Efficacy of dual intracerebroventricular and intravitreal CLN5 gene therapy in sheep prompts the first clinical trial to treat CLN5 Batten disease
Murray, Samantha J., Wellby, Martin P., Barrell, Graham K., Russell, Katharina N., Deane, Ashley R., Wynyard, John R., Gray, Steven J., Palmer, David N., Mitchell, Nadia L.
Published in Frontiers in pharmacology (24.10.2023)
Published in Frontiers in pharmacology (24.10.2023)
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Long-term safety and dose escalation of intracerebroventricular CLN5 gene therapy in sheep supports clinical translation for CLN5 Batten disease
Mitchell, Nadia L, Murray, Samantha J, Wellby, Martin P, Barrell, Graham K, Russell, Katharina N, Deane, Ashley R, Wynyard, John R, Palmer, Madeleine J, Pulickan, Anila, Prendergast, Phillipa M, Casy, Widler, Gray, Steven J, Palmer, David N
Published in Frontiers in genetics (08.08.2023)
Published in Frontiers in genetics (08.08.2023)
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Validation of a death assay for Angiostrongylus cantonensis larvae (L3) using propidium iodide in a rat model (Rattus norvegicus)
Jarvi, Susan I., Jacob, John, Sugihara, Robert T., Leinbach, Israel L., Klasner, Ina H., Kaluna, Lisa M., Snook, Kirsten A., Howe, M. Kathleen, Jacquier, Steven H., Lange, Ingo, Atkinson, Abigail L., Deane, Ashley R., Niebuhr, Chris N., Siers, Shane R.
Published in Parasitology (01.09.2019)
Published in Parasitology (01.09.2019)
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Occurrence of Rat Lungworm (Angiostrongylus cantonensis) in Invasive Coqui Frogs (Eleutherodactylus coqui) and Other Hosts in Hawaii, USA
Niebuhr, Chris N., Jarvi, Susan I., Kaluna, Lisa, Torres Fischer, Bruce L., Deane, Ashley R., Leinbach, Israel L., Siers, Shane R.
Published in Journal of wildlife diseases (01.01.2020)
Published in Journal of wildlife diseases (01.01.2020)
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