Unprecedented diversity of genotypic revertants in lymphocytes of a patient with Wiskott-Aldrich syndrome
Davis, Brian R., DiCola, Michael J., Prokopishyn, Nicole L., Rosenberg, Jonathan B., Moratto, Daniele, Muul, Linda M., Candotti, Fabio, Michael Blaese, R.
Published in Blood (15.05.2008)
Published in Blood (15.05.2008)
Get full text
Journal Article
De novo insertions and deletions of predominantly paternal origin are associated with autism spectrum disorder
Dong, Shan, Walker, Michael F, Carriero, Nicholas J, DiCola, Michael, Willsey, A Jeremy, Ye, Adam Y, Waqar, Zainulabedin, Gonzalez, Luis E, Overton, John D, Frahm, Stephanie, Keaney, 3rd, John F, Teran, Nicole A, Dea, Jeanselle, Mandell, Jeffrey D, Hus Bal, Vanessa, Sullivan, Catherine A, DiLullo, Nicholas M, Khalil, Rehab O, Gockley, Jake, Yuksel, Zafer, Sertel, Sinem M, Ercan-Sencicek, A Gulhan, Gupta, Abha R, Mane, Shrikant M, Sheldon, Michael, Brooks, Andrew I, Roeder, Kathryn, Devlin, Bernie, State, Matthew W, Wei, Liping, Sanders, Stephan J
Published in Cell reports (Cambridge) (09.10.2014)
Published in Cell reports (Cambridge) (09.10.2014)
Get full text
Journal Article
Natural gene therapy: Somatic reversion in the Wiskott–Aldrich syndrome
Davis, Brian R., DiCola, Michael J., Prokopishyn, Nicole L., Rosenberg, Jonathan B., Moratto, Daniele, Muul, Linda M., Candotti, Fabio, Blaese, R. Michael
Published in Blood cells, molecules, & diseases (01.03.2008)
Published in Blood cells, molecules, & diseases (01.03.2008)
Get full text
Journal Article
85. Von Willebrand Factor (VWF) Gene Targeting by Double-Strand Break Enhanced Homologous Recombination
Prokopishyn, Nicole L., Davis, Brian R., Rosenberg, Jonathan B., DiCola, Michael, Brosius, Jennifer, Blaese, R. Michael, Metz, Richard A.
Published in Molecular therapy (01.05.2006)
Published in Molecular therapy (01.05.2006)
Get full text
Journal Article
1040. Towards Gene Correction Therapy for Wiskott-Aldrich Syndrome Using Designed Zinc Finger Endonucleases
Davis, Brian R., Prokopishyn, Nicole L., Rosenberg, Jonathan, DiCola, Michael, Brosius, Jennifer, Michael Blaese, R., Metz, Richard A., Zhang, Lei, Xia, Danny, Miller, Jeffrey C., Kim, Kenneth, Urnov, Fyodor D., Gregory, Philip D., Holmes, Michael C.
Published in Molecular therapy (01.05.2006)
Published in Molecular therapy (01.05.2006)
Get full text
Journal Article