Reversal of Blindness in Animal Models of Leber Congenital Amaurosis Using Optimized AAV2-mediated Gene Transfer
Bennicelli, Jeannette, Wright, John Fraser, Komaromy, Andras, Jacobs, Jonathan B, Hauck, Bernd, Zelenaia, Olga, Mingozzi, Federico, Hui, Daniel, Chung, Daniel, Rex, Tonia S, Wei, Zhangyong, Qu, Guang, Zhou, Shangzhen, Zeiss, Caroline, Arruda, Valder R, Acland, Gregory M, Dell'Osso, Lou F, High, Katherine A, Maguire, Albert M, Bennett, Jean
Published in Molecular therapy (01.03.2008)
Published in Molecular therapy (01.03.2008)
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Journal Article
Safety and Efficacy of Gene Transfer for Leber's Congenital Amaurosis
Maguire, Maureen G, Maguire, Albert M, Simonelli, Francesca, Pierce, Eric A, Pugh, Edward N, Mingozzi, Federico, Bennicelli, Jeannette, Banfi, Sandro, Marshall, Kathleen A, Testa, Francesco, Surace, Enrico M, Rossi, Settimio, Lyubarsky, Arkady, Arruda, Valder R, Konkle, Barbara, Stone, Edwin, Sun, Junwei, Jacobs, Jonathan, Dell'Osso, Lou, Hertle, Richard, Ma, Jian-xing, Redmond, T. Michael, Zhu, Xiaosong, Hauck, Bernd, Zelenaia, Olga, Shindler, Kenneth S, Wright, J. Fraser, Volpe, Nicholas J, McDonnell, Jennifer Wellman, Auricchio, Alberto, High, Katherine A, Bennett, Jean
Published in The New England journal of medicine (22.05.2008)
Published in The New England journal of medicine (22.05.2008)
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Journal Article
Safety and Efficacy of Gene Transfer for Leber's Congenital AmaurosisBrief Report
Maguire, Albert M, Simonelli, Francesca, Pierce, Eric A, Pugh, Edward N, Mingozzi, Federico, Bennicelli, Jeannette, Banfi, Sandro, Marshall, Kathleen A, Testa, Francesco, Surace, Enrico M, Rossi, Settimio, Lyubarsky, Arkady, Arruda, Valder R, Konkle, Barbara, Stone, Edwin, Sun, Junwei, Jacobs, Jonathan, Dell'Osso, Lou, Hertle, Richard, Ma, Jian-xing, Redmond, T Michael, Zhu, Xiaosong, Hauck, Bernd, Zelenaia, Olga, Shindler, Kenneth S, Maguire, Maureen G, Wright, J Fraser, Volpe, Nicholas J, McDonnell, Jennifer Wellman, Auricchio, Alberto, High, Katherine A, Bennett, Jean
Published in The New England journal of medicine (22.05.2008)
Published in The New England journal of medicine (22.05.2008)
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Journal Article