Small-Molecule Modulation of TDP-43 Recruitment to Stress Granules Prevents Persistent TDP-43 Accumulation in ALS/FTD
Fang, Mark Y., Markmiller, Sebastian, Vu, Anthony Q., Javaherian, Ashkan, Dowdle, William E., Jolivet, Philippe, Bushway, Paul J., Castello, Nicholas A., Baral, Ashmita, Chan, Michelle Y., Linsley, Jeremy W., Linsley, Drew, Mercola, Mark, Finkbeiner, Steven, Lecuyer, Eric, Lewcock, Joseph W., Yeo, Gene W.
Published in Neuron (Cambridge, Mass.) (04.09.2019)
Published in Neuron (Cambridge, Mass.) (04.09.2019)
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Autophagy-Independent Lysosomal Targeting Regulated by ULK1/2-FIP200 and ATG9
Goodwin, Jonathan M., Dowdle, William E., DeJesus, Rowena, Wang, Zuncai, Bergman, Philip, Kobylarz, Marek, Lindeman, Alicia, Xavier, Ramnik J., McAllister, Gregory, Nyfeler, Beat, Hoffman, Gregory, Murphy, Leon O.
Published in Cell reports (Cambridge) (05.09.2017)
Published in Cell reports (Cambridge) (05.09.2017)
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Hypoimmune anti-CD19 chimeric antigen receptor T cells provide lasting tumor control in fully immunocompetent allogeneic humanized mice
Hu, Xiaomeng, Manner, Karl, DeJesus, Rowena, White, Kathy, Gattis, Corie, Ngo, Priscilla, Bandoro, Christopher, Tham, Eleonore, Chu, Elaine Y, Young, Chi, Wells, Frank, Basco, Ronald, Friera, Annabelle, Kangeyan, Divy, Beauchesne, Pascal, Dowdle, William E, Deuse, Tobias, Fry, Terry J, Foster, Aaron E, Schrepfer, Sonja
Published in Nature communications (10.04.2023)
Published in Nature communications (10.04.2023)
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TMEM231, mutated in orofaciodigital and Meckel syndromes, organizes the ciliary transition zone
Roberson, Elle C, Dowdle, William E, Ozanturk, Aysegul, Garcia-Gonzalo, Francesc R, Li, Chunmei, Halbritter, Jan, Elkhartoufi, Nadia, Porath, Jonathan D, Cope, Heidi, Ashley-Koch, Allison, Gregory, Simon, Thomas, Sophie, Sayer, John A, Saunier, Sophie, Otto, Edgar A, Katsanis, Nicholas, Davis, Erica E, Attié-Bitach, Tania, Hildebrandt, Friedhelm, Leroux, Michel R, Reiter, Jeremy F
Published in The Journal of cell biology (13.04.2015)
Published in The Journal of cell biology (13.04.2015)
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A high-fat diet regulates gastrin and acid secretion through primary cilia
Saqui-Salces, Milena, Dowdle, William E, Reiter, Jeremy F, Merchant, Juanita L
Published in The FASEB journal (01.08.2012)
Published in The FASEB journal (01.08.2012)
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Role of epidermal primary cilia in the homeostasis of skin and hair follicles
Croyle, Mandy J, Lehman, Jonathan M, O'Connor, Amber K, Wong, Sunny Y, Malarkey, Erik B, Iribarne, Daniela, Dowdle, William E, Schoeb, Trenton R, Verney, Zoe M, Athar, Mohammad, Michaud, Edward J, Reiter, Jeremy F, Yoder, Bradley K
Published in Development (Cambridge) (01.05.2011)
Published in Development (Cambridge) (01.05.2011)
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Human hypoimmune primary pancreatic islets avoid rejection and autoimmunity and alleviate diabetes in allogeneic humanized mice
Hu, Xiaomeng, Gattis, Corie, Olroyd, Ari G, Friera, Annabelle M, White, Kathy, Young, Chi, Basco, Ron, Lamba, Meghan, Wells, Frank, Ankala, Ramya, Dowdle, William E, Lin, August, Egenberger, Kyla, Rukstalis, J Michael, Millman, Jeffrey R, Connolly, Andrew J, Deuse, Tobias, Schrepfer, Sonja
Published in Science translational medicine (12.04.2023)
Published in Science translational medicine (12.04.2023)
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Disruption of a Ciliary B9 Protein Complex Causes Meckel Syndrome
Dowdle, William E., Robinson, Jon F., Kneist, Andreas, Sirerol-Piquer, M. Salomé, Frints, Suzanna G.M., Corbit, Kevin C., Zaghloul, Norann A., van Lijnschoten, Gesina, Mulders, Leon, Verver, Dideke E., Zerres, Klaus, Reed, Randall R., Attié-Bitach, Tania, Johnson, Colin A., García-Verdugo, José Manuel, Katsanis, Nicholas, Bergmann, Carsten, Reiter, Jeremy F.
Published in American journal of human genetics (07.10.2011)
Published in American journal of human genetics (07.10.2011)
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183-OR: Overcoming Immunological Barriers for “Off-the-Shelf” iPSC-Derived Islets
HU, XIAOMENG, WHITE, KATHY, OLROYD, ARI G., DEJESUS, ROWENA, DOMINGUEZ, ANTONIA, DOWDLE, WILLIAM E., CHU, ELAINE Y.L., FRIERA, ANNABELLE, YOUNG, CHI, WELLS, FRANK, MCGILL, TREVOR, RUKSTALIS, MICHAEL, GATTIS, CORIE, BASCO, RONALD, MILLMAN, JEFFREY R., SCHREPFER, SONJA
Published in Diabetes (New York, N.Y.) (01.06.2022)
Published in Diabetes (New York, N.Y.) (01.06.2022)
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SUPT4H1 Depletion Leads to a Global Reduction in RNA
Naguib, Adam, Sandmann, Thomas, Yi, Fei, Watts, Ryan J., Lewcock, Joseph W., Dowdle, William E.
