Expert Consensus Recommendations for the Suspicion and Diagnosis of Transthyretin Cardiac Amyloidosis
Maurer, Mathew S, Bokhari, Sabahat, Damy, Thibaud, Dorbala, Sharmila, Drachman, Brian M, Fontana, Marianna, Grogan, Martha, Kristen, Arnt V, Lousada, Isabelle, Nativi-Nicolau, Jose, Cristina Quarta, Candida, Rapezzi, Claudio, Ruberg, Frederick L, Witteles, Ronald, Merlini, Giampaolo
Published in Circulation. Heart failure (01.09.2019)
Published in Circulation. Heart failure (01.09.2019)
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Journal Article
Tafamidis Treatment for Patients with Transthyretin Amyloid Cardiomyopathy
Maurer, Mathew S, Schwartz, Jeffrey H, Gundapaneni, Balarama, Elliott, Perry M, Merlini, Giampaolo, Waddington-Cruz, Marcia, Kristen, Arnt V, Grogan, Martha, Witteles, Ronald, Damy, Thibaud, Drachman, Brian M, Shah, Sanjiv J, Hanna, Mazen, Judge, Daniel P, Barsdorf, Alexandra I, Huber, Peter, Patterson, Terrell A, Riley, Steven, Schumacher, Jennifer, Stewart, Michelle, Sultan, Marla B, Rapezzi, Claudio
Published in The New England journal of medicine (13.09.2018)
Published in The New England journal of medicine (13.09.2018)
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Journal Article
Inotersen Treatment for Patients with Hereditary Transthyretin Amyloidosis
Benson, Merrill D, Waddington-Cruz, Márcia, Berk, John L, Polydefkis, Michael, Dyck, Peter J, Wang, Annabel K, Planté-Bordeneuve, Violaine, Barroso, Fabio A, Merlini, Giampaolo, Obici, Laura, Scheinberg, Morton, Brannagan, Thomas H, Litchy, William J, Whelan, Carol, Drachman, Brian M, Adams, David, Heitner, Stephen B, Conceição, Isabel, Schmidt, Hartmut H, Vita, Giuseppe, Campistol, Josep M, Gamez, Josep, Gorevic, Peter D, Gane, Edward, Shah, Amil M, Solomon, Scott D, Monia, Brett P, Hughes, Steven G, Kwoh, T. Jesse, McEvoy, Bradley W, Jung, Shiangtung W, Baker, Brenda F, Ackermann, Elizabeth J, Gertz, Morie A, Coelho, Teresa
Published in The New England journal of medicine (05.07.2018)
Published in The New England journal of medicine (05.07.2018)
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Journal Article
Long-Term Survival With Tafamidis in Patients With Transthyretin Amyloid Cardiomyopathy
Elliott, Perry, Drachman, Brian M, Gottlieb, Stephen S, Hoffman, James E, Hummel, Scott L, Lenihan, Daniel J, Ebede, Ben, Gundapaneni, Balarama, Li, Benjamin, Sultan, Marla B, Shah, Sanjiv J
Published in Circulation. Heart failure (01.01.2022)
Published in Circulation. Heart failure (01.01.2022)
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Journal Article
Assessing mNIS+7Ionis and international neurologists' proficiency in a familial amyloidotic polyneuropathy trial
Dyck, Peter J., Kincaid, John C., Dyck, P. James B., Chaudhry, Vinay, Goyal, Namita A., Alves, Christina, Salhi, Hayet, Wiesman, Janice F., Labeyrie, Celine, Robinson‐Papp, Jessica, Cardoso, Márcio, Laura, Matilde, Ruzhansky, Katherine, Cortese, Andrea, Brannagan, Thomas H., Khoury, Julie, Khella, Sami, Waddington‐Cruz, Márcia, Ferreira, João, Wang, Annabel K., Pinto, Marcus V., Ayache, Samar S., Benson, Merrill D., Berk, John L., Coelho, Teresa, Polydefkis, Michael, Gorevic, Peter, Adams, David H., Plante‐Bordeneuve, Violaine, Whelan, Carol, Merlini, Giampaolo, Heitner, Stephen, Drachman, Brian M., Conceição, Isabel, Klein, Christopher J., Gertz, Morie A., Ackermann, Elizabeth J., Hughes, Steven. G., Mauermann, Michelle. L., Bergemann, Rito, Lodermeier, Karen A., Davies, Jenny L., Carter, Rickey E., Litchy, William J.
