachmann, Peter J, MacLaren, Robert E
Published in Gene therapy (01.05.2021)
Published in Gene therapy (01.05.2021)
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Journal Article
Adeno-Associated Virus Vector Gene Delivery Elevates Factor I Levels and Downregulates the Complement Alternative Pathway In Vivo
Ahmad, Amina, Mandwie, Mawj, Dreismann, Anna K, Smyth, Christine M, Doyle, Helen, Malik, Talat H, Pickering, Matthew C, Lachmann, Peter J, Alexander, Ian E, Logan, Grant J
Published in Human gene therapy (01.11.2021)
Published in Human gene therapy (01.11.2021)
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Comprehensive functional characterization of complement factor I rare variant genotypes identified in the SCOPE geographic atrophy cohort
Hallam, Thomas M., Andreadi, Anneliza, Sharp, Scott J., Brocklebank, Vicky, Gardenal, Emanuela, Dreismann, Anna, Arora, Rashi, Dennis, Marcus, Flaxel, Christina, Hall, Edward, Hoyng, Carel, Charbel Issa, Peter, Leveziel, Nicolas, Molnár, Fanni, Navarro, Rafael, Schneiderman, Todd, Steel, David, Tadayoni, Ramin, Tezel, Tongalp, Weber, Michel, Lotery, Andrew J., Marchbank, Kevin J., Harris, Claire L., Jones, Amy V., Kavanagh, David
Published in The Journal of biological chemistry (01.07.2024)
Published in The Journal of biological chemistry (01.07.2024)
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