Calpastatin-mediated inhibition of calpains in the mouse brain prevents mutant ataxin 3 proteolysis, nuclear localization and aggregation, relieving Machado―Joseph disease
SIMOES, Ana T, GONCALVES, Nélio, KOEPPEN, Arnulf, DEGLON, Nicole, KÜGLER, Sebastian, DUARTE, Carlos Bandeira, DE ALMEIDA, Luís Pereira
Published in Brain (London, England : 1878) (01.08.2012)
Published in Brain (London, England : 1878) (01.08.2012)
Get full text
Journal Article
AAV5-miHTT gene therapy demonstrates suppression of mutant huntingtin aggregation and neuronal dysfunction in a rat model of Huntington's disease
Miniarikova, J, Zimmer, V, Martier, R, Brouwers, C C, Pythoud, C, Richetin, K, Rey, M, Lubelski, J, Evers, M M, van Deventer, S J, Petry, H, Déglon, N, Konstantinova, P
Published in Gene therapy (01.10.2017)
Published in Gene therapy (01.10.2017)
Get full text
Journal Article
BDNF overexpression in mouse hippocampal astrocytes promotes local neurogenesis and elicits anxiolytic-like activities
Quesseveur, G, David, D J, Gaillard, M C, Pla, P, Wu, M V, Nguyen, H T, Nicolas, V, Auregan, G, David, I, Dranovsky, A, Hantraye, P, Hen, R, Gardier, A M, Déglon, N, Guiard, B P
Published in Translational psychiatry (30.04.2013)
Published in Translational psychiatry (30.04.2013)
Get full text
Journal Article
Gene transfer engineering for astrocyte-specific silencing in the CNS
Merienne, N, Delzor, A, Viret, A, Dufour, N, Rey, M, Hantraye, P, Déglon, N
Published in Gene therapy (01.10.2015)
Published in Gene therapy (01.10.2015)
Get full text
Journal Article
Activity analysis of housekeeping promoters using self-inactivating lentiviral vector delivery into the mouse retina
KOSTIC, C, CHIODINI, F, ARSENIJEVIC, Y, SALMON, P, WIZNEROWICZ, M, DEGLON, N, HORNFELD, D, TRONO, D, AEBISCHER, P, SCHORDERET, D. F, MUNIER, F. L
Published in Gene therapy (01.05.2003)
Published in Gene therapy (01.05.2003)
Get full text
Journal Article
Implication of the JNK pathway in a rat model of Huntington's disease
Perrin, V., Dufour, N., Raoul, C., Hassig, R., Brouillet, E., Aebischer, P., Luthi-Carter, R., Déglon, N.
Published in Experimental neurology (2009)
Published in Experimental neurology (2009)
Get full text
Journal Article
Neuroprotective gene therapy for Huntington's disease, using polymer-encapsulated cells engineered to secrete human ciliary neurotrophic factor: results of a phase I study
Bloch, J, Bachoud-Lévi, A C, Déglon, N, Lefaucheur, J P, Winkel, L, Palfi, S, Nguyen, J P, Bourdet, C, Gaura, V, Remy, P, Brugières, P, Boisse, M-F, Baudic, S, Cesaro, P, Hantraye, P, Aebischer, P, Peschanski, M
Published in Human gene therapy (01.10.2004)
Published in Human gene therapy (01.10.2004)
Get more information
Journal Article
Lentiviral nigral delivery of GDNF does not prevent neurodegeneration in a genetic rat model of Parkinson's disease
Lo Bianco, C., Déglon, N., Pralong, W., Aebischer, P.
Published in Neurobiology of disease (01.11.2004)
Published in Neurobiology of disease (01.11.2004)
Get full text
Journal Article
Efficient Gene Transfer and Expression of Biologically Active Glial Cell Line‐Derived Neurotrophic Factor in Rat Motoneurons Transduced with Lentiviral Vectors
Cisterni, C., Henderson, C. E., Aebischer, P., Pettmann, B., Déglon, N.
Published in Journal of neurochemistry (01.05.2000)
Published in Journal of neurochemistry (01.05.2000)
Get full text
Journal Article
Improvement of mouse β-thalassemia upon erythropoietin delivery by encapsulated myoblasts
DALLE, B, PAYEN, E, REGULIER, E, DEGLON, N, ROUYER-FESSARD, P, BEUZARD, Y, AEBISCHER, P
Published in Gene therapy (01.02.1999)
Published in Gene therapy (01.02.1999)
Get full text
Journal Article
Gene therapy for amyotrophic lateral sclerosis (ALS) using a polymer encapsulated xenogenic cell line engineered to secrete hCNTF
Aebischer, P, Pochon, N A, Heyd, B, Deglon, N, Joseph, J M, Zurn, A D, Baetge, E E, Hammang, J P, Goddard, M, Lysaght, M, Kaplan, F, Kato, A C, Schluep, M, Hirt, L, Regli, F, Porchet, F, De Tribolet, N
Published in Human gene therapy (01.05.1996)
Published in Human gene therapy (01.05.1996)
Get more information
Journal Article
Dose-dependent neuroprotective effect of ciliary neurotrophic factor delivered via tetracycline-regulated lentiviral vectors in the quinolinic acid rat model of Huntington's disease
Régulier, E, Pereira de Almeida, L, Sommer, B, Aebischer, P, Déglon, N
Published in Human gene therapy (01.11.2002)
Published in Human gene therapy (01.11.2002)
Get more information
Journal Article
The JAK/STAT3 pathway is a common inducer of astrocyte reactivity in Alzheimer's and Huntington's diseases
Ben Haim, Lucile, Ceyzériat, Kelly, Carrillo-de Sauvage, Maria Angeles, Aubry, Fabien, Auregan, Gwennaëlle, Guillermier, Martine, Ruiz, Marta, Petit, Fanny, Houitte, Diane, Faivre, Emilie, Vandesquille, Matthias, Aron-Badin, Romina, Dhenain, Marc, Déglon, Nicole, Hantraye, Philippe, Brouillet, Emmanuel, Bonvento, Gilles, Escartin, Carole
Published in The Journal of neuroscience (11.02.2015)
Published in The Journal of neuroscience (11.02.2015)
Get full text
Journal Article