Published in Cell reports (Cambridge) (02.01.2019)
Published in Cell reports (Cambridge) (02.01.2019)
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Discovery of DNL343: A Potent, Selective, and Brain-Penetrant eIF2B Activator Designed for the Treatment of Neurodegenerative Diseases
Craig, Robert A., De Vicente, Javier, Estrada, Anthony A., Feng, Jianwen A., Lexa, Katrina W., Canet, Mark J., Dowdle, William E., Erickson, Rebecca I., Flores, Brittany N., Haddick, Patrick C. G., Kane, Lesley A., Lewcock, Joseph W., Moerke, Nathan J., Poda, Suresh B., Sweeney, Zachary, Takahashi, Ryan H., Tong, Vincent, Wang, Jing, Yulyaningsih, Ernie, Solanoy, Hilda, Scearce-Levie, Kimberly, Sanchez, Pascal E., Tang, Liwei, Xu, Musheng, Zhang, Rui, Osipov, Maksim
Published in Journal of medicinal chemistry (11.04.2024)
Published in Journal of medicinal chemistry (11.04.2024)
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Potent, Selective, and Orally Bioavailable Inhibitors of VPS34 Provide Chemical Tools to Modulate Autophagy in Vivo
Honda, Ayako, Harrington, Edmund, Cornella-Taracido, Ivan, Furet, Pascal, Knapp, Mark S, Glick, Meir, Triantafellow, Ellen, Dowdle, William E, Wiedershain, Dmitri, Maniara, Wieslawa, Moore, Christine, Finan, Peter M, Hamann, Lawrence G, Firestone, Brant, Murphy, Leon O, Keaney, Erin P
Published in ACS medicinal chemistry letters (14.01.2016)
Published in ACS medicinal chemistry letters (14.01.2016)
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201 Food Intake Stimulates Gastrin and Acid Secretion Through Primary Cilia
Saqui-Salces, Milena, Dowdle, William E, Reiter, Jeremy F, Merchant, Juanita L
Published in Gastroenterology (New York, N.Y. 1943) (01.05.2012)
Published in Gastroenterology (New York, N.Y. 1943) (01.05.2012)
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Role of epidermal primary cilia in the homeostasis of skin and hair follicles
Croyle, Mandy J., Lehman, Jonathan M., O'Connor, Amber K., Wong, Sunny Y., Malarkey, Erik B., Iribarne, Daniela, Dowdle, William E., Schoeb, Trenton R., Verney, Zoe M., Athar, Mohammad, Michaud, Edward J., Reiter, Jeremy F., Yoder, Bradley K.
Published in Journal of cell science (01.05.2011)
Published in Journal of cell science (01.05.2011)
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Selective VPS34 inhibitor blocks autophagy and uncovers a role for NCOA4 in ferritin degradation and iron homeostasis in vivo
Dowdle, William E, Nyfeler, Beat, Nagel, Jane, Elling, Robert A, Liu, Shanming, Triantafellow, Ellen, Menon, Suchithra, Wang, Zuncai, Honda, Ayako, Pardee, Gwynn, Cantwell, John, Luu, Catherine, Cornella-Taracido, Ivan, Harrington, Edmund, Fekkes, Peter, Lei, Hong, Fang, Qing, Digan, Mary Ellen, Burdick, Debra, Powers, Andrew F, Helliwell, Stephen B, D'Aquin, Simon, Bastien, Julie, Wang, Henry, Wiederschain, Dmitri, Kuerth, Jenny, Bergman, Philip, Schwalb, David, Thomas, Jason, Ugwonali, Savuth, Harbinski, Fred, Tallarico, John, Wilson, Christopher J, Myer, Vic E, Porter, Jeffery A, Bussiere, Dirksen E, Finan, Peter M, Labow, Mark A, Mao, Xiaohong, Hamann, Lawrence G, Manning, Brendan D, Valdez, Reginald A, Nicholson, Thomas, Schirle, Markus, Knapp, Mark S, Keaney, Erin P, Murphy, Leon O
Published in Nature cell biology (01.11.2014)
Published in Nature cell biology (01.11.2014)
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Engineered Hypoimmune CAR T Cells Provide Lasting Tumor Control in Fully Immunocompetent Allogeneic Humanized Mice
Hu, Xiaomeng, Beauchesne, Pascal, Manner, Karl, Gattis, Corie, Ngo, Priscilla, De Jesus, Rowena, Young, Chi, Wells, Frank, Weng, Lindong, White, Kathy, Dowdle, William E, Foster, Aaron, Fry, Terry, Schrepfer, Sonja
Published in Blood (15.11.2022)
Published in Blood (15.11.2022)
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Engineered Hypoimmune Allogeneic CAR T Cells Exhibit Innate and Adaptive Immune Evasion Even after Sensitization in Humanized Mice and Retain Potent Anti-Tumor Activity
Hu, Xiaomeng, Dao, Mo, White, Kathy, Gattis, Corie, Clarke, Ryan, Landry, Sam, Basco, Ron, Tham, Eleonore, Tucker, Andrew, Luo, Emily, Bandoro, Christopher, Chu, Elaine, Young, Chi, Foster, Aaron E., Dowdle, William E, Rebar, Edward J, Fry, Terry J., Schrepfer, Sonja
Published in Blood (23.11.2021)
Published in Blood (23.11.2021)
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