Published in Muscle & nerve (01.11.2017)
Published in Muscle & nerve (01.11.2017)
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Journal Article
Treatment characteristics of patients with hereditary transthyretin amyloidosis: a cohort study
Qarni, Taha N, Jones, Felipe J S, Drachman, Brian, Khella, Sami, Pieretti, Janice, Bustamante, Nicolas Sarmiento, Karam, Chafic
Published in Orphanet journal of rare diseases (08.05.2024)
Published in Orphanet journal of rare diseases (08.05.2024)
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Journal Article
ATTR amyloidosis during the COVID-19 pandemic: insights from a global medical roundtable
Brannagan, 3rd, Thomas H, Auer-Grumbach, Michaela, Berk, John L, Briani, Chiara, Bril, Vera, Coelho, Teresa, Damy, Thibaud, Dispenzieri, Angela, Drachman, Brian M, Fine, Nowell, Gaggin, Hanna K, Gertz, Morie, Gillmore, Julian D, Gonzalez, Esther, Hanna, Mazen, Hurwitz, David R, Khella, Sami L, Maurer, Mathew S, Nativi-Nicolau, Jose, Olugemo, Kemi, Quintana, Luis F, Rosen, Andrew M, Schmidt, Hartmut H, Shehata, Jacqueline, Waddington-Cruz, Marcia, Whelan, Carol, Ruberg, Frederick L
Published in Orphanet journal of rare diseases (06.05.2021)
Published in Orphanet journal of rare diseases (06.05.2021)
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Journal Article
The Cardiac Amyloidosis Registry Study (CARS): Rationale, Design and Methodology
STERN, LILY K., GRODIN, JUSTIN L., MAURER, MATHEW S., RUBERG, FREDERICK L., PATEL, AYAN R., KHOURI, MICHEL G., ROTH, LORI R., ARAS, MANDAR A., BHARDWAJ, ANJU, BHATTACHARYA, PRIYANKA, BRAILOVSKY, YEVGENIY, DRACHMAN, BRIAN M., EBONG, IMO A., FINE, NOWELL M., GAGGIN, HANNA, GOPAL, DEEPA, GRIFFIN, JAN, JUDGE, DANIEL, KIM, PAUL, MITCHELL, JOSHUA, MITTER, SUMEET S., MOHAN, RAJEEV C., RAMOS, HANNIA, REYENTOVICH, ALEX, SHEIKH, FAROOQ H., SPERRY, BRETT, CARTER, SPENCER, UREY, MARCUS, VAISHNAV, JOBAN, VEST, AMANDA R., KITTLESON, MICHELLE M., PATEL, JIGNESH K.
Published in Journal of cardiac failure (01.05.2024)
Published in Journal of cardiac failure (01.05.2024)
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Journal Article
Age- and Sex-Related Differences in Patients With Wild-Type Transthyretin Amyloidosis: Insights From THAOS
Mora-Ayestaran, Nerea, Dispenzieri, Angela, Kristen, Arnt V, Maurer, Mathew S, Diemberger, Igor, Drachman, Brian M, Grogan, Martha, Gupta, Pritam, Glass, Oliver, Amass, Leslie, Garcia-Pavia, Pablo
Published in JACC. Advances (Online) (01.08.2024)
Published in JACC. Advances (Online) (01.08.2024)
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Journal Article
Rationale and design of a randomized trial of automated hovering for post-myocardial infarction patients: The HeartStrong program
Troxel, Andrea B., ScD, Asch, David A., MD, MBA, Mehta, Shivan J., MD, MBA, MSHP, Norton, Laurie, MA, Taylor, Devon, BS, Calderon, Tirza A., MPH, Lim, Raymond, MA, Zhu, Jingsan, MS, MBA, Kolansky, Daniel M., MD, Drachman, Brian M., MD, Volpp, Kevin G., MD, PhD
Published in The American heart journal (01.09.2016)
Published in The American heart journal (01.09.2016)
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Journal Article
Long-term survival in people with transthyretin amyloid cardiomyopathy who took tafamidis: A Plain Language Summary
Elliott, Perry, Drachman, Brian M, Gottlieb, Stephen S, Hoffman, James E, Hummel, Scott L, Lenihan, Daniel J, Ebede, Ben, Gundapaneni, Balarama, Li, Benjamin, Sultan, Marla B, Shah, Sanjiv J
Published in Future cardiology (01.01.2023)
Published in Future cardiology (01.01.2023)
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Journal Article
Avoiding misdiagnosis: expert consensus recommendations for the suspicion and diagnosis of transthyretin amyloidosis for the general practitioner
Gertz, Morie, Adams, David, Ando, Yukio, Beirão, João Melo, Bokhari, Sabahat, Coelho, Teresa, Comenzo, Raymond L, Damy, Thibaud, Dorbala, Sharmila, Drachman, Brian M, Fontana, Marianna, Gillmore, Julian D, Grogan, Martha, Hawkins, Philip N, Lousada, Isabelle, Kristen, Arnt V, Ruberg, Frederick L, Suhr, Ole B, Maurer, Mathew S, Nativi-Nicolau, Jose, Quarta, Candida Cristina, Rapezzi, Claudio, Witteles, Ronald, Merlini, Giampaolo
Published in BMC family practice (23.09.2020)
Published in BMC family practice (23.09.2020)
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Journal Article
Assessing mNIS+7 Ionis and international neurologists' proficiency in a familial amyloidotic polyneuropathy trial
