Small molecule recognition of disease-relevant RNA structures
Meyer, Samantha M, Williams, Christopher C, Akahori, Yoshihiro, Tanaka, Toru, Aikawa, Haruo, Tong, Yuquan, Childs-Disney, Jessica L, Disney, Matthew D
Published in Chemical Society reviews (05.10.2020)
Published in Chemical Society reviews (05.10.2020)
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Design of a small molecule against an oncogenic noncoding RNA
Velagapudi, Sai Pradeep, Cameron, Michael D., Haga, Christopher L., Rosenberg, Laura H., Lafitte, Marie, Duckett, Derek R., Phinney, Donald G., Disney, Matthew D.
Published in Proceedings of the National Academy of Sciences - PNAS (24.05.2016)
Published in Proceedings of the National Academy of Sciences - PNAS (24.05.2016)
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A cross-linking approach to map small molecule-RNA binding sites in cells
Velagapudi, Sai Pradeep, Li, Yue, Disney, Matthew D.
Published in Bioorganic & medicinal chemistry letters (15.06.2019)
Published in Bioorganic & medicinal chemistry letters (15.06.2019)
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Journal Article
Small Molecule Inhibition of microRNA-210 Reprograms an Oncogenic Hypoxic Circuit
Costales, Matthew G, Haga, Christopher L, Velagapudi, Sai Pradeep, Childs-Disney, Jessica L, Phinney, Donald G, Disney, Matthew D
Published in Journal of the American Chemical Society (08.03.2017)
Published in Journal of the American Chemical Society (08.03.2017)
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Journal Article
Discovery of a Biomarker and Lead Small Molecules to Target r(GGGGCC)-Associated Defects in c9FTD/ALS
Su, Zhaoming, Zhang, Yongjie, Gendron, Tania F., Bauer, Peter O., Chew, Jeannie, Yang, Wang-Yong, Fostvedt, Erik, Jansen-West, Karen, Belzil, Veronique V., Desaro, Pamela, Johnston, Amelia, Overstreet, Karen, Oh, Seok-Yoon, Todd, Peter K., Berry, James D., Cudkowicz, Merit E., Boeve, Bradley F., Dickson, Dennis, Floeter, Mary Kay, Traynor, Bryan J., Morelli, Claudia, Ratti, Antonia, Silani, Vincenzo, Rademakers, Rosa, Brown, Robert H., Rothstein, Jeffrey D., Boylan, Kevin B., Petrucelli, Leonard, Disney, Matthew D.
Published in Neuron (Cambridge, Mass.) (03.09.2014)
Published in Neuron (Cambridge, Mass.) (03.09.2014)
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Journal Article
Promoter-Bound Trinucleotide Repeat mRNA Drives Epigenetic Silencing in Fragile X Syndrome
Colak, Dilek, Zaninovic, Nikica, Cohen, Michael S., Rosenwaks, Zev, Yang, Wang-Yong, Gerhardt, Jeannine, Disney, Matthew D., Jaffrey, Samie R.
Published in Science (American Association for the Advancement of Science) (28.02.2014)
Published in Science (American Association for the Advancement of Science) (28.02.2014)
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Journal Article
Small-molecule targeted recruitment of a nuclease to cleave an oncogenic RNA in a mouse model of metastatic cancer
Costales, Matthew G., Aikawa, Haruo, Li, Yue, Childs-Disney, Jessica L., Abegg, Daniel, Hoch, Dominic G., Velagapudi, Sai Pradeep, Nakai, Yoshio, Khan, Tanya, Wang, Kye Won, Yildirim, Ilyas, Adibekian, Alexander, Wang, Eric T., Disney, Matthew D.
Published in Proceedings of the National Academy of Sciences - PNAS (04.02.2020)
Published in Proceedings of the National Academy of Sciences - PNAS (04.02.2020)
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Journal Article
A general fragment-based approach to identify and optimize bioactive ligands targeting RNA
Suresh, Blessy M., Li, Weichao, Zhang, Peiyuan, Wang, Kye Won, Yildirim, Ilyas, Parker, Christopher G., Disney, Matthew D.
Published in Proceedings of the National Academy of Sciences - PNAS (29.12.2020)
Published in Proceedings of the National Academy of Sciences - PNAS (29.12.2020)
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Journal Article
Precise small-molecule cleavage of an r(CUG) repeat expansion in a myotonic dystrophy mouse model
Angelbello, Alicia J., Rzuczek, Suzanne G., Mckee, Kendra K., Chen, Jonathan L., Olafson, Hailey, Cameron, Michael D., Moss, Walter N., Wang, Eric T., Disney, Matthew D.
Published in Proceedings of the National Academy of Sciences - PNAS (16.04.2019)
Published in Proceedings of the National Academy of Sciences - PNAS (16.04.2019)
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Journal Article
Inforna 2.0: A Platform for the Sequence-Based Design of Small Molecules Targeting Structured RNAs
Disney, Matthew D, Winkelsas, Audrey M, Velagapudi, Sai Pradeep, Southern, Mark, Fallahi, Mohammad, Childs-Disney, Jessica L
Published in ACS chemical biology (17.06.2016)
Published in ACS chemical biology (17.06.2016)
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Journal Article
A Designed Small Molecule Inhibitor of a Non-Coding RNA Sensitizes HER2 Negative Cancers to Herceptin
Costales, Matthew G, Hoch, Dominic G, Abegg, Daniel, Childs-Disney, Jessica L, Velagapudi, Sai Pradeep, Adibekian, Alexander, Disney, Matthew D
Published in Journal of the American Chemical Society (20.02.2019)
Published in Journal of the American Chemical Society (20.02.2019)
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Journal Article
Sequestration of DROSHA and DGCR8 by Expanded CGG RNA Repeats Alters MicroRNA Processing in Fragile X-Associated Tremor/Ataxia Syndrome
Sellier, Chantal, Freyermuth, Fernande, Tabet, Ricardos, Tran, Tuan, He, Fang, Ruffenach, Frank, Alunni, Violaine, Moine, Herve, Thibault, Christelle, Page, Adeline, Tassone, Flora, Willemsen, Rob, Disney, Matthew D., Hagerman, Paul J., Todd, Peter K., Charlet-Berguerand, Nicolas
Published in Cell reports (Cambridge) (01.03.2013)
Published in Cell reports (Cambridge) (01.03.2013)
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Journal Article
Design of small molecules targeting RNA structure from sequence
Ursu, Andrei, Childs-Disney, Jessica L, Andrews, Ryan J, O'Leary, Collin A, Meyer, Samantha M, Angelbello, Alicia J, Moss, Walter N, Disney, Matthew D
Published in Chemical Society reviews (19.10.2020)
Published in Chemical Society reviews (19.10.2020)
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Journal Article
Aberrant deposition of stress granule-resident proteins linked to C9orf72-associated TDP-43 proteinopathy
Chew, Jeannie, Cook, Casey, Gendron, Tania F, Jansen-West, Karen, Del Rosso, Giulia, Daughrity, Lillian M, Castanedes-Casey, Monica, Kurti, Aishe, Stankowski, Jeannette N, Disney, Matthew D, Rothstein, Jeffrey D, Dickson, Dennis W, Fryer, John D, Zhang, Yong-Jie, Petrucelli, Leonard
Published in Molecular neurodegeneration (15.02.2019)
Published in Molecular neurodegeneration (15.02.2019)
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