Dyck, Peter J, Kincaid, John C, Dyck, P James B, Chaudhry, Vinay, Goyal, Namita A, Alves, Christina, Salhi, Hayet, Wiesman, Janice F, Labeyrie, Celine, Robinson-Papp, Jessica, Cardoso, Márcio, Laura, Matilde, Ruzhansky, Katherine, Cortese, Andrea, Brannagan, 3rd, Thomas H, Khoury, Julie, Khella, Sami, Waddington-Cruz, Márcia, Ferreira, João, Wang, Annabel K, Pinto, Marcus V, Ayache, Samar S, Benson, Merrill D, Berk, John L, Coelho, Teresa, Polydefkis, Michael, Gorevic, Peter, Adams, David H, Plante-Bordeneuve, Violaine, Whelan, Carol, Merlini, Giampaolo, Heitner, Stephen, Drachman, Brian M, Conceição, Isabel, Klein, Christopher J, Gertz, Morie A, Ackermann, Elizabeth J, Hughes, Steven G, Mauermann, Michelle L, Bergemann, Rito, Lodermeier, Karen A, Davies, Jenny L, Carter, Rickey E, Litchy, William J
Published in Muscle & nerve (01.11.2017)
Published in Muscle & nerve (01.11.2017)
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Journal Article
A prospective study of continuous intravenous milrinone therapy for status IB patients awaiting heart transplant at home
Brozena, Susan C., Twomey, Carol, Goldberg, Lee R., Desai, Shashank S., Drachman, Brian, Kao, Andrew, Popjes, Eric, Zimmer, Ross, Jessup, Mariell
Published in The Journal of heart and lung transplantation (01.09.2004)
Published in The Journal of heart and lung transplantation (01.09.2004)
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Journal Article
Genotype and Phenotype of Transthyretin Cardiac Amyloidosis
Maurer, Mathew S., MD, Hanna, Mazen, MD, Grogan, Martha, MD, Dispenzieri, Angela, MD, Witteles, Ronald, MD, Drachman, Brian, MD, Judge, Daniel P., MD, Lenihan, Daniel J., MD, Gottlieb, Stephen S., MD, Shah, Sanjiv J., MD, Steidley, D. Eric, MD, Ventura, Hector, MD, Murali, Srinivas, MD, Silver, Marc A., MD, Jacoby, Daniel, MD, Fedson, Savitri, MD, Hummel, Scott L., MD, Kristen, Arnt V., MD, Damy, Thibaud, MD, PhD, Planté-Bordeneuve, Violaine, MD, PhD, Coelho, Teresa, MD, Mundayat, Rajiv, MS, Suhr, Ole B., MD, Waddington Cruz, Márcia, MD, Rapezzi, Claudio, MD
Published in Journal of the American College of Cardiology (12.07.2016)
Published in Journal of the American College of Cardiology (12.07.2016)
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Journal Article
A new transthyretin variant (Glu61Gly) associated with cardiomyopathy
Rosenzweig, Michael, Skinner, Martha, Prokaeva, Tatiana, Théberge, Roger, Costello, Catherine, Drachman, Brian M., Connors, Lawreen H.
Published in Amyloid (01.03.2007)
Published in Amyloid (01.03.2007)
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Journal Article
Genotype and Phenotype of Transthyretin Cardiac Amyloidosis: THAOS (Transthyretin Amyloid Outcome Survey)
Maurer, Mathew S, Hanna, Mazen, Grogan, Martha, Dispenzieri, Angela, Witteles, Ronald, Drachman, Brian, Judge, Daniel P, Lenihan, Daniel J, Gottlieb, Stephen S, Shah, Sanjiv J, Steidley, D Eric, Ventura, Hector, Murali, Srinivas, Silver, Marc A, Jacoby, Daniel, Fedson, Savitri, Hummel, Scott L, Kristen, Arnt V, Damy, Thibaud, Planté-Bordeneuve, Violaine, Coelho, Teresa, Mundayat, Rajiv, Suhr, Ole B, Waddington Cruz, Márcia, Rapezzi, Claudio
Published in Journal of the American College of Cardiology (12.07.2016)
Published in Journal of the American College of Cardiology (12.07.2016)
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Journal Article
Effect of Electronic Reminders, Financial Incentives, and Social Support on Outcomes After Myocardial Infarction: The HeartStrong Randomized Clinical Trial
Volpp, Kevin G, Troxel, Andrea B, Mehta, Shivan J, Norton, Laurie, Zhu, Jingsan, Lim, Raymond, Wang, Wenli, Marcus, Noora, Terwiesch, Christian, Caldarella, Kristen, Levin, Tova, Relish, Mike, Negin, Nathan, Smith-McLallen, Aaron, Snyder, Richard, Spettell, Claire M, Drachman, Brian, Kolansky, Daniel, Asch, David A
Published in JAMA internal medicine (01.08.2017)
Published in JAMA internal medicine (01.08.2017)
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Journal Article
Baseline Characteristics Of Patients With Transthyretin Cardiac Amyloidosis Enrolled In The Patisiran Expanded Access Program
Saha, Naveen, Shah, Zubair, Hanna, Mazen A., Nikolova, Andriana, Moffitt, Colleen, Summers, Catherine, Capocelli, Kelley, Drachman, Brian M.
Published in Journal of cardiac failure (01.01.2024)
Published in Journal of cardiac failure (01.01.2024)
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Journal Article